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Clinical Trials on Leigh Disease
Total 376650 results
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PTC TherapeuticsAxio Research. LLCCompleted
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Horizon Pharma USA, Inc.CompletedInherited Mitochondrial Disease, Including Leigh SyndromeUnited States
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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Aadi Bioscience, Inc.Withdrawn
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Taysha Gene Therapies, Inc.Withdrawn
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Khondrion BVDrug Research Unit Ghent, BelgiumCompletedMitochondrial Disease | MELAS | Leigh Syndrome | LHON | Mitochondrial DNA tRNALeu(UUR) m.3243A<G MutationBelgium
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The University of Texas Health Science Center,...RecruitingLeigh Disease | Leigh Syndrome | Leigh's Necrotizing Encephalopathy | Subacute Necrotizing Encephalomyopathy | Subacute Necrotizing EncephalomyelopathyUnited States
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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Khondrion BVJulius Clinical; ProPharma Group; Europees Fonds voor Regionale Ontwikkeling... and other collaboratorsRecruitingMitochondrial Diseases | MELAS | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Subacute Necrotizing EncephalomyelopathyNetherlands
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial Disorders | Leigh Disease | Oxidative Phosphorylation Deficiencies | Electron Transport Chain Disorders, MitochondrialUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMitochondrial Disease | Mitochondrial Disorders | Melas | Kearns Sayer | NARP | MNGIE | LHON | Mitochondrial Depletion Syndrome | Leigh's DiseaseUnited States
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Gangnam Severance HospitalRecruitingPancretic Dissease (Benign/Malignancy) | BIle Duct Diseae(Benign/Malignancy) | Ampulla of Vater Disease (Benign/Malignancy)Korea, Republic of
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University of MichiganNational Institutes of Health (NIH); National Institute of Dental and Craniofacial...CompletedPeriodontal Disease | Non-diseased PatientsUnited States
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Yonsei UniversityActive, not recruitingCoronary Artery DiseasseKorea, Republic of
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McMaster Children's HospitalSt. Justine's HospitalCompletedInflammatory Bowel Diseases | Crohn Disease | Colitis | Pediatric Crohns DiseaseCanada
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Academisch Medisch Centrum - Universiteit van Amsterdam...CelltrionRecruitingBowel Disease | Inflammatory Disease | Disease CrohnNetherlands
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First Affiliated Hospital of Wenzhou Medical UniversityCompletedLiver Diseases | Small Bowel Disease | Colorectal Disease | Gastric Diseases | Digestive Tract DiseasesChina
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Vascular Diseases | Raynaud's Disease
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The Second Hospital of Nanjing Medical UniversityAir Force Military Medical University, ChinaRecruitingInflammatory Bowel Disease | Crohn's DiseasesChina
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Central Hospital, Nancy, FranceInstitut Régional de Médecine Physique et de RéadaptationUnknownInterest of Hydrophysiotherapy Care in Parkinson Disease's Motor and Non-motor Symptoms (THERMAPARK)Interest of Hydrophysiotherapy Care in Parkinson Disease's Non-motor Symptoms
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University of BernMerck Sharp & Dohme LLC; University Hospital, Basel, Switzerland; University... and other collaboratorsCompleted
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Facet BiotechCompletedCrohn's Disease | Colitis | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseUnited States, Canada
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First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal DiseaseChina
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Children's Hospital Los AngelesCompleted
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Fondazione IRCCS Policlinico San Matteo di PaviaUniversity of PaviaRecruitingCalcific Aortic Valve DiaseaseItaly
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Ryazan State Medical UniversityCompletedChronic Obstructive Pulmonary Disease | Peripheral Artery DiseaseRussian Federation
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Direct Biologics, LLCRecruitingInflammatory Bowel Diseases | Crohn DiseaseUnited States
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Klinikum Westbrandenburg GmbHUnknown
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National Institute of Allergy and Infectious Diseases...RecruitingOccupational Accidents | Incubation Period, Infectious DiseseUnited States
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University of North Carolina, Chapel HillUniversity of Amsterdam; Crohn's and Colitis FoundationRecruitingCrohn Disease | Pediatric Crohns DiseaseNetherlands, United States, Canada, Israel
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National Institutes of Health Clinical Center (CC)CompletedVascular Diseases | Cancer | Metabolic Bone Disease | Inflammatory DiseaseUnited States
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Cedars-Sinai Medical CenterUnknownCrohn's Disease | Inflammatory Bowel DiseaseUnited States
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Dartmouth-Hitchcock Medical CenterAbbottCompletedCrohn's Disease | Inflammatory Bowel DiseaseUnited States
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Pharmbio Korea Co., Ltd.CompletedColonic Diseases | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseKorea, Republic of
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First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal Disease;China
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Janssen-Cilag Ltd.RecruitingFistulizing Crohns Disease | Perianal Crohns DiseaseNetherlands, United States, Belgium, Korea, Republic of, Taiwan, Israel, Japan, Canada, Hungary, Germany, Greece, United Kingdom, Australia, Spain, Saudi Arabia, Poland, Turkey, Portugal, Czechia, Italy, Jordan, France
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Medtronic - MITGCompletedInflammatory Bowel Disease, Crohn DiseaseIsrael
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Simon Fraser UniversityCanadian Institutes of Health Research (CIHR); Michael Smith Foundation for...CompletedHeart Failure | Diabetes | Chronic Obstructive Pulmonary Disease | Chronic Kidney Disease | Ischemic Heart DiseaseCanada
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Pharmbio Korea Co., Ltd.RecruitingColonic Diseases | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseKorea, Republic of
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New Aera, IncUnknownInterstitial Lung Disease | Chronic Obstructive Lung Disease
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Hospices Civils de LyonNot yet recruitingCrohn Disease | Pediatric Crohns DiseaseFrance
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University of NebraskaNot yet recruitingPeripheral Arterial Disease | Peripheral Vascular Diseases | Peripheral Arterial Occlusive Disease | Peripheral Artery DiseaseUnited States
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Astellas Pharma IncCompletedCoronary Artery Disease | Pulmonary Disease, Chronic Obstructive | AsthmaUnited States
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University of TorontoUnknownStroke | CHD - Coronary Heart Disease | CVD - Cerebrovascular DiseaseCanada
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Monash UniversityNovartis PharmaceuticalsRecruitingCerebrovascular Disease | Coronary Heart Disease (CHD) | Peripheral Arterial Disease (PAD) | Atherosclerotic Cardiovascular Disease (ASCVD)Australia
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Morphic Therapeutic, IncRecruitingInflammatory Bowel Diseases | Crohn's DiseaseUnited States
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Qu Biologics Inc.CompletedCrohn's Disease | Inflammatory Bowel DiseaseCanada