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Clinical Trials on Bardet-Biedl Syndrome 10
Total 122 results
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Rhythm Pharmaceuticals, Inc.Approved for marketingObesity | Bardet-Biedl Syndrome (BBS)
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
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Marshfield Clinic Research FoundationRecruiting
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Assistance Publique - Hôpitaux de ParisRecruitingClassification, Functional Stratification and Biomarkers in Ciliopathy (CILLICORIRCM) (CILLICORIRCM)Ciliopathies | Bardet-Biedl Syndrome | Nephronophthisis | Senior-Loken Syndrome | Joubert Syndrome | Jeune SyndromeFrance
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Oslo University HospitalSykehuset Telemark; Lovisenberg Diakonale HospitalEnrolling by invitationBardet-Biedl SyndromeNorway
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National Human Genome Research Institute (NHGRI)Terminated
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University Hospital TuebingenWithdrawnVisual Impairment | Bardet-Biedl Syndrome
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University Hospital, Strasbourg, FranceCompletedBardet-Biedl Syndrome | Orphan DiseasesFrance
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Lisa M. Guay-WoodfordNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingNephronophthisis | Joubert Syndrome | Bardet Biedl Syndrome | Autosomal Recessive Polycystic Kidney Disease | Congenital Hepatic Fibrosis | Hepato/Renal Fibrocystic Disease | Meckel-Gruber Syndrome | Caroli Syndrome | Oro-Facial-Digital Syndrome Type I | Glomerulocystic Kidney DiseaseUnited States
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University Hospital, Strasbourg, FranceRecruitingBardet-Biedl Syndrome | Alström SyndromeFrance
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Indonesia UniversityCompletedBurnout Syndrome | Interleukin-6 | Neutrophil-Lymphocyte Ratio | Interleukin-10Indonesia
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University of JenaUnknownSevere Sepsis or Septic Shock (ICD-10-GM, R65.0, R65.1)Germany
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Assiut UniversityCompletedMyopic LASIK Candidates With Spherical Equivalent up to - 10 DioptersEgypt
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OctapharmaCompletedPrimary and Secondary Immunodeficiency and Other Conditions Requiring Regular Administration of Octagam 5% or 10% IVIGCanada, Austria, France, Spain, United Kingdom
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingAcute Myeloid Leukemia | Recurrent Acute Myeloid Leukemia | Recurrent Myelodysplastic Syndrome | Refractory Acute Myeloid Leukemia | Refractory Myelodysplastic Syndrome | High Risk Myelodysplastic Syndrome | Blasts More Than 10 Percent of Bone Marrow Nucleated CellsUnited States
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Adult Acute Myeloid Leukemia in Remission | Blasts Under 10 Percent of Bone Marrow Nucleated Cells | Therapy-Related Myeloid NeoplasmUnited States
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Mauna Kea TechnologiesCellvizio Inc.CompletedAdenocarcinoma | Barrett's Esophagus | Barrett Esophagus | Barrett Syndrome | Barrett's SyndromeUnited States, United Kingdom, France
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Mauna Kea TechnologiesEmissary International LLC; Cellvizio Inc.CompletedAdenocarcinoma | Barrett's Esophagus | Barrett Esophagus | Barrett Syndrome | Barrett's SyndromeUnited States, France, Germany
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Boston Children's HospitalCompletedAML | ALL | Biphenotypic Leukemia | Refractory Anemia | Refractory Cytopenia With Multilineage Dysplasia | Refractory Anemia With Ringed Sideroblasts | Undifferentiated Leukemia | Ref. Cytopenia w Multilineage Dysplasia & Ringed Sideroblasts | Refractory Anemia With Excess Blasts-1 (5-10% Blasts) | Refractory... and other conditionsUnited States
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University Hospital, Basel, SwitzerlandRecruitingGuillain-Barre Syndrome (GBS)Switzerland
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Ning Wang, MD., PhD.Recruiting
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NHS Greater Glasgow and ClydeUniversity of GlasgowUnknownGullian Barre SyndromeUnited Kingdom
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Mansoura University Children HospitalCompletedGuillain Barre SyndromeEgypt
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingAcute Myeloid Leukemia | Previously Treated Myelodysplastic Syndrome | Secondary Acute Myeloid Leukemia | Untreated Adult Acute Myeloid Leukemia | Myelodysplastic Syndrome | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Blast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive and other conditionsUnited States
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University of WashingtonNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Myelodysplastic Syndrome With Excess Blasts-2 | Myeloid Neoplasm | Chronic Myelomonocytic Leukemia-2 | Blasts 10 Percent or More of Bone Marrow Nucleated... and other conditionsUnited States
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Technical University of MunichGerman Cancer Research Center; Helmholtz Munich, Munich; Charité University Hospital...RecruitingMyalgic Encephalomyelitis/Chronic Fatigue Syndrome (ME/CFS) (ICD-10 G93.3)Germany
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Mansoura University HospitalUnknownGuillain Barre SyndromeEgypt
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Chiba UniversityJapan Agency for Medical Research and DevelopmentCompleted
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingRecurrent Chronic Myelomonocytic Leukemia | Refractory Chronic Myelomonocytic Leukemia | Blasts More Than 5 Percent of Bone Marrow Nucleated Cells | Recurrent High Risk Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic Syndrome | Blasts 10-19 Percent of Bone Marrow Nucleated Cells and other conditionsUnited States
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Mansoura UniversityCompletedMyasthenia Gravis | Guillain-Barre SyndromeEgypt
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Fatma Banu DemirdasCompletedFrail Elderly Syndrome | Frailty | Caregiver BurdenTurkey
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TC Erciyes UniversityCompletedCaregiver Stress Syndrome | Caregiver Burnout | ReikiTurkey
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Assistance Publique - Hôpitaux de ParisImagine Institute; Axonal-Biostatem; CERBA laboratory; SATT; SNC Graft Versus Host...RecruitingAcute Lymphoblastic Leukemia | Acute Myeloid Leukemia in Remission | Lymphoma in Remission | Non-progressive Myeloproliferative Syndrome | Myelodysplasia With Stable Blasts is Cell Number and < 10% of Blastocysts | Acute Leukemia Biphenotypic in RemissionFrance, Germany, Belgium
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Secondary Acute Myeloid Leukemia | Myelodysplastic Syndrome | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Myeloproliferative Neoplasm | Myeloblasts 10 Percent or More of Bone Marrow Nucleated CellsUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingCaregiver Burden | Caregiver Stress Syndrome | Caregiver BurnoutUnited States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Hoffmann-La RocheChugai Pharmaceutical Co., Ltd. (Sponsor in Taiwan and Japan)Withdrawn
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Pontificia Universidad Catolica de ChileAgencia Nacional de Investigación y DesarrolloRecruitingCritical Illness | Cognitive Impairment | Caregiver Burden | Mental Health | Social Support | Resilience | Family Members | Post Intensive Care Syndrome | Family Satisfaction | Physical HealthChile
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Annexon, Inc.International Centre for Diarrhoeal Disease Research, Bangladesh; ResearchPoint...CompletedGuillain-Barré SyndromeDenmark, Bangladesh
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International Centre for Diarrhoeal Disease Research...Erasmus Medical Center; GBS-CIDP Foundation International; National Institute...CompletedGuillain-Barré SyndromeBangladesh
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Nihon Pharmaceutical Co., LtdCompletedGuillain-Barré SyndromeJapan
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Cellenkos, Inc.Withdrawn
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Japan Blood Products OrganizationCompleted
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National Taiwan University HospitalUnknownGuillain Barré SyndromeTaiwan
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University of MinnesotaMayo Clinic; Minneapolis Veterans Affairs Medical Center; United States Department...RecruitingCaregiver Burden | Caregiver Stress Syndrome | Caregiver BurnoutUnited States
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Annexon, Inc.RecruitingGuillain-Barre SyndromeBangladesh, Philippines
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Assiut UniversityUnknownGuillain-Barre Syndrome