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Clinical Trials on Familial LCAT Deficiency
Total 10114 results
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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University of PennsylvaniaSuspendedLipid Metabolism, Inborn Errors | Cholesterol, HDL | Tangier Disease | LCAT Deficiency | Cholesteryl Ester Transfer Protein (CETP) DeficiencyUnited States
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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National Institute of Allergy and Infectious Diseases...Circassia LimitedCompletedCat Allergy | Cat HypersensitivityCanada
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Opus Genetics, IncRecruiting
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Hadassah Medical OrganizationUnknownNatural Killer Cell Deficiency, Familial IsolatedIsrael
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Catabasis PharmaceuticalsCompletedHypertriglyceridemia | Hyperlipoproteinemia Type I | Lipoprotein Lipase Deficiency, Familial | Chylomicronemia, FamilialCanada
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National Institute of Allergy and Infectious Diseases...Immune Tolerance Network (ITN)CompletedCat Allergy | Cat HypersensitivityUnited States
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National Institute of Dental and Craniofacial Research...RecruitingOsteomalacia | Tumor Induced Osteomalcia | Familial Tumoral CalcinosisUnited States
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyCompletedFamilial Lipoprotein Lipase DeficiencyCanada
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UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
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Amsterdam Molecular TherapeuticsInternational Antiviral Therapy Evaluation CenterUnknownFamilial Lipoprotein Lipase DeficiencyCanada
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Assistance Publique Hopitaux De MarseilleNot yet recruiting
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Tel-Aviv Sourasky Medical CenterUnknownCat-scratch Disease | Bartonella InfectionsIsrael
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Assistance Publique - Hôpitaux de ParisRecruitingX-linked HypophosphatemiaFrance
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Wuerzburg University HospitalKyowa Kirin, Inc.Completed
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Hospices Civils de LyonCompleted
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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Peking Union Medical College HospitalUnknownX-linked HypophosphatemiaChina
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University of AarhusAarhus University Hospital; University of East Anglia; Kolding SygehusCompleted
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Zeria PharmaceuticalCompletedPrimary Hypophosphatemic RicketsJapan
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Japan, Ireland, United Kingdom, France, Italy
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaNetherlands, United States, United Kingdom, France
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked HypophosphatemiaUnited Kingdom, France, Ireland, Italy
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Kyowa Hakko Kirin Pharma, Inc.Completed
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Johns Hopkins UniversityNational Institute of Allergy and Infectious Diseases (NIAID); Genentech, Inc.CompletedCat AllergyUnited States
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Circassia LimitedCetero Research, San Antonio; Adiga Life Sciences, Inc.Completed
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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Hospices Civils de LyonCompletedHypophosphatemic RicketsFrance
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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Haukeland University HospitalUnknown
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Thomas KuendigCompletedCat Dander AllergySwitzerland
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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Children's Mercy Hospital Kansas CityWithdrawn
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Kyowa Kirin Pharmaceutical Development LtdRecruitingX-Linked HypophosphatemiaFrance, Netherlands, United Kingdom
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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Circassia LimitedAdiga Life Sciences, Inc.Completed
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ALK-Abelló A/SCetero Research, San AntonioCompleted
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University of ZurichImVision GmbH, HannoverCompleted
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National Medical Research Center for Therapy and...Moscow State University of Medicine and DentistryRecruitingMedication Adherence | Adherence, Medication | Treatment Adherence | Familial Hypercholesterolemia | Motivational Interviewing | Adherence, Patient | Treatment Adherence and Compliance | Patient Compliance | Adherence | Hypercholesterolemia, Familial | Patient Adherence | Hypercholesterolemia, Autosomal Dominant and other conditionsRussian Federation
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada, France, Germany
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of