Example: Heart Attack
Clinical Trials on Genetic Diseases, X-Linked
Total 1117 results
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NCT04157595Enrolling by invitationConditions: X-Linked Genetic Diseases; Autosomal Recessive Disorder
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NCT00359411CompletedConditions: X-Linked Lymphoproliferative Disease; Lymphoproliferative Disease; Genetic Diseases, X-Linked
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NCT00100230CompletedConditions: Retinitis Pigmentosa; X-linked Genetic Diseases
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NCT00001405RecruitingConditions: Granuloma; Granulomatous Disease, Chronic; Leukocyte Disease; Genetic Disease, X-Linked; Genetic Disease, Inborn
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NCT03512314RecruitingConditions: XIAP Deficiency; NLRC4-MAS
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NCT03113760RecruitingConditions: NLRC4-MAS; XIAP Deficiency
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NCT03321604TerminatedConditions: ESRD; Fabry Disease; Rare Diseases; Kidney Diseases; End Stage Renal Disease; Genetic Diseases, X-Linked
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NCT03275714CompletedConditions: Bipolar Affective Disorder
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NCT00397605WithdrawnConditions: Bipolar Affective Disorder
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NCT03862950RecruitingConditions: Fragile X Syndrome; Fragile X Mental Retardation Syndrome; Mental Retardation, X-Linked; Genetic Diseases, X-Linked; Trinucleotide Repeat Expansion; Fra(X) Syndrome; Intellectual Disability; FXS; Neurobehavioral Manifestations; Sex Chromosome Disorders
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NCT03479476RecruitingConditions: Fragile X Syndrome; Fragile X Mental Retardation Syndrome; Mental Retardation, X Linked; Genetic Diseases, X-Linked; Trinucleotide Repeat Expansion; Fra(X) Syndrome; Intellectual Disability; FXS; Neurobehavioral Manifestations; Sex Chromosome Disorders
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NCT03876301Active, not recruitingConditions: Blood Coagulation Disorder; Blood Coagulation Disorders, Inherited; Coagulation Protein Disorders; Hemophilia A; Genetic Diseases, Inborn; Genetic Diseases, X-Linked; Hematologic Diseases; Hemorrhagic Disorders; Factor VIII Deficiency
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NCT03734588Active, not recruitingConditions: Adeno-Associated Virus (AAV); Blood Coagulation Disorder; Blood Coagulation Disorders, Inherited; Coagulation Protein Disorders; Factor VIII (FVIII); Factor VIII (FVIII) Deficiency; Factor VIII (FVIII) Gene; Factor VIII (FVIII) Protein; Genetic Diseases, Inborn; Genetic Diseases, X-Linked; Gene Therapy; Gene Transfer; Hematologic Diseases; Hemorrhagic Disorders; Recombinant; Vector; Inhibitors
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NCT03406780CompletedConditions: Muscular Dystrophies; Muscular Dystrophy, Duchenne; Muscular Disorders, Atrophic; Muscular Diseases; Neuromuscular Diseases; Nervous System Diseases; Genetic Diseases, X-Linked; Genetic Diseases, Inborn
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NCT03179631Active, not recruitingConditions: Muscular Dystrophy, Duchenne; Muscular Dystrophies; Muscular Disorders, Atrophic; Muscular Diseases; Musculoskeletal Disease; Neuromuscular Diseases; Nervous System Diseases; Genetic Diseases, X-Linked; Genetic Diseases, Inborn
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NCT02090959TerminatedConditions: Muscular Dystrophy, Duchenne; Muscular Dystrophies; Muscular Disorders, Atrophic; Muscular Diseases; Musculoskeletal Diseases; Neuromuscular Diseases; Nervous System Diseases; Genetic Diseases, X-Linked; Genetic Diseases, Inborn
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NCT01826487CompletedPhase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)Conditions: Muscular Dystrophy, Duchenne; Muscular Dystrophies; Muscular Disorders, Atrophic; Muscular Diseases; Musculoskeletal Diseases; Neuromuscular Diseases; Nervous System Diseases; Genetic Diseases, X-Linked; Genetic Diseases, Inborn
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NCT03019458CompletedConditions: X-Linked Dystonia Parkinsonism
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NCT04168697Not yet recruitingConditions: Bipolar Affective Disorder, Currently in Remission; Bipolar Disorder I; Bipolar Disorder II
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NCT03249857CompletedConditions: Bipolar Affective Disorder
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NCT00474357Unknown statusConditions: Bipolar Affective Disorder
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NCT01108068CompletedConditions: Osteoporosis Pseudoglioma
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NCT02642653CompletedConditions: Fragile X Syndrome; Genetic Diseases
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NCT04687007Not yet recruitingConditions: X-linked Adrenoleukodystrophy
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NCT04675749RecruitingConditions: X-linked Adrenoleukodystrophy