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Clinical Trials on Friedreich Ataxia
Total 430 results
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Children's Hospital of PhiladelphiaUniversity of California, Los Angeles; University of FloridaCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Vidara Therapeutics Research LtdCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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University Hospital, MontpellierNeurogenetic department, CHU Bordeaux; Genetic Department , CHU Montpellier-France and other collaboratorsUnknown
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IpsenCompleted
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Ralitza GavrilovaCardero Therapeutics, Inc.Completed
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Azienda Policlinico Umberto ICompleted
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University of Colorado, DenverCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, Germany, United Kingdom
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Federico II UniversityFriedreich's Ataxia Research Alliance; Associazione Italiana per la lotta alle...Completed
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University of South FloridaPfizer; Friedreich's Ataxia Research AllianceTerminatedFriedreich's AtaxiaUnited States
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National Human Genome Research Institute (NHGRI)CompletedFriedreich AtaxiaUnited States
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National Institute of Neurological Disorders and...CompletedFriedreich AtaxiaUnited States
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German Center for Neurodegenerative Diseases (DZNE)McMaster University; Sorbonne UniversityRecruitingFriedreich AtaxiaAustria, Germany, France
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Weill Medical College of Cornell UniversityRecruitingFriedreich's AtaxiaUnited States
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University of PittsburghFriedreich's Ataxia Research AllianceCompleted
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Murdoch Childrens Research InstituteFriedreich's Ataxia Research AllianceCompleted
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Larimar Therapeutics, Inc.Clinilabs, Inc.CompletedHealthy Volunteers | Friedreich AtaxiaUnited States
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research CenterCompletedFriedreich AtaxiaUnited States
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Adverum Biotechnologies, Inc.Adverum Biotechnologies SAS, a wholly owned subsidiary of Adverum Biotechnologies...CompletedFriedreich's AtaxiaFrance
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CENTOGENE GmbH RostockEnrolling by invitationHereditary Diseases | FXN Gene | FRDALebanon
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Lexeo TherapeuticsRecruitingFriedreich Ataxia | Cardiomyopathy, SecondaryUnited States, Canada
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University of FloridaAcorda TherapeuticsCompletedSpinocerebellar Ataxias Type 1 | Spinocerebellar Ataxias Type 2 | Spinocerebellar Ataxias Type 3 | Spinocerebellar Ataxias Type 6United States
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Imperial College LondonUnknown
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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Azienda Socio Sanitaria Territoriale degli Spedali...CompletedAtaxia | Multiple System Atrophy | Spinocerebellar Ataxias | Spinocerebellar Ataxia 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Ataxia With Oculomotor Apraxia | CANVASItaly
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Hasan Kalyoncu UniversityCompleted
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Cairo UniversityCompletedCore Stability | Ataxic Cerebral Palsied Children | Balance and Coordination | Severity of the AtaxiaEgypt
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Cadent TherapeuticsWithdrawnSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8 | Spinocerebellar Ataxia Type 17 | ARCA1 - Autosomal Recessive...United States
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Biohaven Pharmaceuticals, Inc.Active, not recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8United States, China
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Assistance Publique - Hôpitaux de ParisCompletedSpinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia, Autosomal Recessive 3 | Episodic Ataxia, Type 7France
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Assistance Publique - Hôpitaux de ParisCompletedCongenital Cerebellar Ataxias | Early-onset Cerebellar AtaxiasFrance
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Sclnow Biotechnology Co., Ltd.Not yet recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6
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University of California, Los AngelesActive, not recruitingSpinocerebellar Ataxias | Spinocerebellar Ataxia 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | MSA-CUnited States
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Institut National de la Santé Et de la Recherche...Biogen; Ionis Pharmaceuticals, Inc.CompletedSpinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 7France
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Federico II UniversityCompletedSPINOCEREBELLAR ATAXIA 2Italy
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University of PittsburghCompletedPulmonary Hypertension | Friedreich Ataxia | Iron-sulfur Cluster DeficiencyUnited States
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Teachers College, Columbia UniversityActive, not recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 7United States
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University of FloridaUniversity of California, Los Angeles; National Ataxia FoundationRecruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6United States
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Biohaven Pharmaceuticals, Inc.Active, not recruitingSpinocerebellar Ataxias | Spinocerebellar Ataxia Genotype Type 1 | Spinocerebellar Ataxia Genotype Type 2 | Spinocerebellar Ataxia Genotype Type 3 | Spinocerebellar Ataxia Genotype Type 6 | Spinocerebellar Ataxia Genotype Type 7 | Spinocerebellar Ataxia Genotype Type 8 | Spinocerebellar Ataxia Genotype...United States
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Chang Gung UniversityRecruiting
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University of CagliariAngela Sanna; Micaela Porta; Paolo Tacconi; Chiara PauCompletedSpinocerebellar AtaxiasItaly
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National University of MalaysiaRadboud University Medical CenterRecruiting
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The Methodist Hospital Research InstituteJohns Hopkins University; University of Colorado, Denver; University of Pennsylvania and other collaboratorsActive, not recruitingSpinocerebellar Ataxia 3 | Spinocerebellar Ataxia Type 1United States