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Clinical Trials on Bardet-Biedl Syndrome
Total 34359 results
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Rhythm Pharmaceuticals, Inc.Approved for marketingObesity | Bardet-Biedl Syndrome (BBS)
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
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Marshfield Clinic Research FoundationRecruiting
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Assistance Publique - Hôpitaux de ParisRecruitingClassification, Functional Stratification and Biomarkers in Ciliopathy (CILLICORIRCM) (CILLICORIRCM)Ciliopathies | Bardet-Biedl Syndrome | Nephronophthisis | Senior-Loken Syndrome | Joubert Syndrome | Jeune SyndromeFrance
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Oslo University HospitalSykehuset Telemark; Lovisenberg Diakonale HospitalEnrolling by invitationBardet-Biedl SyndromeNorway
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National Human Genome Research Institute (NHGRI)Terminated
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University Hospital TuebingenWithdrawnVisual Impairment | Bardet-Biedl Syndrome
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University Hospital, Strasbourg, FranceCompletedBardet-Biedl Syndrome | Orphan DiseasesFrance
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Lisa M. Guay-WoodfordNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingNephronophthisis | Joubert Syndrome | Bardet Biedl Syndrome | Autosomal Recessive Polycystic Kidney Disease | Congenital Hepatic Fibrosis | Hepato/Renal Fibrocystic Disease | Meckel-Gruber Syndrome | Caroli Syndrome | Oro-Facial-Digital Syndrome Type I | Glomerulocystic Kidney DiseaseUnited States
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University Hospital, Strasbourg, FranceRecruitingBardet-Biedl Syndrome | Alström SyndromeFrance
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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Mauna Kea TechnologiesCellvizio Inc.CompletedAdenocarcinoma | Barrett's Esophagus | Barrett Esophagus | Barrett Syndrome | Barrett's SyndromeUnited States, United Kingdom, France
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Mauna Kea TechnologiesEmissary International LLC; Cellvizio Inc.CompletedAdenocarcinoma | Barrett's Esophagus | Barrett Esophagus | Barrett Syndrome | Barrett's SyndromeUnited States, France, Germany
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University Hospital, Basel, SwitzerlandRecruitingGuillain-Barre Syndrome (GBS)Switzerland
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Ning Wang, MD., PhD.Recruiting
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NHS Greater Glasgow and ClydeUniversity of GlasgowUnknownGullian Barre SyndromeUnited Kingdom
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Mansoura University Children HospitalCompletedGuillain Barre SyndromeEgypt
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Mansoura University HospitalUnknownGuillain Barre SyndromeEgypt
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Chiba UniversityJapan Agency for Medical Research and DevelopmentCompleted
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Mansoura UniversityCompletedMyasthenia Gravis | Guillain-Barre SyndromeEgypt
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Fatma Banu DemirdasCompletedFrail Elderly Syndrome | Frailty | Caregiver BurdenTurkey
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TC Erciyes UniversityCompletedCaregiver Stress Syndrome | Caregiver Burnout | ReikiTurkey
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingCaregiver Burden | Caregiver Stress Syndrome | Caregiver BurnoutUnited States
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Portsmouth Hospitals NHS TrustUniversity of PortsmouthUnknownBarrett Esophagus | Barrett Adenocarcinoma | Barrett Metaplasia | Barrett Oesophagitis With DysplasiaUnited Kingdom
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Hoffmann-La RocheChugai Pharmaceutical Co., Ltd. (Sponsor in Taiwan and Japan)Withdrawn
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Pontificia Universidad Catolica de ChileAgencia Nacional de Investigación y DesarrolloRecruitingCritical Illness | Cognitive Impairment | Caregiver Burden | Mental Health | Social Support | Resilience | Family Members | Post Intensive Care Syndrome | Family Satisfaction | Physical HealthChile
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H. Lee Moffitt Cancer Center and Research InstituteNational Cancer Institute (NCI)Recruiting
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Jordi Gol i Gurina FoundationInstitut Catala de Salut; Catalan Society of Family MedicineCompleted
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Annexon, Inc.International Centre for Diarrhoeal Disease Research, Bangladesh; ResearchPoint...CompletedGuillain-Barré SyndromeDenmark, Bangladesh
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International Centre for Diarrhoeal Disease Research...Erasmus Medical Center; GBS-CIDP Foundation International; National Institute...CompletedGuillain-Barré SyndromeBangladesh
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Nihon Pharmaceutical Co., LtdCompletedGuillain-Barré SyndromeJapan
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SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
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PersImmune, IncUniversity of California, San DiegoUnknown
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TJ Biopharma Co., Ltd.Recruiting
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI)RecruitingMyelodysplastic Syndromes (MDS)United States, Israel
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AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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The First Affiliated Hospital with Nanjing Medical...UnknownMyelodysplastic Syndromes (MDS)China
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University of North Carolina, Chapel HillNorth Carolina Department of Health and Human ServicesRecruitingCaregiver Burnout | Caregiver Stress | Care Giving Burden | Caregiver Wellbeing | Support, Family | Care BurdenUnited States
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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University of MinnesotaMayo Clinic; Minneapolis Veterans Affairs Medical Center; United States Department...RecruitingCaregiver Burden | Caregiver Stress Syndrome | Caregiver BurnoutUnited States
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Cellenkos, Inc.Withdrawn
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Japan Blood Products OrganizationCompleted
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National Taiwan University HospitalUnknownGuillain Barré SyndromeTaiwan