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Clinical Trials on Malonyl-CoA Decarboxylase Deficiency
Total 56 results
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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University Hospital, MontpellierRecruitingAromatic L-Amino Acid Decarboxylase DeficiencyFrance
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Shanghai Jiao Tong University School of MedicineShanghai Vitalgen BioPharma Co., Ltd.RecruitingAromatic L-amino Acid Decarboxylase (AADC) DeficiencyChina
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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Oregon Health and Science UniversityCompletedTrifunctional Protein Deficiency | Carnitine Palmitoyltransferase 2 Deficiency | Very Long-chain Acyl-CoA Dehydrogenase Deficiency | Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency
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Oregon Health and Science UniversityCompletedNormal Volunteers | Trifunctional Protein Deficiency | Very Long-chain Acyl-CoA Dehydrogenase Deficiency | Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency | Medium-chain Acyl-CoA Dehydrogenase Deficiency | Carnitine Palmitoyltransferase II Deficiency, MyopathicUnited States
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Oregon Health and Science UniversityRecruitingTrifunctional Protein Deficiency | Very Long Chain Acyl Coa Dehydrogenase Deficiency | Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency | Carnitine Palmitoyltransferase Deficiency 2United States
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Rigshospitalet, DenmarkGroupe Hospitalier Pitie-SalpetriereCompletedCarnitine Palmitoyltransferase II Deficiency | Very Long Chain Acyl Coa Dehydrogenase DeficiencyDenmark
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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National Taiwan University HospitalCompletedAromatic L-amino Acid Decarboxylase DeficiencyTaiwan
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Ultragenyx Pharmaceutical IncCompletedCarnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine-acylcarnitine Translocase (CACT) DeficiencyUnited States, United Kingdom
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University of PittsburghHorizon Pharma Ireland, Ltd., Dublin IrelandCompletedMedium-chain Acyl-CoA Dehydrogenase (MCAD) DeficiencyUnited States
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD) | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine Palmitoyltransferase (CPT II) Deficiency | Longchain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyUnited States, United Kingdom
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Fondation Ophtalmologique Adolphe de RothschildCompleted
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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McGill University Health Centre/Research Institute...RecruitingPeroxisome Biogenesis Disorder | Zellweger Spectrum Disorder | RCDP - Rhizomelic Chondrodysplasia Punctata | D-Bifunctional Protein Deficiency | Alpha-Methylacyl-CoA Racemase Deficiency | Peroxisomal Acyl-CoA Oxidase Deficiency | Peroxisomal Acyl-CoA Oxidase 2 Deficiency | ATP Binding Cassette Subfamily... and other conditionsCanada
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.RecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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Centre Hospitalier Régional de la CitadelleSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Universitaire... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncRecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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Saglik Bilimleri UniversitesiUnknownGrowth Disorders | Cow Milk Allergy | Eating Behavior | Nutrient DeficiencyTurkey
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Parc de Salut MarUniversitat Pompeu FabraCompletedZinc Deficiency | Sars-CoV-2 InfectionSpain
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ANRS, Emerging Infectious DiseasesBristol-Myers SquibbCompleted
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Royal Centre for Defence MedicineLiverpool John Moores University; Leeds Beckett UniversityUnknownCovid19 | Vitamin D Deficiency | SARS-CoV Infection | Acute Respiratory Tract InfectionUnited Kingdom
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Prof. Dr. Jörg LeuppiCompletedCovid19 | Vitamin D Deficiency | Corona Virus Infection | ARDS | SARS-CoV Infection | CoronavirusSwitzerland
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Fundacion SEIMC-GESIDAAbbottCompletedHIV Infections | HIV/HCV Co-infectionSpain
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Hospitales Universitarios Virgen del RocíoActive, not recruitingHIV Infection | SARS-CoV-2 RNA VaccinesSpain
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Taoyuan General HospitalMerck Sharp & Dohme LLCCompleted
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ANRS, Emerging Infectious DiseasesCompleted
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Johns Hopkins UniversityNational Institute of Allergy and Infectious Diseases (NIAID); National Institutes... and other collaboratorsActive, not recruitingHIV | MDR-TBSouth Africa
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Andrea BranchNational Institute on Drug Abuse (NIDA)Completed
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Applied Biology, Inc.Hospital Universitario Ramon y CajalWithdrawnCOVID-19 | SARS-CoV 2 | COVID | Androgenetic Alopecia | Androgen Deficiency | Androgen Receptor AbnormalSpain
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National Institute of Allergy and Infectious Diseases...Completed
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Imperial College LondonCompletedHIV Infections | HIV | Acute Hepatitis CUnited Kingdom
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Johns Hopkins UniversityCompletedHepatitis C, Chronic | HIVUnited States
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Icahn School of Medicine at Mount SinaiGilead SciencesCompletedHepatitis C InfectionUnited States
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ANRS, Emerging Infectious DiseasesUnknown
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Ottawa Hospital Research InstituteOntario Lung AssociationWithdrawnHIV Infections | TuberculosisCanada, South Africa
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University of California, San FranciscoCalifornia HIV/AIDS Research ProgramCompletedHIV Infections | Hepatitis C | Human Immunodeficiency VirusUnited States
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Gilead SciencesCompletedHepatitis C Infection With HIV Co-InfectionUnited Kingdom, Germany
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National Institutes of Health Clinical Center (CC)Washington D.C. Veterans Affairs Medical CenterCompletedHepatitis B | Hepatitis C | HIV-HCV Co-InfectionUnited States
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Gritstone bio, Inc.Completed
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Ottawa Hospital Research InstituteGilead Sciences; CIHR Canadian HIV Trials NetworkCompletedHepatitis C, Chronic | Human Immunodeficiency VirusCanada
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University of California, San FranciscoCompletedHIV Infections | Hepatitis CUnited States
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Ministry of Science and Technology, IndiaIndian Council of Medical ResearchUnknownImpact of HIV Infection on Latent Tuberculosis (TB) Among Patients With HIV-TB Co-infection (HIV-TB)HIV Infections | Tuberculosis | Latent Tuberculosis InfectionIndia
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ViiV HealthcareGlaxoSmithKlineCompletedHIV Infections | Infection, Human Immunodeficiency VirusMexico, Peru, Thailand, South Africa, Russian Federation, Argentina, Brazil