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Clinical Trials on Muscular Dystrophies
Total 50261 results
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Laval UniversityCompleted
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Atamyo TherapeuticsNot yet recruiting
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Alkeus Pharmaceuticals, Inc.CompletedAge-related Macular Degeneration | Stargardt Disease | Other Retinal Dystrophies
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingRetinal Detachment | Epiretinal Membrane | Macular Holes | Macular DystrophiesItaly
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Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
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Wake Forest University Health SciencesCompleted
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South Valley UniversityUnknownMuscular DystrophyEgypt
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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GlaxoSmithKlineCompleted
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University Children's Hospital, ZurichUniversity of ZurichWithdrawnMuscular Dystrophies
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Alessandra PedrocchiCompletedMuscular DystrophiesItaly
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FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
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Universitat Pompeu FabraHospital Clinic of BarcelonaRecruiting
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IRCCS Eugenio MedeaCompletedMuscular DystrophiesItaly
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AbiliTech Medical Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownMuscular Dystrophies
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Neurogen Brain and Spine InstituteWithdrawn
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Centre for Human Drug Research, NetherlandsFacio TherapeuticsCompleted
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Hoffmann-La RocheTerminatedMuscular Dystrophy (DMD)United States, Canada
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Centre Hospitalier Universitaire de Saint EtienneAssociation Française contre les Myopathies (AFM), ParisCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Santhera PharmaceuticalsCompleted
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Shanghai General Hospital, Shanghai Jiao Tong University...RecruitingInherited Retinal DystrophiesChina
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Mads Peter Godtfeldt StemmerikEdgewise Therapeutics, Inc.CompletedBecker Muscular Dystrophy | McArdle Disease | Limb-Girdle Muscular Dystrophy Type 2Denmark
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, United States
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Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
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Centre Hospitalier Universitaire de NiceActive, not recruitingMuscular Dystrophy | FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, France; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy | FacioscapulohumeralFrance
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Istanbul University - Cerrahpasa (IUC)CompletedFacioscapulohumeral Muscular DystrophyTurkey
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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Fondation Ophtalmologique Adolphe de RothschildRecruitingHereditary Retinal DystrophiesFrance
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular DystrophyFrance
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Newcastle UniversityRecruitingFacioscapulohumeral Muscular DystrophyUnited Kingdom
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Hillel Yaffe Medical CenterRecruiting
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Robert Jones and Agnes Hunt Orthopaedic and District...CompletedFacioscapulohumeral Muscular Dystrophy
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Bioblast Pharma Ltd.CompletedMuscular Dystrophy, Oculopharyngeal (OPMD)Canada
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Rigshospitalet, DenmarkUnknownOculopharyngeal Muscular DystrophyDenmark
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Centre Hospitalier Universitaire de NiceCompletedFacioscapulohumeral Muscular DystrophyFrance
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University Hospital, AngersFederico II University; University of Modena and Reggio EmiliaNot yet recruitingFacioscapulohumeral Muscular Dystrophy