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Clinical Trials on Molybdenum Cofactor Deficiency (MoCD)
Total 102 results
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency (MoCD) | Rare Autosomal Recessive Disorder | Deficiency of Activity of Molybdenum-dependent Enzymes (Sulfite Oxidase [SOX], Xanthine Dehydrogenase, and Aldehyde Oxidase)United States
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Spain, Israel, Norway, Turkey, United Kingdom
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Orphatech Pharmaceuticals, GmbHWithdrawnMolybdenum Cofactor Deficiency Type AAustralia
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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St. James's Hospital, IrelandUnknown
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Baxalta now part of ShireCompletedProthrombin Complex Factor DeficiencyHungary, Austria
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CSL BehringCompletedAcquired Coagulation Factor DeficiencyAustria, Germany, Hungary, Israel, Lithuania, Netherlands, Poland, Switzerland
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University Hospital GoettingenCompletedExtracorporeal Membrane Oxygenation Complication | Coagulation Factor DeficiencyGermany
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University of LjubljanaBarbara Jakše s.p.CompletedVitamin D Deficiency | Cardiovascular Risk Factor | Injuries | Nutritional DeficiencySlovenia
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Assiut UniversityUnknownCoagulation Factor Deficiency
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University of SevilleRecruitingInsulin Growth Factor I Deficiency | IGF1 Deficiency | Executive Function DisorderSpain
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Catalyst BiosciencesTerminatedPrevious Diagnosis With a Complement-mediated Disease and/or With Clinical Manifestations Reasonably Associated With Complement Factor I DeficiencyUnited States
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Patricia Duque GonzálezCompletedAcquired Factor XIII Deficiency DiseaseSpain
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Hoffmann-La RocheCompletedHaemophilia A | Moderate Hereditary Factor VIII Deficiency Disease Without Inhibitor | Severe Hereditary Factor VIII Deficiency Disease Without InhibitorItaly
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University of California, DavisCompletedInflammation | Cardiovascular Risk Factor | Micronutrient DeficiencyUnited States
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SourseCitruslabsActive, not recruitingMood | Energy Supply; Deficiency | B12 Deficiency VitaminUnited States
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Drexel UniversityAmerican Heart AssociationCompletedVitamin D Deficiency | Overweight and Obesity | Cardiovascular Risk Factor | Magnesium DeficiencyUnited States
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Oslo University HospitalCompletedHereditary Factor VIII Deficiency Disease With InhibitorNorway
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Bio Products LaboratoryCompletedFactor 10 DeficiencyUnited States
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Hospices Civils de LyonUnknownFactor XI Deficiency | Factor XII DeficiencyFrance
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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CSL BehringCompletedCongenital Coagulation Factor VII DeficiencyNetherlands, Norway
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National Yang Ming UniversityCompletedBurnout | Sleep | Mood | Melatonin Deficiency | Cortisol DeficiencyTaiwan
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Children's Mercy Hospital Kansas CityTerminatedHemophilia A | Hemophilia B | Hemophilia | Factor IX Deficiency | Factor VIII DeficiencyUnited States
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Region SkaneCompletedCoagulopathy, Consumption | Coagulation Factor Deficiency | Vitamin K DeficiencySweden
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PfizerCompletedFactor VIII Deficiency, Congenital | Hemophilia A, Congenital | Factor 8 Deficiency, Congenital | Autosomal Hemophilia A | Classic Hemophilia
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St Mary's University CollegeUnknownDepression | Anxiety | Choline DeficiencyUnited Kingdom
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The Hospital for Sick ChildrenCanadian Hemophilia SocietyCompletedHemophilia A | Hemophilia B | Factor IX Deficiency | Factor VIII DeficiencyCanada
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Cairo UniversityCompletedLeiden Factor V Deficiency,Preeclampsia | Doppler Examination | Palental Pathology
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IpsenTerminatedrhGH and rhIGF-1 Combination Therapy in Children With Short Stature Associated With IGF-1 DeficiencyInsulin-like Growth Factor-1 DeficiencyUnited States
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IpsenTerminatedPrimary Insulin-like Growth Factor-1 DeficiencyUnited States
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Bioverativ, a Sanofi companyCompletedFactor VIII DeficiencyUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, France, Germany, Greece, Hungary, Italy, Japan, Korea, Republic of, Mexico, Netherlands, Spain, Taiwan, United Kingdom
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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University of ReadingTufts University; California Walnut CommissionCompletedCognitive Change | Inflammatory Response | Mood | Satiety | Brain Derived Neurotrophic Factor LevelUnited Kingdom
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Mackay Memorial HospitalRecruitingVitamin D Deficiency | Major DepressionTaiwan
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University of Colorado, DenverThe University of Texas Health Science Center, Houston; Bayer; Emory University; Rush University Medical Center and other collaboratorsCompleted
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University of Sao Paulo General HospitalMerit Medical Systems, Inc.RecruitingHemophilia | Arthropathy | Synovitis | Hemarthrosis | Embolization | Clotting Factor DeficiencyBrazil
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Northumbria UniversityBayerCompletedCognitive Function and Mood | Non-anaemic Iron DeficiencyUnited Kingdom
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Benha UniversityNew Jeddah Clinic HospitalCompletedDepression | Hemodialysis Complication | Iron Deficiency Anemia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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CSL BehringCompletedFactor XIII DeficiencyUnited States, Spain
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Masaryk Hospital Krajská zdravotní a.s.CompletedCoagulation Disorder | Multiple Trauma | Coagulation Defect; Acquired | Coagulation Factor DeficiencyCzechia