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Clinical Trials on Myopathies, Structural, Congenital
Total 9079 results
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Hadassah Medical OrganizationUnknown
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Vastra Gotaland RegionEnrolling by invitationMusculoskeletal Diseases | Neuromuscular Diseases | Centronuclear Myopathy | Nemaline Myopathy | Congenital Myopathy | Myosin Storage MyopathySweden
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DynacureWithdrawnCentronuclear MyopathyGermany, France
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DynacureTerminatedCentronuclear MyopathyFrance, Netherlands, United Kingdom, Belgium, Denmark, Germany
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DynacureWithdrawnCentronuclear Myopathy
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Institut de Myologie, FranceDynacureCompletedCentronuclear MyopathyFrance, Belgium, Germany, Italy, Spain
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Cure CMDUniversity of Chicago; Boston Children's Hospital; Valerion Therapeutics, LLC; Congenital...Completed
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Radboud University Medical CenterUMC UtrechtNot yet recruitingCentronuclear Myopathy | Nemaline Myopathy | Central Core Disease | Multi-Minicore DiseaseNetherlands
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Valerion Therapeutics, LLCInstitut de Myologie, France; GenethonCompletedMyotubular MyopathyFrance, Belgium, United States, Canada, Germany, Italy, Spain
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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University of FloridaAudentes TherapeuticsCompletedX-linked Myotubular MyopathyUnited States
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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Radboud University Medical CenterCompletedInspiratory Muscle Training | Nemaline MyopathyNetherlands
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Institut BergoniéAstraZeneca; National Cancer Institute, FranceNot yet recruitingAdvanced Solid TumorFrance
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University of California, San FranciscoEnrolling by invitationFetal Structural AnomaliesUnited States
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AORTICA GroupUniversity of SalamancaCompleted
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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Second Affiliated Hospital, School of Medicine,...CompletedCT Angiography | Marker; StructuralChina
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Akron Children's HospitalThomas C. Dispenza, M.D.; John R. Bockoven, M.D. M.B.A.CompletedHeart Murmurs | Congenital Heart Disease | Structural Heart DiseaseUnited States
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National Taiwan University HospitalNational Health Research Institutes, TaiwanCompletedCognitive Function | Brain Structural ConnectivityTaiwan
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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Nantes University HospitalCompletedAortic Bioprosthesis Structural Valve DysfunctionFrance
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East Carolina UniversityRecruitingVaccine Hesitancy | Structural Barriers | Vaccine TrustUnited States
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Centre Cardiologique du NordOspedale San Donato; University of Bern; Groupe Hospitalier Pitie-Salpetriere; Royal... and other collaboratorsWithdrawnRoss Operation | Pulmonary Autograft | Structural Valve DegenerationFrance
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Assistance Publique Hopitaux De MarseilleUnknownChildren Born Very Prematurely in Relation to Structural Brain Abnormalities
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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RenJi HospitalNot yet recruitingIdiopathic Inflammatory Myopathies
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Janssen Research & Development, LLCRecruitingMyositisUnited States, Korea, Republic of, Italy, United Kingdom, Hungary, Spain, Japan, Czechia, France, Germany, Canada, Mexico, Poland
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Peking University People's HospitalRecruitingIdiopathic Inflammatory MyopathiesChina
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University Hospital, BrestRecruiting
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The First Affiliated Hospital of Xiamen UniversityRecruiting
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University of ManchesterKarolinska Institutet; Eli Lilly and Company; Clinical Trials Unit, ManchesterCompletedIdiopathic Inflammatory MyopathiesUnited Kingdom
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Yale UniversityCompletedIdiopathic Inflammatory MyopathiesUnited States
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Benha UniversityUnknownIdiopathic Inflammatory MyopathiesEgypt
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCongenital Heart Disease | Structural Heart Disease | Pulmonary Artery HypertensionUnited States
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Northwestern UniversityTerminated
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University of Sao PauloCompletedPhysical Activity | Idiopathic Inflammatory MyopathiesBrazil
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Peking University People's HospitalUnknownInflammatory Myopathy
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University of ManchesterKing's College Hospital NHS Trust; Northern Care Alliance NHS Foundation Trust and other collaboratorsActive, not recruitingMyositis | Idiopathic Inflammatory MyopathyUnited Kingdom
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Peking University People's HospitalUnknown
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Hospital Universitari Vall d'Hebron Research InstituteNot yet recruitingAortic Valve Stenosis | Structural Valve Degeneration | Structural Valve DeteriorationSpain
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingFetal Structural AnomaliesUnited States
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Reata, a wholly owned subsidiary of BiogenAbbVieCompletedMItochondrial MyopathiesUnited States, Denmark