- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Glycogenesis 2 Acid Maltase Deficiency
Total 349 results
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States, Israel, France, United Kingdom
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
-
Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
-
Genzyme, a Sanofi CompanyTerminatedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Israel
-
Genzyme, a Sanofi CompanyCompletedGlycogenesis 2 Acid Maltase Deficiency | Pompe Disease (Late-Onset) | Glycogen Storage Disease Type II (GSD II)United States, Netherlands, United Kingdom, Germany
-
Genzyme, a Sanofi CompanyCompletedGlycogenesis 2 Acid Maltase Deficiency | Pompe Disease (Late-Onset) | Glycogen Storage Disease Type II (GSD II)France
-
Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
-
Genzyme, a Sanofi CompanyRecruitingPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Glycogenesis 2 Acid Maltase DeficiencyCroatia, United States, Italy, Belgium, Czechia
-
Genzyme, a Sanofi CompanyTerminatedGlycogenosis 2 | Glycogen Storage Disease Type II (GSD II) | Acid Maltase Deficiency | Pompe Disease (Infantile-Onset)United States, Taiwan, Germany
-
Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2Netherlands
-
Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2France
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
-
AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
-
University Hospital, MontpellierRecruitingAromatic L-Amino Acid Decarboxylase DeficiencyFrance
-
Maria Luz Couce PicoFundación Ramón DomínguezWithdrawnLong-chain Fatty Acid Transport DeficiencySpain
-
Shanghai Jiao Tong University School of MedicineShanghai Vitalgen BioPharma Co., Ltd.RecruitingAromatic L-amino Acid Decarboxylase (AADC) DeficiencyChina
-
Spark TherapeuticsActive, not recruitingLysosomal Storage Diseases | Glycogen Storage Disease Type II | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Canada, Netherlands, France, Denmark, Germany, Italy, United Kingdom
-
Spark TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Italy, United Kingdom, Netherlands, France, Germany
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
-
Indonesia UniversityUnited States Agency for International Development (USAID); Ministry of Research...Completed
-
Harvard UniversityCompleted
-
Oklahoma State University Center for Health SciencesActive, not recruiting
-
National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
-
Hadassah Medical OrganizationUnknown
-
National Institute of Health and NutritionCompletedFolate Deficiency
-
Mansoura UniversitySwedish University of Agricultural Sciences; The Swedish Research Council for...Completed
-
University Hospital HeidelbergGerman Cancer Research CenterCompletedType2 Diabetes | Fatty Acid Deficiency | Alteration of Mitochondrial MembraneGermany
-
Meir Medical CenterCompletedFolic Acid Deficiency | Vitamin B12 DeficiencyIsrael
-
University of TorontoThe Hospital for Sick Children; Heinz EndowmentsCompletedIron Deficiency | Folic Acid DeficiencyCanada
-
King's College Hospital NHS TrustCompletedAcidosis | Acid Base Disorder | Cardiac; DeficiencyUnited Kingdom
-
Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
-
University Hospital, Strasbourg, FranceCompletedFolic Acid Deficiency | Elderly Patients | Social IsolationFrance
-
National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
-
Boston Children's HospitalUNICEF; Ministry of Health, Liberia; Liberia Institute of Statistics and Geo-Information...WithdrawnNutritional Anemia | Knowledge, Attitudes, Practice | Food Habits | Iron Deficiency Anemia Treatment | Nutritional Deficiency | Adolescent Development | Folic Acid Deficiency Anemia, Dietary
-
Oslo University HospitalUniversity of Oslo; Umeå University; University of Geneva, SwitzerlandActive, not recruitingImmature Infant | Essential Fatty Acid DeficiencyNorway
-
Walden UniversityCompletedPregnancy Related | Autism Spectrum Disorder | Autistic Disorder | Folate Deficiency | Folic Acid Deficiency | Diet, Healthy | Autism | Diet; Deficiency | Folic Acid OverdoseUnited States
-
Genzyme, a Sanofi CompanyCompletedPompe Disease | Glycogen Storage Disease Type II (GSD II) | Acid Maltase DeficiencyUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
-
Eduardo FerriolliCompletedFatty Acid Deficiency | Nutrient Deficiency | Vitamin E Deficiency | Selenium Deficiency | Age-Related Immunodeficiency | Institutionalization; Disinhibited AttachmentBrazil
-
Bina Nusantara UniversityMaastricht University; Yayasan Rumah Sakit Islam (YARSI) University; Universitas...Completed
-
Hospices Civils de LyonRecruitingDeficiency, Vitamin CFrance
-
The University of Hong KongQueen Mary Hospital, Hong KongNot yet recruitingThalassemia | Folic Acid Deficiency Anemia
-
Smt. Kashibai Navale Medical College and General...CompletedType 2 Diabetes | Vitamin B12 Deficiency | HyperhomocysteinemiaIndia
-
University of California, DavisUniversity of California, San Francisco; Ethiopian Public Health Institute; Nutrition...Enrolling by invitationFolate Deficiency | Iodine Deficiency | Anemia, Macrocytic | Anemia Deficiency | Salt IntakeEthiopia
-
SingHealth PolyclinicsCompletedVitamin D Deficiency | Fall | Vitamin B 12 Deficiency | Folate Deficiency | Muscle Strength | HyperhomocysteinemiaSingapore
-
University of California, DavisUniversity of California, San Francisco; University of Rhode Island; Ethiopian... and other collaboratorsNot yet recruitingVitamin B 12 Deficiency | Folate Deficiency | Iodine Deficiency | Anemia Deficiency | Salt Intake | Anemia Macrocytic
-
Cornell UniversityCenters for Disease Control and Prevention; Arogyavaram Medical CentreActive, not recruitingAnemia | Vitamin B 12 Deficiency | Folate DeficiencyIndia
-
Cornell UniversityCenters for Disease Control and Prevention; St. John's Research Institute; Arogyavaram...Active, not recruiting
-
SEAMEO Regional Centre for Food and NutritionLondon School of Hygiene and Tropical Medicine; University College, London; University... and other collaboratorsRecruitingProtozoan Infections | Birth Weight | Weight Gain | Vitamin A Deficiency | Folate Deficiency | Zinc Deficiency | Child Development | Salmonella Infections | Anemia, Iron Deficiency | Fatty Acid Deficiency | Birth Length | B12 Deficiency Vitamin | Mineral Deficiency | E. Coli Infection | Shigella Infection | Amino Acid Deficiency and other conditionsIndonesia