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Clinical Trials on Monogenic Diseases
Total 376501 results
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University Hospital, MontpellierABM IndustriesUnknown
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Kunling ShenShengjing Hospital; Xinhua Hospital, Shanghai Jiao Tong University School of... and other collaboratorsRecruiting
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ApteeusEnrolling by invitationMonogenic DisordersFrance
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Chinese Academy of Medical Sciences, Fuwai HospitalUnknown
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University Hospital, BordeauxNot yet recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Children's Hospital of Fudan UniversityRecruitingSystemic Lupus Erythematosus | Monogenic LupusChina
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University Hospital, BordeauxNot yet recruitingMonogenic Obesity | Non Syndromic ObesityFrance
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University of ChicagoCompleted
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Assistance Publique - Hôpitaux de ParisCompletedNon Autoimmune Monogenic Diabetes
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Joslin Diabetes CenterEnrolling by invitationType 1 Diabetes | Monogenic DiabetesUnited States
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United Arab Emirates UniversityNot yet recruitingMaturity-onset Diabetes of the Young | MODY | Monogenic Diabetes
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AHEPA University HospitalUnknownTumor Induced Oncogenic OsteomalaciaGreece
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National Institute of Dental and Craniofacial Research...CompletedNeoplasms | OsteomalaciaUnited States
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Regeneron PharmaceuticalsAvailablePartial Lipodystrophy | Generalized Lipodystrophy | Monogenic Obesity Due to LEP or LEPR Loss of Function
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CASI Pharmaceuticals, Inc.CompletedMyelodysplasia | Hematological Malignancies | Agnogenic Myeloid MetaplasiaCanada
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Dana-Farber Cancer InstituteMassachusetts General Hospital; Novartis; Brigham and Women's HospitalCompletedMyelofibrosis | Chronic Myelomonocytic Leukemia | Myeloid Metaplasia | Agnogenic Myeloid MetaplasiaUnited States
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Peking Union Medical College HospitalUnknown
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National Institute of Dental and Craniofacial Research...TerminatedOncogenic Osteomalacia | Tumor-Induced OsteomalaciaUnited States
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M.D. Anderson Cancer CenterNovartisCompletedAcute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Agnogenic Myeloid MetaplasiaUnited States
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Guang NingRecruitingType 2 Diabetes Mellitus | Type1 Diabetes Mellitus | Monogenetic Diabetes | Pancreatogenic Diabetes | Drug-Induced Diabetes Mellitus | Other Forms of Diabetes MellitusChina
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Johns Hopkins UniversityMassachusetts General Hospital; Washington University School of Medicine; Emory... and other collaboratorsCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Healthy Controls | Flail Arm ALS | Monomelic Amyotrophy | Asymptomatic ALS Gene CarriersUnited States
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M.D. Anderson Cancer CenterNovartisCompletedLeukemia | Myelofibrosis | Mantle Cell LymphomaUnited States
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M.D. Anderson Cancer CenterBristol-Myers SquibbCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Polycythemia Vera | Myelofibrosis | Leukemia, Myelomonocytic, Chronic | Hypereosinophilic Syndrome | Mastocytosis | Agnogenic Myeloid MetaplasiaUnited States
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McGill University Health Centre/Research Institute...RecruitingDiabetes Mellitus, Type 1 | Wolfram Syndrome | Neonatal Diabetes | Monogenic Diabetes | Maturity-onset Diabetes in the Young (MODY) | Wolcott-Rallison Syndrome | Mitochondrial DiabetesCanada
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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University of MichiganNational Institutes of Health (NIH); National Institute of Dental and Craniofacial...CompletedPeriodontal Disease | Non-diseased PatientsUnited States
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Yonsei UniversityActive, not recruitingCoronary Artery DiseasseKorea, Republic of
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Gangnam Severance HospitalRecruitingPancretic Dissease (Benign/Malignancy) | BIle Duct Diseae(Benign/Malignancy) | Ampulla of Vater Disease (Benign/Malignancy)Korea, Republic of
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Central Hospital, Nancy, FranceInstitut Régional de Médecine Physique et de RéadaptationUnknownInterest of Hydrophysiotherapy Care in Parkinson Disease's Motor and Non-motor Symptoms (THERMAPARK)Interest of Hydrophysiotherapy Care in Parkinson Disease's Non-motor Symptoms
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McMaster Children's HospitalSt. Justine's HospitalCompletedInflammatory Bowel Diseases | Crohn Disease | Colitis | Pediatric Crohns DiseaseCanada
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First Affiliated Hospital of Wenzhou Medical UniversityCompletedLiver Diseases | Small Bowel Disease | Colorectal Disease | Gastric Diseases | Digestive Tract DiseasesChina
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Academisch Medisch Centrum - Universiteit van Amsterdam...CelltrionRecruitingBowel Disease | Inflammatory Disease | Disease CrohnNetherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Vascular Diseases | Raynaud's Disease
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The Second Hospital of Nanjing Medical UniversityAir Force Military Medical University, ChinaRecruitingInflammatory Bowel Disease | Crohn's DiseasesChina
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First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal DiseaseChina
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National Institutes of Health Clinical Center (CC)CompletedVascular Diseases | Cancer | Metabolic Bone Disease | Inflammatory DiseaseUnited States
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Fondazione IRCCS Policlinico San Matteo di PaviaUniversity of PaviaRecruitingCalcific Aortic Valve DiaseaseItaly
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Facet BiotechCompletedCrohn's Disease | Colitis | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseUnited States, Canada
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University of BernMerck Sharp & Dohme LLC; University Hospital, Basel, Switzerland; University... and other collaboratorsCompleted
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Children's Hospital Los AngelesCompleted
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First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal Disease;China
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Ryazan State Medical UniversityCompletedChronic Obstructive Pulmonary Disease | Peripheral Artery DiseaseRussian Federation
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Klinikum Westbrandenburg GmbHUnknown
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Direct Biologics, LLCRecruitingInflammatory Bowel Diseases | Crohn DiseaseUnited States
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University of North Carolina, Chapel HillUniversity of Amsterdam; Crohn's and Colitis FoundationRecruitingCrohn Disease | Pediatric Crohns DiseaseNetherlands, United States, Canada, Israel
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Pharmbio Korea Co., Ltd.CompletedColonic Diseases | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseKorea, Republic of
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Konkuk University Medical CenterCompletedValvular Heart Disease | Aortic DiseaseKorea, Republic of
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Sheikh Zayed Federal Postgraduate Medical InstituteHigher Education Commission (Pakistan)CompletedCoronary Heart Disease | Periodontal DiseasePakistan