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Clinical Trials on Inherited Retinal Dystrophy Due to RPE65 Mutations
Total 86 results
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Innostellar Biotherapeutics Co.,LtdActive, not recruitingInherited Retinal Dystrophy Associated With RPE65 MutationsChina
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Frontera TherapeuticsRecruitingBiallelic RPE65 Mutation-associated Retinal DystrophyChina
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Novartis PharmaceuticalsActive, not recruitingBiallelic RPE65 Mutation-associated Retinal DystrophyJapan
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Shahid Beheshti University of Medical SciencesUnknownInherited Retinal Dystrophy Primarily Involving Sensory Retina | Inherited Retinal Dystrophy Primarily Involving Retinal Pigment EpitheliumIran, Islamic Republic of
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Gangnam Severance HospitalCompletedInherited Retinal Dystrophy Primarily Involving Sensory Retina | Inherited Retinal Dystrophy Primarily Involving Retinal Pigment EpitheliumKorea, Republic of
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Innostellar Biotherapeutics Co.,LtdRecruitingInherited Retinal DystrophyChina
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HuidaGene Therapeutics Co., Ltd.Cholgene Therapeutics, Inc.RecruitingLeber Congenital Amaurosis | Inherited Retinal Diseases Caused by RPE65 MutationsUnited States, China
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Retina Implant AGTerminatedRetinal Degeneration | Inherited Retinal Dystrophy Primarily Involving Sensory RetinaFrance
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University of WashingtonRecruitingInherited Retinal Dystrophy Primarily Involving Sensory RetinaUnited States
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Sun Yat-sen UniversityCompletedRetinitis Pigmentosa | Inherited Retinal Dystrophy | Retina DisorderChina
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Novartis PharmaceuticalsCompletedNeovascular AMD, Visual Impairment Due to DME, Visual Impairment Due to Macular Oedema Secondary to Branch or Central RVO, Visual Impairment Due to CNVGermany
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Shanghai General Hospital, Shanghai Jiao Tong University...RecruitingInherited Retinal DystrophiesChina
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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Fondazione G.B. Bietti, IRCCSRecruitingMacular Edema | Inherited Retinal Dystrophy | Laser RetinopathyItaly
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Istituto Superiore di SanitàFondazione G.B. Bietti, IRCCS; Ospedale Pediatrico Bambin GesùRecruitingRetinitis Pigmentosa | Macular Dystrophy | Inherited Retinal DystrophyItaly
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Ankara Universitesi TeknokentCompletedRetinitis Pigmentosa | Inherited Retinal DystrophyTurkey
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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University Hospital "Sestre Milosrdnice"CompletedRhegmatogenous Retinal Detachment | Toxic Effect of Silicone | Glaucoma Due to Silicon OilCroatia
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Jaeb Center for Health ResearchFoundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Inherited Retinal DegenerationUnited States, United Kingdom, France, Brazil, Canada, Finland, Israel, Mexico, Netherlands, Switzerland, Australia
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Imperial College London Diabetes CentreUnknownMendelian Disorders | Genetic Disorder | Novel Mutation | Hereditary Disorder | De Novo Mutation | Inherited Disease | Single-Gene DefectsUnited Arab Emirates
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Zhongshan Ophthalmic Center, Sun Yat-sen UniversityRecruiting
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Sudhalkar Eye HospitalNot yet recruitingClinically Significant Macular Edema Due to Diabetes MellitusGermany
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Kyoto University, Graduate School of MedicineNovartisUnknown
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Charite University, Berlin, GermanyWithdrawnNeed for Renal Replacement Therapy and Anti-infective Therapy Due to Severe InfectionGermany
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Novartis PharmaceuticalsWithdrawnVisual Impairment Due to Diabetic Macular EdemaGermany
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Second Affiliated Hospital, School of Medicine,...RecruitingVitreous Hemorrhage | Macular Edema Due to Diabetes MellitusChina
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Novartis PharmaceuticalsWithdrawnVisual Impairment Due to Diabetic Macular Edema
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Hospital Clinic of BarcelonaFundació La Marató de TV3UnknownDiabetes Mellitus | Diabetes Mellitus, Type 1 | Diabetic Retinopathy | Retinal Vascular | Retinal Disease | Retinal Ischemia | Retinal Ischaemia Due to Type 1 Diabetes Mellitus | Vessels; Retina, TortuousSpain
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University of OxfordCompletedAge-related Macular Degeneration | Retinitis Pigmentosa | Inherited Retinal Dystrophies | Optic Nerve PathologyUnited Kingdom
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Mayo ClinicrEVO BiologicsTerminatedThrombophilia Due to Acquired Antithrombin III DeficiencyUnited States
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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Novartis PharmaceuticalsTerminatedVisual Impairment Due to Diabetic Macular EdemaGermany
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CAMC Health SystemUnknownAKI (Acute Kidney Injury) Due to TraumaUnited States
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Hannover Medical SchoolCompletedAcute Kidney Injury | Infection Due to Resistant BacteriaGermany
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Assiut UniversityNot yet recruitingAcute Kidney Injury Due to covid_19Egypt
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Oregon Health and Science UniversityCompletedArthropathy Due to Bleeding From HemophiliaUnited States
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Mahmoud Kamel Mohamed Abd elhaqNot yet recruitingAcute Kidney Injury Due to Sepsis
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Hospital Universitario Dr. Jose E. GonzalezCompletedChronic Kidney Disease Due to Hypertension | Chronic Kidney Disease Due to Type 2 Diabetes MellitusMexico
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Uptown Eye SpecialistsUnknownDiabetic Retinopathy | Cataract | Macular Edema Due to Diabetes MellitusCanada
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University of British ColumbiaVancouver Coastal Health Research Institute; Genome British ColumbiaRecruitingAcute Coronary Syndrome | Familial Hypercholesterolemia | STEMI | NSTEMI - Non-ST Segment Elevation MI | Familial Hypercholesterolemia - Heterozygous | Familial Hypercholesterolemia Due to Genetic Defect of Apolipoprotein B | Familial Hypercholesterolemia Due to Heterozygous LDL Receptor Mutation and other conditionsCanada
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Ain Shams UniversityCompletedAKI (Acute Kidney Injury) Due to TraumaEgypt
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Second Affiliated Hospital of Soochow UniversityRecruitingPatient Admitted to Hospital With Acute Kidney Injury Due to SepsisChina
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University of Sao PauloInstituto Dante Pazzanese de CardiologiaRecruitingAcute Kidney Injury Due to Circulatory FailureBrazil
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IRCCS MultimedicaAbbVieRecruitingDiabetic Macular Edema | Retinal Vein Occlusion | Macular Edema Due to Diabetes MellitusItaly
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Chang Gung Memorial HospitalCompletedSecondary Hyperparathyroidism Due to Renal CausesTaiwan
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Fundación SenefroAbbVie; Effice Servicios Para la Investigacion S.L.CompletedSecondary Hyperparathyroidism Due to Renal CausesSpain
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Cairo UniversityCompleted