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Clinical Trials on Muscular Dystrophies
Total 50211 results
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Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of Kansas Medical CenterSeattle Children's Hospital; University of Rochester; University of Nevada, Reno and other collaboratorsRecruitingFSHDUnited States, Canada, United Kingdom
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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Centre d'Investigation Clinique et Technologique...Unknown
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Duke UniversityCompleted
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
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Grete Andersen, MDAP Moeller Foundation; The Danish Rheumatism Association; Aase and Ejnar Danielsens... and other collaboratorsCompletedFacioscapulohumeral Muscle DystrophyDenmark
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Centre Hospitalier Universitaire de NiceCompletedFacio-Scapulo-Humeral DystrophyFrance
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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BioLeaders CorporationCompleted
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Summit TherapeuticsCompletedModified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietMuscular Dystrophy, DuchenneUnited Kingdom
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Ohio State UniversityCompletedMuscular Dystrophy, Facioscapulohumeral
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PTC TherapeuticsCooperative International Neuromuscular Research Group; The John Walton Muscular...Active, not recruitingMuscular Dystrophy, DuchenneGermany, France, United Kingdom, Brazil, Italy, Austria, Sweden, Czechia, Greece, Hungary, Israel, Latvia, Norway, Portugal, Romania, Slovenia
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BioMarin PharmaceuticalTerminatedMuscular DystrophiesUnited States, Canada
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Centre Hospitalier Universitaire de Saint EtienneÖrebro University, Sweden; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
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Hoffmann-La RocheRecruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Denmark, United Kingdom, Italy
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Spain, Italy, Denmark, Canada, Germany, France, Netherlands, United Kingdom
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Fulcrum TherapeuticsCompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, France, Italy
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy 1Netherlands
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Stanford UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of California... and other collaboratorsCompletedMuscular Dystrophy, DuchenneUnited States
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Centre Hospitalier Universitaire de NiceRecruitingType 1 Facioscapulohumeral Muscular DystrophyFrance
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Netherlands, France, Italy
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Grete Andersen, MDCompletedFSHD - Facioscapulohumeral Muscular DystrophyDenmark
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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University of Southern CaliforniaCompletedRecessive Dystrophic Epidermolysis Bullosa
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University of Southern CaliforniaCompleted
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King's College LondonUnknownRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Stanford UniversityTerminatedEpidermolysis Bullosa DystrophicaUnited States
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GAAD Medical Research Institute Inc.UnknownMuscular DystrophiesCanada
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University of Southern CaliforniaRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Stanford UniversityRecruitingEpidermolysis Bullosa DystrophicaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Phoenicis TherapeuticsNot yet recruitingDystrophic Epidermolysis BullosaUnited States
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Thomas Jefferson UniversityOnconova Therapeutics, Inc.RecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Castle Creek Biosciences, LLC.Active, not recruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Gangnam Severance HospitalDaewoong Pharmaceutical Co. LTD.CompletedRecessive Dystrophic Epidermolysis BullosaKorea, Republic of
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King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom