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Clinical Trials on Anemia, Dyserythropoietic, Congenital
Total 11596 results
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Children's Hospital Medical Center, CincinnatiRecruitingCongenital Dyserythropoietic Anemia (CDA)United States
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Lille Catholic UniversityUnknown
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Wolfson Medical CenterUnknownPatients With Thalassemia Intermedia, | Congenital Dyserythropoietic Anemia Type I
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Northwell HealthCompletedPure Red Cell Aplasia | Diamond Blackfan Anemia | Blackfan Diamond Syndrome | DBA | Congenital Hypoplastic AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterCompletedBeta Thalassemia Major | Congenital AnemiasUnited States
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University of KinshasaKU LeuvenCompletedSickle-Cell AnaemiaCongo, The Democratic Republic of the
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Muhimbili University of Health and Allied SciencesUniversity of Pittsburgh; Muhimbili National HospitalUnknownSickle Cell Anaemia
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Institute of Child HealthUnknown
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GlaxoSmithKlineRecruitingHematologic Diseases | Anaemia, Sickle CellUnited States
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, United Kingdom, Egypt, Canada, Saudi Arabia
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, Turkey, United Kingdom, Egypt, Saudi Arabia, Brazil, Canada, Tunisia
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited Kingdom, United States, Germany
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Makerere UniversityUnknownPreventing Stroke in Sickle Cell AnaemiaUganda
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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Masonic Cancer Center, University of MinnesotaNational Marrow Donor ProgramCompletedSickle Cell Disease | Thalassemia | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Shwachman-Diamond SyndromeUnited States
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Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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Queen Fabiola Children's University HospitalRecruitingIron Deficiency Anemia | Congenital Heart Disease in Children | Cardiac Surgical Procedures | Iron DeficienciesBelgium
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Singapore General HospitalShanghai Yueyang Integrated Medicine Hospital; Singapore Bao Zhong Tang TCM...CompletedMyelodysplastic Syndrome (MDS) | Myelofibrosis (MF) | Thalassemia Intermedia | Aplastic Anaemia (AA)Singapore
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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European Society for Blood and Marrow TransplantationCHUGAI sanofi-aventisTerminatedAplastic AnaemiaFrance, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia
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Medical Research CouncilCompletedIron Deficiency AnaemiaUnited Kingdom
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Vifor PharmaPierrel Research Europe GmbHCompletedAnaemiaAustralia, Germany, Sweden, Switzerland, Turkey
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Red-Cell Aplasia, Pure | Anemia, Diamond-BlackfanUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSteroid-refractory Diamond-Blackfan Anemia (DBA)United States
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedAplastic Anemia | Pure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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Northwell HealthTerminatedDiamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiamond Blackfan AnemiaUnited States
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Bayside HealthNational Health and Medical Research Council, Australia; Monash UniversityRecruiting
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University College, LondonCompleted
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Oriflame Cosmetics ABKarolinska InstitutetWithdrawn
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Jiangsu HengRui Medicine Co., Ltd.Completed
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Jiangsu HengRui Medicine Co., Ltd.Completed
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King Faisal Specialist Hospital & Research CenterCompleted
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Federal Scientific Clinical Centre of Pediatric...Unknown
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingAnemia, Diamond-BlackfanUnited States
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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Feinstein Institute for Medical ResearchDiamond Blackfan Anemia Foundation, Inc.Recruiting
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland