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Clinical Trials on Limb-girdle Muscular Dystrophy Type 2A

Total 24 results

    • NCT03488784
      Recruiting
      Natural History of Limb Girdle Muscular Dystrophy Type 2A and Type 2E
      Conditions: Limb-Girdle Muscular Dystrophy Type 2A; Limb-Girdle Muscular Dystrophy, Type 2E
    • NCT04800874
      Enrolling by invitation
      BBP-418 in Patients With LGMD2I
      Conditions: LGMD2I
    • NCT02841267
      Completed
      A Trial of PF-06252616 in Ambulatory Participants With LGMD2I
      Conditions: LGMD2I
    • NCT01976091
      Completed
      Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA
      Conditions: Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
    • NCT02165358
      Completed
      Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I
      Conditions: Becker Muscular Dystrophy; Limb-Girdle Muscular Dystrophy Type 2I
    • NCT01344798
      Completed
      Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
      Conditions: Limb Girdle Muscular Dystrophy Type 2C; Gamma-sarcoglycanopathy
    • NCT03492346
      Recruiting
      Limb Girdle Muscular Dystrophy Type 2E Recruitment Study
      Conditions: Limb-Girdle Muscular Dystrophy, Type 2E
    • NCT04509609
      Recruiting
      Clinical Determinants of Disease Progression in Patients With Limb Girdle Muscular Distrophy Type 2E
      Conditions: LGMD2E
    • NCT03842878
      Recruiting
      Natural History Study of Patients With Limb-Girdle Muscular Dystrophy 2I
      Conditions: LGMD2I
    • NCT04202627
      Enrolling by invitation
      Biomarker Development in LGMD 2i
      Conditions: Muscular Dystrophies; Limb Girdle Muscular Dystrophy
    • NCT03930628
      Recruiting
      Limb-Girdle Muscular Dystrophy Type 2I in Norway
      Conditions: Limb Girdle Muscular Dystrophy, Type 2I; Limb Girdle Muscular Dystrophy; Muscular Dystrophies
    • NCT00527228
      Completed
      Deflazacort in Dysferlinopathies
      Conditions: LGMD2B; Miyoshi Myopathy; Dysferlinopathy
    • NCT04475926
      Recruiting
      A Study of the Natural History of Patients With LGMD2E/R4, LGMD2D/R3, and LGMD2C/R5, ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice
      Conditions: Limb-girdle Muscular Dystrophy
    • NCT03652259
      Active, not recruiting
      Gene Delivery Clinical Trial of SRP-9003 for Patients With LGMD2E (Beta-sarcoglycan Deficiency)
      Conditions: Limb-Girdle Muscular Dystrophy, Type 2E
    • NCT00494195
      Completed
      Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
      Conditions: Muscular Dystrophies
    • NCT02759302
      Completed
      MRI on Persons With Mutations in POMT2 Gene (LGMD2N)
      Conditions: Limb-girdle Muscular Dystrophy
    • NCT03783923
      Completed
      A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)
      Conditions: Limb-Girdle Muscular Dystrophy
    • NCT01676077
      Unknown status
      Clinical Outcome Study for Dysferlinopathy
      Conditions: Dysferlinopathy; LGMD2B; Miyoshi Myopathy
    • NCT04349566
      Enrolling by invitation
      Fast Troponin as a Biomarker to Assess Exercise-induced Muscle Damage in Muscle Diseases
      Conditions: Becker Muscular Dystrophy; McArdle Disease; Limb-Girdle Muscular Dystrophy Type 2
    • NCT01403402
      Unknown status
      Congenital Muscle Disease Study of Patient and Family Reported Medical Information
      Conditions: Congenital Muscular Dystrophy (Including Unspecified/Undiagnosed); Dystroglycanopathy; Congenital Fiber Type Disproportion; Rigid Spine Muscular Dystrophy; Congenital Myopathy (Including Unspecified/Undiagnosed); Collagen VI CMD (Ullrich CMD, Intermediate, Bethlem Myopathy); Laminin Alpha 2 Related Congenital Muscular Dystrophy; LAMA2-CMD/Merosin Deficient/MDC1A; Walker-Warburg Syndrome; Muscle-Eye-Brain Disease; Fukuyama/Fukutin Related Muscular Dystrophy; Integrin Alpha 7 Deficiency; Integrin Alpha 9 Deficiency; LMNA-CMD/Lamin A/C/Laminopathy; SEPN1-Related Myopathy; Bethlem Myopathy; Actin Aggregation Myopathy; Cap Disease; Central Core Disease; Centronuclear Myopathy; Core Rod Myopathy; Hyaline Body Myopathy; Multiminicore Myopathy; Myotubular Myopathy; Nemaline Myopathy; Tubular Aggregate Myopathy; Zebra Body Myopathy; Reducing Body Myopathy; Spheroid Body Myopathy; LGMD1B (LMNA); LGMD1E (DES); LGMD2G (TCAP); LGMD2H (TRIM32); LGMD2I (FKRP); LGMD2J (TTN); LGMD2K (POMT1); LGMD2M (FKTN); LGMD2N (POMT2); LGMD2O (POMGnT1); LGMD2P (DAG1); LGMD2Q (PLEC1); LGMD2R (DES); LGMD2S (TRAPPC11); LGMD2T (GMPPB); LGMD2U (ISPD); LGMD2V (GAA); Ullrich Congenital Muscular Dystrophy; Titinopathy; Choline Kinase B Receptor; Emery-Dreifuss Muscular Dystrophy; RYR1 Related Myopathy; SYNE1/Nesprin Related Muscular Dystrophy; Telethonin Related Muscular Dystrophy (TCAP/Titin-Cap); Congenital Myasthenic Syndrome; Escobar Syndrome; Myofibrillar Myopathy; Malignant Hyperthermia; Alpha-Dystroglycan Related Muscular Dystrophy (DAG1, DPM1, DPM2, DPM3, FKRP, FKTN); Alpha-Dystroglycan Related Muscular Dystrophy (GAA, ISPD, LARGE, POMT1, POMT2, POMGnT1); Alpha-Dystroglycan Related Muscular Dystrophy (Unspecified/Undiagnosed/Other)
    • NCT04001595
      Recruiting
      The Global FKRP Patient Registry
      Conditions: LGMD2I; LGMDR9; Limb Girdle Muscular Dystrophy; Congenital Muscular Dystrophy; Muscle-Eye-Brain Disease; Walker-Warburg Syndrome; FKRP Gene Mutation
    • NCT02579239
      Completed
      The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies
      Conditions: Limb-Girdle Muscular Dystrophies; Facioscapulohumeral Muscular Dystrophy
    • NCT00893334
      Completed
      Evaluation of Limb-Girdle Muscular Dystrophy
      Conditions: Becker Muscular Dystrophy; Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency); Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency); Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)
    • NCT02710500
      Completed
      rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
      Conditions: Dysferlinopathy
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