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Clinical Trials on Inherited Metabolic Disorders IMD
Total 38627 results
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Novartis PharmaceuticalsWithdrawnInherited Metabolic Disorders IMD
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Magenta Therapeutics, Inc.TerminatedInherited Metabolic Disorders (IMD)United States
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University of BernUniversity Hospital Inselspital, Berne; University of Lausanne Hospitals; University... and other collaboratorsRecruitingCongenital Muscular Dystrophy | SMA | DMD | BMD | IMDSwitzerland
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Magenta Therapeutics, Inc.CompletedInherited Metabolic Disorders (IMD)United States
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Academisch Medisch Centrum - Universiteit van Amsterdam...Stichting MetakidsCompletedInherited Metabolic DisordersNetherlands
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University Hospital, GrenobleRecruitingSchizophrenia | Inherited Metabolic Disorder of Nervous SystemFrance
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National Human Genome Research Institute (NHGRI)CompletedUndiagnosed Disease | Healthy Volunteer (Adult With Typically Developing Child) | Inherited Neurodegenerative Disorders | Inherited Metabolic Disorders (Inborn Errors of Metabolism) | Alzheimer's Disease and Related DementiasUnited States
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Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatedInherited Metabolic Storage DiseasesUnited States
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Assistance Publique Hopitaux De MarseilleRecruitingInherited Metabolic Diseases Requiring Restrictive and Specific DietFrance
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Prollenium Medical Technologies Inc.Completed
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Institut National de la Santé Et de la Recherche...Enrolling by invitationCharacterization of New Candidate Genes in Cases of Human Inherited Thrombocytopenia (CATCH) (CATCH)Thrombocytopenia | Inherited Platelet DisorderFrance
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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IRCCS Policlinico S. MatteoCompleted
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Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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University of AberdeenCompletedMetabolism Disorder, GlucoseUnited Kingdom
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingLipid Metabolism DisorderUnited States
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Université de SherbrookeHospices Civils de LyonCompleted
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Merck Sharp & Dohme LLCCompletedLipid Metabolism Disorder
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Columbia UniversityCompletedMetabolism Disorder, GlucoseUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Neuromuscular Disease | Inherited Neuromuscular Conditions | Inherited NeuropathiesUnited States
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Organon and CoCompleted
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Michigan State UniversityCompletedIron Deficiency Anemia (IDA) | Iron Deficiency (ID) | General AnemiaGhana
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Luye Pharma Group Ltd.CompletedLipid Metabolism DisorderUnited States
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Lo.Li.Pharma s.r.lCompleted
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Maastricht University Medical CenterDSM Food SpecialtiesRecruitingProtein Metabolism DisorderNetherlands
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Maastricht University Medical CenterActive, not recruiting
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Hadassah Medical OrganizationUnknownGestational Diabetes | Epigenetic Changes | Pregestational Diabetes | Neurodevelopmental Outcome | IDM (Infant of Diabetic Mothers)Israel
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Hasselt UniversityRecruitingExercise | Sedentary Behavior | Lipid Metabolism DisorderBelgium
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Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of MelbourneRecruitingHematologic Diseases | Inherited Platelet Disorder | Inherited BMF SyndromeAustralia
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Region SkaneEnrolling by invitationObesity, Adolescent | Mental Health Impairment | IBDSweden
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AdventHealth Translational Research InstituteTakeda; Sanford-Burnham Medical Research InstituteActive, not recruitingObesity | Lipid Metabolism Disorders | Disorder of Lipid Storage and Metabolism | Metabolic DisorderUnited States
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General and Teaching Hospital CeljeCompletedDiabetes Mellitus, Type 1 | Biomarkers | Endothelial Dysfunction | Arterial Stiffness | FMD | Incretins | Endothelial Progenitor Cells | SGLT 2 Inhibitors | Glucose Excursions | FPFSlovenia
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Xiang Guang-daCompletedEndothelial Function | LVM | Type 2 Diabetic Patients With IHDChina
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Nanjing Medical UniversityNot yet recruitingNutrition | Metabolism DisorderChina
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Sanjiv Narayan, MD, PhDWithdrawnAnxiety | Patient Engagement | ICDUnited States
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German Research FoundationUnknownSchizophrenia | Delusional Disorders (ICD-10)Germany
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University of South CarolinaCompletedPhysical Activity | Sedentary Lifestyle | Metabolism Disorder, GlucoseUnited States
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Rigshospitalet, DenmarkUniversity Hospital, Gentofte, CopenhagenCompletedAnxiety | Cognitive Therapy | ICDDenmark
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University of KonstanzLudwig-Maximilians - University of Munich; Jimma UniversityCompletedCommon Mental Disorders (CMD) | Psychotic Symptoms
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Shandong Provincial HospitalRecruitingMetabolism and Nutrition Disorder | Rhythm Nodal | Metabolism Disorder, LipidChina
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Memorial Sloan Kettering Cancer CenterRecruitingHemoglobinopathies | AML | MDS | Bone Marrow Failure | ALL | Inherited Metabolic Disorders | HLH | MPD Withou Myelofibrosis | NHL or HLUnited States
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Solvay PharmaceuticalsTerminatedDyslipidemia | Glucose Metabolism DisorderPoland, Croatia, Finland, France, Germany, Netherlands, Romania, Ukraine
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Azienda Ospedaliero, Universitaria PisanaCompletedPregnancy Related | Maternal-Fetal Relations | Metabolism Disorder, GlucoseItaly
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Nantes University HospitalCompletedHemophilia | Arthropathy | OsteopeniaFrance
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Texas A&M UniversityCompletedLipoprotein Metabolism Disorder
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Solvay PharmaceuticalsCompletedDyslipidemia/Glucose Metabolism DisorderPoland, Ukraine, United Kingdom