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Clinical Trials on Hyperammonemia
Total 19 results
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University Hospital, GhentRecruitingHyperammonemic EncephalopathyBelgium
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Elizabeth A RosenfeldNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedHyperinsulinism-Hyperammonemia SyndromeUnited States
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Children's Hospital of PhiladelphiaUniversity of Pennsylvania; Lawson Wilkins Pediatric Endocrine SocietyWithdrawn
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TenNor Therapeutics (Suzhou) LimitedCompleted
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Liminal BioSciences Ltd.TerminatedHyperammonemiaUnited Kingdom
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TenNor Therapeutics (Suzhou) LimitedCompleted
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Institute of Liver and Biliary Sciences, IndiaCompleted
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Children's Mercy Hospital Kansas CityWithdrawnHypoglycemia | Seizures | HyperammonemiaUnited States
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Mendel TuchmanEunice Kennedy Shriver National Institute of Child Health and Human Development...UnknownInborn Errors of MetabolismUnited States
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Groupe Hospitalier Pitie-SalpetriereCompletedMetabolic Disease | Adverse Drug Event | Hyperammonemia | Drug ToxicityFrance
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Target PharmaSolutions, Inc.Recordati Rare DiseasesEnrolling by invitationPropionic Acidemia | Methylmalonic Acidemia | HyperammonemiaUnited States
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.RecruitingPropionic Acidemia | Methylmalonic Acidemia | HyperammonemiaUnited States
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Nicola LongoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...Completed
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Ocera Therapeutics, Inc.CompletedHepatic Encephalopathy | Acute Episode of Overt Hepatic EncephalopathyBelgium, Germany, Italy, Spain, United States, France, Austria, Russian Federation, Czechia, Australia, Hungary, Israel, Netherlands, Bulgaria, Estonia, Denmark, New Zealand
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
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Centre Hospitalier Régional de la CitadelleSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Universitaire... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States