Example: Heart Attack
Clinical Trials on Genetic Diseases, Inborn
Total 9908 results
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NCT04564378RecruitingConditions: Fuchs Dystrophy
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NCT04564495RecruitingConditions: Neurologic Disorder; Stroke; Spinal Cord Injuries; Cerebral Palsy; Hemiplegia; Hemiparesis; Multiple Sclerosis; Parkinson Disease; Trauma, Brain; Transverse Myelitis; Friedreich Ataxia
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NCT04564755Temporarily not availableConditions: Atopic Dermatitis
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NCT04565236Not yet recruitingConditions: Hemophilia A
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NCT04561765Not yet recruitingConditions: Neurofibromatosis 1; Chronic Pain
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NCT04561973RecruitingConditions: Pain; Cystic Fibrosis
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NCT04562116Not yet recruitingConditions: Atopic Dermatitis
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NCT04563286RecruitingConditions: Transthyretin Amyloidosis
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NCT04563520Not yet recruitingConditions: Hemophilia A
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NCT04560933RecruitingConditions: Hemophilia A
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NCT04561466RecruitingConditions: Safety Issues; Efficacy, Self
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NCT04558736Not yet recruitingConditions: Aplastic Anemia; Bone Marrow Failure Syndrome; Dyskeratosis Congenita
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NCT04558983RecruitingConditions: Retinitis Pigmentosa
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NCT04556162RecruitingConditions: Salt; Deficit (or Low); Cystic Fibrosis
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NCT04556461Not yet recruitingConditions: Atopic Dermatitis
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NCT04556487Not yet recruitingConditions: Developmental Delay Disorder; Genetic Disease; Metabolic Disease; Congenital Disorders; Musculoskeletal Diseases
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NCT04556500Not yet recruitingConditions: Musculoskeletal Diseases; Genetic Disease; Metabolic Disease; Delays Developmental
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NCT04556656Not yet recruitingConditions: Huntington Disease
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NCT04557319CompletedConditions: Hereditary Angioedema
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NCT04554940Not yet recruitingConditions: Achondroplasia
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NCT04555486Not yet recruitingConditions: Primary Hyperoxaluria Type 3
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NCT04552405CompletedConditions: Familial Adenomatous Polyposis (FAP)
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NCT04552691AvailableConditions: Fabry Disease
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NCT04553094Not yet recruitingConditions: Marfan Syndrome
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NCT04553224CompletedConditions: Atopic Dermatitis
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NCT04553419RecruitingConditions: Cystic Fibrosis
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NCT04550988Not yet recruitingConditions: Sonography; Haemophilia
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NCT04551170RecruitingConditions: Pseudohypoparathyroidism; Albright Hereditary Osteodystrophy; Pseudohypoparathyroidism Type 1a
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NCT04548791Not yet recruitingConditions: Factor VII Deficiency; Glanzmann Thrombasthenia; Hemophilia A With Inhibitor
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NCT04548921RecruitingConditions: FXN Gene; FRDA; Hereditary Diseases
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NCT04549077RecruitingConditions: Cystic Fibrosis
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NCT04549792Not yet recruitingConditions: Ichthyosis
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NCT04546399Not yet recruitingConditions: Down Syndrome; Recurrent B Acute Lymphoblastic Leukemia
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NCT04547140Not yet recruitingConditions: COVID-19
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NCT04548284Not yet recruitingConditions: Thyroid Associated Ophthalmopathy
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NCT04545515Not yet recruitingConditions: Cystic Fibrosis
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NCT04545554Not yet recruitingConditions: Osteogenesis Imperfecta
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NCT04543929RecruitingConditions: Cystic Fibrosis
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NCT04544410RecruitingConditions: Congenital Adrenal Hyperplasia
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NCT04544501Enrolling by invitationConditions: Hereditary Breast and Ovarian Cancer Syndrome
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NCT04544943Not yet recruitingConditions: Atopic Dermatitis
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NCT04541628RecruitingConditions: Hemophilia A
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NCT04541654Not yet recruitingConditions: Li-Fraumeni Syndrome; TP53 Gene Mutation; Hereditary Cancer Syndrome; Clonal Hematopoiesis; Mosaicism
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NCT04541875Not yet recruitingConditions: Cystic Fibrosis; Hemophilia A; Hemophilia B; Idiopathic Pulmonary Fibrosis; Myasthenia Gravis; Sickle Cell Disease
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NCT04542590Not yet recruitingConditions: Primary Hyperoxaluria Type 3
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NCT04539340RecruitingA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy VolunteersConditions: Mucopolysaccharidosis Type II; Metabolic Diseases
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NCT04539535CompletedConditions: Down Syndrome
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NCT04539639Not yet recruitingClinical Study of Jieketinib in the Treatment of Patients With Moderate and Severe Atopic DermatitisConditions: Atopic Dermatitis
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NCT04536688RecruitingConditions: Polycystic Kidney Disease, Autosomal Dominant
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NCT04536792RecruitingConditions: Healthy Volunteers; Anemia, Sickle Cell