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Clinical Trials on Infantile Neuroaxonal Dystrophy
Total 1433 results
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Retrotope, Inc.CompletedNeuroaxonal Dystrophy, InfantileEgypt, China, Saudi Arabia, India, Tunisia
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Retrotope, Inc.Active, not recruitingInfantile Neuroaxonal DystrophyUnited States
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Retrotope, Inc.CompletedInfantile Neuroaxonal Dystrophy | INADUnited States
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Duke UniversityTerminatedInfantile Neuroaxonal DystrophyUnited States
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University Hospital, Clermont-FerrandEnrolling by invitationNeuroaxonal Dystrophy, AtypicalFrance
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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University Hospital, MontpellierUnknownDuchenne Muscular Distrophy (DMD)France
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Assiut UniversityRecruiting
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SOFAR S.p.A.CompletedInfantile Colic | Colic, InfantileItaly
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Assistance Publique - Hôpitaux de ParisOSO-AIRecruiting
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Hospital San BartolomeInstituto de Investigacion de las Alteraciones del Crecimiento, Desarrollo...Unknown
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Yuzuncu Yıl UniversityIstanbul University - Cerrahpasa (IUC)Recruiting
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Federico II UniversityCompleted
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Children's Hospital of Orange CountyRecruiting
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CerecinActive, not recruiting
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University of Colorado, DenverPediatric Epilepsy Research Foundation; West Therapuetics, IncSuspended
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Suvasini SharmaUnknownInfantile SpasmIndia
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Radius Pharmaceuticals, Inc.TerminatedInfantile SpasmUnited States
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University of Colorado, DenverMallinckrodtRecruitingInfantile Spasms, Non-IntractableUnited States
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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Kullasate SakpichaisakulRecruitingWest Syndrome | Infantile SpasmThailand
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Bio-Pharm Solutions Co., Ltd.TerminatedRefractory Infantile SpasmsUnited States, Korea, Republic of
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UCB Biopharma S.P.R.L.TerminatedInfantile Spasms (IS)France
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EarliTec Diagnostics, IncMarcus Autism CenterRecruitingAutism Spectrum Disorder | Developmental Delay | Autism | Autism, Early Infantile | Autism, InfantileUnited States
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University of California, BerkeleyMakerere UniversityCompletedDiarrhea | Dehydration | Infantile Diarrhea
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Manhattan Eye, Ear & Throat HospitalNorthwell HealthWithdrawnPattern Dystrophy of MaculaUnited States
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's Hospital and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Myotonic Dystrophy | Facioscapulohumeral Muscular DystrophyUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompletedBecker Muscular Dystrophy | Facioscapulohumeral Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Legacy Health SystemDevers Eye Institute; Lions Eye Bank of Oregon Vision Research Laboratory; Fischer...UnknownFuchs' Corneal Endothelial DystrophyUnited States
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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Royan InstituteUnknown
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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Jazz PharmaceuticalsCompletedInfantile SpasmsUnited States, Poland
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Lady Hardinge Medical CollegeCompleted
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INSYS Therapeutics IncTerminatedSpasms, InfantileUnited States
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Lady Hardinge Medical CollegeWithdrawnInfantile SpasmsIndia
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Lundbeck LLCWithdrawn
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University Hospital, LilleRecruitingMacular Degeneration | Cone Dystrophy | Cone Rod Dystrophy | Retinal Dystrophy, Cone-RodFrance
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Marinus PharmaceuticalsTerminated
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Jazz PharmaceuticalsCompletedInfantile SpasmsUnited States, Poland
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All India Institute of Medical Sciences, New DelhiCompleted
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineCompletedFuchs Endothelial Corneal DystrophyFrance
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingLimb-girdle Muscular Dystrophy | Neuromuscular; Disorder, Hereditary | Duchenne/Becker Muscular DystrophyUnited States
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Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
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University of Colorado, DenverCompleted
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The Hospital for Sick ChildrenWithdrawnInfantile SpasmsCanada