- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital FVII Deficiency
Total 17483 results
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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Novo Nordisk A/SCompletedObservational Study on Safety and Efficacy of NovoSeven® in Subjects With Congenital FVII DeficiencyCongenital Bleeding Disorder | Congenital FVII DeficiencyJapan
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CSL BehringCompletedCongenital Coagulation Factor VII DeficiencyNetherlands, Norway
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseGermany
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Baxalta now part of ShireCompletedHemophilia A | Congenital Factor VIII (FVIII) DeficiencyUnited Kingdom, France, Germany, Hungary
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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Centers for Disease Control and PreventionCompleted
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QOL Medical, LLCCompletedCongenital Sucrase-Isomaltase DeficiencyUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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National Cardiovascular Center Harapan Kita Hospital...UnknownCardiopulmonary Bypass | Congenital Heart Disease | Thiamine DeficiencyIndonesia
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Children's Hospital of Eastern OntarioMcGill University; Ottawa Hospital Research Institute; The Ottawa Hospital; Children...CompletedVitamin D Deficiency | Heart Defects, Congenital | Thoracic Surgery | Pediatric DisordersCanada
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Queen Fabiola Children's University HospitalRecruitingIron Deficiency Anemia | Congenital Heart Disease in Children | Cardiac Surgical Procedures | Iron DeficienciesBelgium
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University of MinnesotaRecruiting
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Northwestern UniversityCompletedCongenital Leptin Deficiency (Disorder)United States
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QOL Medical, LLCJohns Hopkins University; Massachusetts General Hospital; Baylor College of Medicine and other collaboratorsCompletedCongenital Sucrase-isomaltase Deficiency (CSID)United States
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Maggie's Pearl, LLCActive, not recruitingPmm2-CDG | Phosphomannomutase 2 Deficiency | Phosphomannomutase 2 Congenital Disorder of Glycosylation | Phosphomannomutase II Congenital Disorder of Glycosylation | Phosphomannomutase II DeficiencyUnited States
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PfizerCompletedFactor VIII Deficiency, Congenital | Hemophilia A, Congenital | Factor 8 Deficiency, Congenital | Autosomal Hemophilia A | Classic Hemophilia
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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Universitas Sumatera UtaraNot yet recruitingAtrial Septal Defect | Congenital Heart Disease | Patent Ductus Arteriosus | Ventricular Septal Defect | Thiamine DeficiencyIndonesia
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QOL Medical, LLCRecruitingCongenital Sucrase-Isomaltase Deficiency | CSID | Sucrase Isomaltase DeficiencyUnited States
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University of Alabama at BirminghamCompletedFolic Acid Deficiency | Neural Tube Defects | FortificationUnited States
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OctapharmaRecruitingCongenital Antithrombin DeficiencySpain, United States, Italy, France, Hungary, Austria, Germany, United Kingdom
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Kyowa Hakko Kirin UK, Ltd.CompletedCongenital Antithrombin DeficiencyFrance, Germany, Italy, Sweden, United Kingdom
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AryoGen Pharmed Co.CompletedFactor VII DeficiencyIran, Islamic Republic of
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Cure CMDCongenital Muscle Disease International RegistrWithdrawnLAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)United States
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Laboratoire français de Fractionnement et de BiotechnologiesCompletedHypofibrinogenemia, Congenital | Afibrinogenemia, CongenitalFrance, Lebanon, Morocco, Turkey
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The University of Hong KongQueen Mary Hospital, Hong KongNot yet recruitingThalassemia | Folic Acid Deficiency Anemia
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Novo Nordisk A/SEnrolling by invitationCongenital Bleeding Disorder | Congenital FXIII DeficiencyJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencySpain, United States, Canada, Italy, United Kingdom, Hungary
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom, Israel, United States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, United Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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University of L'AquilaTRIB s.r.l.Completed
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Hydrocephalus and Neuroscience InstituteCompletedFolic Acid Deficiency | Neural Tube Defects | Spina Bifida | Anencephaly-Spina BifidaUnited States
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BiotestAccovion GmbH; ICON plc; SYNLAB Analytics and Services Germany GmbH; Phoenix Clinical... and other collaboratorsCompletedCongenital Afibrinogenemia | Congenital HypofibrinogenemiaBulgaria, Egypt, Germany, Lebanon, Tunisia
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Rigshospitalet, DenmarkUltragenyx Pharmaceutical IncCompletedTarui Disease | Debrancher Deficiency | GYG1 DEFICIENCYDenmark
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University Hospital, Clermont-FerrandTerminatedVisual Deficiency | Congenital Blindness | Acquired BlindnessFrance
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Prometic Biotherapeutics, Inc.CompletedHypoplasminogenemia | Congenital Plasminogen DeficiencyUnited States, Norway
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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University Hospital, GrenobleNot yet recruitingArthrogryposis Multiplex Congenita (AMC)
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University Hospital, GrenobleRecruitingArthrogryposis Multiplex Congenita (AMC)France
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Steno Diabetes Center CopenhagenThe Novo Nordisk Foundation Center for Basic Metabolic Research; Department... and other collaboratorsCompletedDiabetes Mellitus, Type 2 | Metabolic Disease | Sucrase Isomaltase Deficiency | Sucrose Intolerance CongenitalGreenland
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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Eva Morava-KoziczChildren's Hospital of Philadelphia; Seattle Children's HospitalNot yet recruiting
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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Agios Pharmaceuticals, Inc.TerminatedAnemia | Anemia, Hemolytic | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency AnemiaUnited States, United Kingdom, Italy, Spain, Netherlands