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Clinical Trials on Inherited Bone Marrow Failure Syndromes
Total 10250 results
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Sohag UniversityAssiut University; Kyoto UniversityRecruitingInherited BMF SyndromeEgypt
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Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
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National Cancer Institute (NCI)RecruitingInherited Bone Marrow Failure Syndrome | Familial Platelet Disorder With Predisposition to Myeloid MalignanciesUnited States
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Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of MelbourneRecruitingHematologic Diseases | Inherited Platelet Disorder | Inherited BMF SyndromeAustralia
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Telomere Biology Disorders | Inherited Bone Marrow Failure SyndromesUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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Children's Hospital of PhiladelphiaAvailableLeukemia | Immunodeficiencies | Bone Marrow Failure SyndromeUnited States
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St. Jude Children's Research HospitalActive, not recruitingAplastic Anemia | Bone Marrow Failure SyndromeUnited States
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University of CalgaryUnknownBone Marrow Failure Syndrome
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Rabin Medical CenterUnknownHematological Malignancy | Bone Marrow Failure SyndromeIsrael
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Children's Hospital of PhiladelphiaCompletedBone Marrow Failure Syndromes | Immunodeficiencies | Immune Dysregulation SyndromesUnited States
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University of British ColumbiaCompletedHematological Malignancy | Bone Marrow Failure SyndromeCanada
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Cellenkos, Inc.Active, not recruitingBone Marrow DiseaseUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMDS (Myelodysplastic Syndrome) | Severe Aplastic AnemiaUnited States
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Medical College of WisconsinChildren's Hospital of PhiladelphiaCompletedMalignant Diseases (ie, Leukemia, MDS, Lymphoma) | Non-malignant Diseases (ie, Bone Marrow Failure Syndromes)United States
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Children's Hospital of PhiladelphiaRecruiting
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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Johns Hopkins All Children's HospitalRecruitingSevere Aplastic Anemia | Bone Marrow Failure Syndrome | Hemoglobinopathy (Disorder)United States
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University of California, San FranciscoTerminatedMyeloid Malignancy | Metabolic Disease | Bone Marrow Failure Syndrome | Transfusion-dependent Red Blood Cell (RBC) Defect | Congenital Immunodeficiency | Severe Immune DysregulationUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedBone Marrow Failure Syndromes | Severe Aplastic AnemiaUnited States
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Cooperative Study Group A for HematologyCompletedBone Marrow Failure SyndromesKorea, Republic of
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AlexionCompleted
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Asan Medical CenterCompletedMyelodysplastic Syndromes | Leukemia | Nonmalignant Neoplasm | Paroxysmal Nocturnal HemoglobinuriaKorea, Republic of
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Emory UniversityTerminated
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Peter MacCallum Cancer Centre, AustraliaRecruitingAplastic Anemia | Bone Marrow Failure SyndromeAustralia
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Columbia UniversityTerminatedLymphoma | Leukemia | Histiocytosis | Bone Marrow Failure Syndromes | ImmunodeficienciesUnited States
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Emory UniversityWithdrawnHematopoietic and Lymphoid Cell Neoplasm | Leukemia | Anemia | Myelodysplastic Syndrome | Aplastic Anemia | Bone Marrow FailureUnited States
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Anjali SharathkumarAmgenActive, not recruitingThrombocytopenia | Bone Marrow Failure Disorders | Aplastic Anemia | Refractory Cytopenia of Childhood | Myelodysplastic Syndrome(MDS)United States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Children's Hospital of PhiladelphiaRecruitingLeukemia | Bone Marrow Failure Syndromes | Immunodeficiencies | Inborn Errors of Metabolism | Immunodysregulation Polyendocrinopathy Enteropathy X-linked SyndromeUnited States
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Elixirgen Therapeutics, Inc.Not yet recruiting
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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Assistance Publique - Hôpitaux de ParisRecruiting
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BioLineRx, Ltd.CompletedAplastic Anemia | Hypoplastic Myelodysplastic SyndromeUnited States
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King Faisal Specialist Hospital & Research CenterUnknownAplastic Anemia and Other Marrow Failure SyndromeSaudi Arabia
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedMyelodysplastic Syndrome | Aplastic AnemiaUnited States
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Qianfoshan HospitalChinese Medical AssociationRecruiting
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Memorial Sloan Kettering Cancer CenterRecruitingHemoglobinopathies | AML | MDS | Bone Marrow Failure | ALL | Inherited Metabolic Disorders | HLH | MPD Withou Myelofibrosis | NHL or HLUnited States
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King's College Hospital NHS TrustCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Bone Marrow Transplantation | Aplastic AnemiaUnited Kingdom
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Elixirgen Therapeutics, Inc.RecruitingBone Marrow Failure | Telomere ShorteningUnited States
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medac GmbHSyneos Health; Celerion; Venn Life SciencesCompletedBone Marrow Failure Syndromes | Inborn Errors of Metabolism | Primary Immunodeficiencies | HaemoglobinopathiesPoland, Czechia, Germany, Italy
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Aplastic Anemia | de Novo Myelodysplastic SyndromeUnited States
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University of Sao PauloConselho Nacional de Desenvolvimento Científico e TecnológicoCompletedIdiopathic Pulmonary Fibrosis | Aplastic Anemia | Bone Marrow Failure Syndromes | Telomere ShorteningBrazil
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingModerate Aplastic Anemia | Unilineage Bone Marrow Failure DisordersUnited States
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Henry Ford Health SystemCompletedHematologic Disorders and Bone Marrow Failure, Hematopoietic Stem Cell Transplantation (HSCT) or Cellular Therapy (CART)United States