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Clinical Trials on Duchenne Muscular Dystrophy
Total 50281 results
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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University of BernUniversity Hospital Inselspital, Berne; University of Lausanne Hospitals; University... and other collaboratorsRecruitingCongenital Muscular Dystrophy | SMA | DMD | BMD | IMDSwitzerland
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Assistance Publique - Hôpitaux de ParisRecruitingLimb Girdle Muscular DystrophiesFrance
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Radboud University Medical CenterRecruitingSELENON-related Myopathy | LAMA2-related Muscular DystrophyNetherlands
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University Hospital, CaenUniversity Hospital, Rouen; Centre Hospitalier Universitaire, Amiens; University... and other collaboratorsTerminatedMuscular Dystrophy, Oculopharyngeal | PtosisFrance
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Lupin Ltd.WithdrawnMyotonic Dystrophy Type 1 and Type 2
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Nationwide Children's HospitalRecruiting
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Istanbul University - Cerrahpasa (IUC)CompletedFacio-Scapulo-Humeral DystrophyTurkey
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Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Rigshospitalet, DenmarkCompletedSpinal Muscular Atrophy | Merosin Deficient Congenital Muscular DystrophyDenmark
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Murdoch Childrens Research InstituteCompletedFacio-Scapulo-Humeral Dystrophy | FSHD2 | FSHD1Australia
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Medical University of BialystokUnknownIncrease Muscle Strength in Patients With Muscular DystrophyPoland
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMDCompletedCongenital Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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University Hospital, LilleRecruitingMacular Degeneration | Cone Dystrophy | Cone Rod Dystrophy | Retinal Dystrophy, Cone-RodFrance
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Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon...Recruiting
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Istituto Superiore di SanitàFondazione G.B. Bietti, IRCCS; Ospedale Pediatrico Bambin GesùRecruitingRetinitis Pigmentosa | Macular Dystrophy | Inherited Retinal DystrophyItaly
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Radboud University Medical CenterCompletedMDC1A | SELENON-related MyopathyNetherlands
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CHU de ReimsCompletedMyotonic Dystrophy Type 1 (DM1)France
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IRCCS San Camillo, Venezia, ItalyCompletedMyotonic Dystrophy Type 1 (DM1)
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Fondazione G.B. Bietti, IRCCSRecruitingMacular Edema | Inherited Retinal Dystrophy | Laser RetinopathyItaly
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
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LMU KlinikumRecruitingMyasthenia Gravis | Myotonic Dystrophy | Inclusion Body Myositis | Facioscapulohumeral Muscular Dystrophies | The Falls Efficacy Scale International | The Morse Fall ScaleGermany
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Pitié-Salpêtrière HospitalRecruitingLaminopathies | EmerinopathiesFrance
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Indiana University School of MedicineMuscular Dystrophy AssociationCompletedMuscular Dystrophy | Arrhythmia | Sudden Cardiac DeathUnited States
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CHABiotech CO., LtdCompletedStargardt's Macular DystrophyKorea, Republic of
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Astellas Institute for Regenerative MedicineCompleted
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Astellas Institute for Regenerative MedicineCompleted
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ARTHEx Biotech S.L.Not yet recruitingMyotonic Dystrophy 1
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Huashan HospitalEnrolling by invitation
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National Eye Institute (NEI)CompletedMacular DegenerationUnited States
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McMaster UniversityNot yet recruiting
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Centre Hospitalier Universitaire de NiceWithdrawn
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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University of RochesterCompletedMyotonic DystrophyUnited States