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Clinical Trials on Distal Hereditary Motor Neuronopathy Type VI
Total 181 results
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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Academisch Medisch Centrum - Universiteit van Amsterdam...CompletedCharcot-Marie-Tooth Disease | Hereditary Motor and Sensory NeuropathiesNetherlands
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University of IowaUniversity of South Florida; National Institute of Neurological Disorders and... and other collaboratorsCompletedCharcot Marie Tooth Disease | Inherited Peripheral NeuropathyUnited States, United Kingdom
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Massachusetts General HospitalCompletedHereditary Sensory and Autonomic Neuropathy Type IUnited States
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Oslo University HospitalUniversity of Oslo; Norwegian National Advisory Unit on Rare Disorders (NKSD); Foreningen for MuskelsykeEnrolling by invitationHereditary Motor and Sensory Neuropathy | Polyneuropathies | Charcot-Marie-ToothNorway
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Columbia UniversityUniversity of North Carolina, Chapel HillTerminated
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First Affiliated Hospital of Fujian Medical UniversityRecruiting
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Xuanwu Hospital, BeijingRecruitingGait | Motor FunctionChina
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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Nationwide Children's HospitalSuspendedCharcot-Marie-Tooth Neuropathy Type 1AUnited States
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IRCCS Fondazione Stella MarisCompletedHereditary Spastic Paraplegia | Spastic Paraplegia Type 11Italy
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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Spaulding Rehabilitation HospitalMassachusetts General HospitalWithdrawnHereditary Spastic Paraplegia
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University College, LondonRecruitingHereditary Sensory Neuropathy Type IUnited Kingdom
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St George's, University of LondonUniversity College London HospitalsUnknownPeripheral Neuropathy | CMT - Charcot-Marie-Tooth Disease | Hereditary Peripheral Neuropathy | CMT1AUnited Kingdom
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University Hospital TuebingenCompleted
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Dr. Rebecca SchuleGerman Federal Ministry of Education and Research; German Center for Neurodegenerative...RecruitingHereditary Spastic ParaplegiaAustria, Germany, Italy
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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University Hospital TuebingenCompleted
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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University Hospital TuebingenRecruitingHereditary Spastic Paraplegia | Hereditary, Spastic Paraplegia, Autosomal DominantGermany
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Assistance Publique - Hôpitaux de ParisCompletedHereditary Spastic ParaplegiaFrance
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European University of LefkeCompletedHereditary Spastic ParaplegiaCyprus
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Radboud University Medical CenterJacques and Gloria Gossweiler FoundationCompletedHereditary Spastic Paraplegia | Strumpell DiseaseNetherlands
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National Institute of Neurological Disorders and...TerminatedHereditary Spastic ParaplegiaUnited States
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University of Campinas, BrazilConselho Nacional de Desenvolvimento Científico e Tecnológico; Cristália Produtos...CompletedHereditary Spastic ParaplegiaBrazil
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States
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Central Hospital, Nancy, FranceRecruiting
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Cairo UniversityRecruitingEntrapment NeuropathiesEgypt
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Neurogene Inc.TerminatedCharcot-Marie-Tooth Disease | Hereditary Motor and Sensory Neuropathy IVUnited States
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Institut National de la Santé Et de la Recherche...CompletedSpastic Paraplegia, HereditaryFrance
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Istituto Ortopedico RizzoliCompletedEntrapment Neuropathy, Carpal Tunnel | Compression Neuropathy, Carpal Tunnel | Median Neuropathy, Carpal TunnelItaly
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MedDay Pharmaceuticals SACompletedCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyneuropathy | Charcot-Marie-Tooth Disease Type 1A | Charcot-Marie-Tooth Disease, Type 1B | Anti-MAG NeuropathyFrance
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Liminal BioSciences Ltd.TerminatedAlström SyndromeUnited Kingdom
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Boston Children's HospitalBoston Children's Hospital - Children's Rare Disease Cohorts InitiativeRecruitingMovement Disorders | Neurodegenerative Diseases | Motor Neuron Disease | Spasticity, Muscle | Pediatric Disorder | Hereditary Spastic ParaplegiaUnited States
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Elpida Therapeutics SPCNot yet recruitingNeuromuscular Diseases | Peripheral Neuropathy | Neuro-Degenerative Disease
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Guy Hains ChiropractorCompletedCompression Neuropathy, Carpal TunnelCanada
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National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Hereditary Spastic ParaplegiaUnited States
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Federal University of São PauloCompletedCarpal Tunnel Syndrome | Compression Neuropathy, Carpal Tunnel | Median Neuropathy, Carpal TunnelBrazil
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Afyonkarahisar Health Sciences UniversityCompletedMusculoskeletal Diseases | Carpal Tunnel Syndrome | Median Neuropathy | Entrapment NeuropathyTurkey
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Christine M. Kleinert Institute for Hand and MicrosurgeryUnknownMedian Nerve CompressionUnited States
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Pacira CryoTech, Inc., a wholly owned subsidiary...CompletedEntrapment NeuropathyUnited States
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Aarhus University HospitalUniversity of Southern DenmarkCompletedDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Diabetic Polyneuropathy | Hereditary Axonal Neuropathy | Hereditary Demyelinated Neuropathy | Polyneuropathy, Inflammatory Demyelinating, ChronicDenmark, Germany
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Nemours Children's ClinicTerminated
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University Hospital, Strasbourg, FranceTerminated