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Clinical Trials on Céroïdes-lipofuscinoses neuronales
Total 72 results
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University of RochesterRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3 | Neuronal Ceroid Lipofuscinosis CLN5 | Neuronal Ceroid Lipofuscinosis CLN1 | Neuronal Ceroid Lipofuscinosis CLN2 | Neuronal Ceroid Lipofuscinosis CLN7 | Neuronal Ceroid Lipofuscinosis... and other conditionsUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingBatten Disease | Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)United States
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Amicus TherapeuticsTerminatedBatten Disease | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3United States
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Amicus TherapeuticsCompletedVariant Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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Weill Medical College of Cornell UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityTerminatedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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REGENXBIO Inc.WithdrawnLate-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky DiseaseUnited States, Italy, Germany, United Kingdom
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)CompletedBatten Disease | Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Neurogene Inc.RecruitingNeuronal Ceroid Lipofuscinosis CLN5United States, United Kingdom
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Polaryx Therapeutics, Inc.Not yet recruitingJuvenile Neuronal Ceroid Lipofuscinosis
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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University of RochesterBatten Disease Support and Research Assocation (BDSRA)CompletedJuvenile Neuronal Ceroid LipofuscinosisUnited States
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StemCells, Inc.CompletedNeuronal Ceroid LipofuscinosisUnited States
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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REGENXBIO Inc.WithdrawnNeuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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IRCCS Fondazione Stella MarisCompletedNeuronal Ceroid-LipofuscinosesItaly
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Neurogene Inc.RecruitingCeroid Lipofuscinosis, Neuronal 5United States
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David L Rogers, MDActive, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United States
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Jessica ScherrBioMarin PharmaceuticalEnrolling by invitationBatten Disease | Neuronal Ceroid-Lipofuscinoses | CLN2United States
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Eunice Kennedy Shriver National Institute of Child...CompletedInfantile Neronal Ceroid LipofuscinosisUnited States
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StemCells, Inc.WithdrawnNeuronal Ceroid LipofuscinosisUnited States
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Nationwide Children's HospitalMassachusetts General HospitalCompletedNeuronal Ceroid Lipofuscinosis | Batten's DiseaseUnited States
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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Emily de los ReyesRecruitingBatten Disease | CLN6United States
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late-Infantile Neuronal Ceroid Lipfuscinosis
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Universitätsklinikum Hamburg-EppendorfRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | CLN1 Disease | CLN2 Disease | CLN3 Disease | CLN4 Disease | CLN5 Disease | CLN6 Disease | CLN7 Disease | CLN8 Disease | CLN10 Disease | CLN11 Disease | CLN12 Disease | CLN13 Disease | CLN14 DiseaseGermany
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
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Amicus TherapeuticsActive, not recruiting
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Amicus TherapeuticsActive, not recruitingBatten Disease | CLN6United States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Rupert LanzenbergerUnknown
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Medical University of ViennaUnknownNeuronal Plasticity | SsriAustria
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University of Massachusetts, WorcesterCompleted
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Fondation Ophtalmologique Adolphe de RothschildRecruiting
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Fondation Ophtalmologique Adolphe de RothschildRecruitingBenign Neuronal DeseaseFrance
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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Hadassah Medical OrganizationUnknownMapping the Limbic STN Using Neuronal ResponsesIsrael
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The Catholic University of KoreaRecruitingPostural Balance | Elderly Population | Neuronal PlasticityKorea, Republic of
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Universiteit LeidenRecruitingAging | Magnetic Resonance Imaging | Motor Activity | Music | Neuronal PlasticityNetherlands
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Azienda Socio Sanitaria Territoriale degli Spedali...CompletedTranscranial Magnetic Stimulation | Neuronal Plasticity | Electromagnetic Fields
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Centre Hospitalier Universitaire de Saint EtienneCompletedMagnetic Resonance Imaging | Neuronal ActivityFrance
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Centre Hospitalier Universitaire de Saint EtienneUniversity Hospital of Saint-EtienneCompleted
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Nadir Hastalıkları Araştırma DerneğiRecruitingNeuronal Ceroid Lipofuxinosis Type2 (CLN2)Turkey
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First Affiliated Hospital of Zhejiang UniversityZhejiang University Interdisciplinary Institute of Neuroscience and TechnologyUnknownNeuronal Intranuclear Inclusion DiseaseChina