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Clinical Trials on Leber Congenital Amaurosis
Total 8789 results
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ProQR TherapeuticsTerminatedEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium
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ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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Eyecure Therapeutics Inc.Beijing Tongren HospitalUnknownLeber Congenital Amaurosis, Retinitis PigmentosaChina
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)Canada, United States, Germany, Netherlands, United Kingdom
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)United States, Canada, Germany, Netherlands, United Kingdom
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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University of Campania "Luigi Vanvitelli"Retina Italia OnlusCompletedLeber Congenital Amaurosis 2 | Retinitis Pigmentosa 20Italy
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QLT Inc.CompletedLeber Congenital Amaurosis (LCA) | Retinitis Pigmentosa (RP)United States, Canada, Denmark, Germany, Netherlands, Switzerland, United Kingdom
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ProQR TherapeuticsCompletedLeber's Congenital AmaurosisUnited States, Belgium
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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Editas Medicine, Inc.CompletedEye Diseases | Retinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Blindness | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Netherlands, France, Germany
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics CorporationCompletedRetinal DegenerationUnited Kingdom
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HuidaGene Therapeutics Co., Ltd.Xinhua Hospital, Shanghai Jiao Tong University School of MedicineRecruitingLeber Congenital AmaurosisChina
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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MeiraGTx UK II LtdCompletedNatural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65Leber Congenital AmaurosisUnited Kingdom, United States
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Xinhua Hospital, Shanghai Jiao Tong University...HuidaGene Therapeutics Co., Ltd.RecruitingLeber Congenital AmaurosisChina
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Assistance Publique - Hôpitaux de ParisCompletedLeber Congenital AmaurosisFrance
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Spark TherapeuticsCompleted
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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Hadassah Medical OrganizationCompletedLeber Congenital AmaurosisIsrael
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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HuidaGene Therapeutics Co., Ltd.Cholgene Therapeutics, Inc.RecruitingLeber Congenital Amaurosis | Inherited Retinal Diseases Caused by RPE65 MutationsUnited States, China
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OcugenRecruitingRetinitis Pigmentosa | Leber Congenital AmaurosisUnited States
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Shanghai General Hospital, Shanghai Jiao Tong University...Not yet recruitingTo Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
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Qlaris Bio, Inc.CompletedOcular Hypertension | Glaucoma | Glaucoma Congenital | Sturge-Weber Syndrome (SWS)United States
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University Hospital, ToursCompletedPort Wine Stain | Parkes Weber Syndrome | Klippel Trenaunay SyndromeFrance
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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Abbott Medical DevicesCompletedCarotid Artery Stenting Outcomes in the Standard Risk Population for Carotid Endarterectomy (CANOPY)Stroke | Carotid Artery Disease | Amaurosis Fugax | Transient Ischemic Attack (TIA)United States
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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Nantes University HospitalCompletedRetinal Diseases | AmaurosisFrance
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AdvanceCor GmbHCompletedStroke | Atherosclerosis | Carotid Stenosis | TIA | Transient-ischaemic Attack | Amaurosis FugaxGermany, United Kingdom
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Johns Hopkins UniversityVascular Birthmarks FoundationCompletedEpilepsy | Sturge Weber SyndromeUnited States
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Clinica Universidad de Navarra, Universidad de...Completed
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University of California, IrvineMainz UniversityCompletedSturge - Weber Syndrome (SWS)United States
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Wills EyeUniversity of Medicine and Dentistry of New JerseyTerminatedSturge Weber Syndrome | Port-wine MarkUnited States
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Baylor College of MedicineNovartis PharmaceuticalsWithdrawnSturge Weber SyndromeUnited States
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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University Hospital, AngersUnknownLeber Hereditary Optic NeuropathyFrance
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyFrance
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Santhera PharmaceuticalsEuropean Vision Institute Clinical Research NetworkCompletedLeber Hereditary Optic Neuropathy (LHON)Belgium, France, Denmark, Italy, Slovenia
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)United States