Example: Heart Attack

Clinical Trials on Mucopolysaccharidosis Type IVA

Total 27 results

NCT01733615

Terminated

Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA

Conditions: Mucopolysaccharidosis Type IVA
NCT02208661

Completed

Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study)

Conditions: Morquio A Syndrome; Mucopolysaccharidosis IV A
NCT01920828

Completed

Gait Analysis in MPS IVA

Conditions: MPS IVA; Morquio Syndrome
NCT03204370

Recruiting

Natural History of Atypical Morquio A Disease

Conditions: Mucopolysaccharidosis IV A
NCT01275066

Completed

A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Conditions: MPS IV A
NCT01415427

Completed

Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Conditions: Mucopolysaccharidosis IV A; Morquio A Syndrome; MPS IVA
NCT01609062

Terminated

Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome

Conditions: Mucopolysaccharidosis IVA; Morquio A Syndrome; MPS IVA
NCT01697319

Terminated

Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation

Conditions: Mucopolysaccharidosis IVA; Morquio A Syndrome; MPS IVA
NCT01515956

Completed

Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Conditions: Mucopolysaccharidosis IVA; Morquio A Syndrome; MPS IVA
NCT01242111

Terminated

A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

Conditions: MPS IV A; Mucopolysaccharidosis IVA; Morquio A Syndrome
NCT00787995

Terminated

A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

Conditions: MPS IV A; Mucopolysaccharidosis IVA; Morquio A Syndrome
NCT02153255

Withdrawn

Dynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa

Conditions: Mucopolysaccharidosis IV; Morquio A Disease
NCT00884949

Completed

A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA

Conditions: MPS IV A
NCT01961518

Completed

Screening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy Syndrome

Conditions: Morquio Syndrome A; Maroteaux Lamy Syndrome; MPS IVA; MPS VI
NCT01966029

Completed

BMN 110 Phase 3B in Australian Patients

Conditions: Mucopolysaccharidosis IVA (Morquio A Syndrome)
NCT01858103

Approved for marketing

BMN 110 US Expanded Access Program

Conditions: Mucopolysaccharidosis IVA; Morquio A Syndrome; MPS IVA
NCT03632213

Recruiting

Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI

Conditions: Mucopolysaccharidosis IV A; Mucopolysaccharidosis VI; Mucopolysaccharidoses; MPS IV A; MPS VI; MPS - Mucopolysaccharidosis; Morquio A Syndrome; Morquio Syndrome A; Morquio Syndrome
NCT00609440

Terminated

Morquio's Syndrome: a Case Study

Conditions: Morquio's Disease
NCT01752296

Completed

Psychological Concomitants of Morquio Syndrome (The MAP Study)

Conditions: Morquio Disease; Mucopolysaccharidosis IV
NCT03150069

Recruiting

Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them?

Conditions: Morquio Disease; MPS - Mucopolysaccharidosis
NCT02067650

Completed

Ultrasound Findings of Finger, Wrist and Knee Joints in Mucopolysaccharidosis

Conditions: MPS I; MPS IV
NCT01707433

Completed

Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease

Conditions: Mucopolysaccharidosis IV A; Mucopolysaccharidosis VI
NCT02294877

Recruiting

A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)

Conditions: Mucopolysaccharidosis IV Type A; Morquio A Syndrome; MPS IVA
NCT01457456

Active, not recruiting

Biomarker for Morquio Disease (BioMorquio)

Conditions: Morquio Syndrome; Accumulation of Mucopolysaccharides; Morquio Syndrome A; Morquio B Disease
NCT04532047

Not yet recruiting

In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases

Conditions: MPS I; MPS II; MPS IVA; MPS VI; Mps VII; Gaucher Disease, Type 2; Gaucher Disease, Type 3; Pompe Disease Infantile-Onset; Wolman Disease