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Clinical Trials on Other Lipid Storage Disorders
Total 8965 results
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University of SienaCareggi HospitalCompletedInfant, Newborn, Diseases | Other Lipid Storage DisordersItaly
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AdventHealth Translational Research InstituteTakeda; Sanford-Burnham Medical Research InstituteActive, not recruitingObesity | Lipid Metabolism Disorders | Disorder of Lipid Storage and Metabolism | Metabolic DisorderUnited States
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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Maastricht University Medical CenterCompletedNeutral Lipid Storage DiseaseNetherlands
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Ankara UniversityAlexion PharmaceuticalsCompleted
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Assiut UniversityNot yet recruitingPsychiatric Problem | Wolman Disease
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
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Johns Hopkins UniversityVAP Diagnostics LabActive, not recruiting
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Sadat City UniversityRecruitingSchizophrenia | DyslipidemiasEgypt
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Children's Hospital Medical Center, CincinnatiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedWolman Disease | Cholesterol Ester Storage Disease | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2United States
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Fundació Sant Joan de DéuParc Sanitari Sant Joan de Déu; Hospital del Mar; Hospitales Universitarios Virgen... and other collaboratorsNot yet recruitingPsychosis | Mother-Child Relations
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Massachusetts General HospitalAlexion PharmaceuticalsUnknownCholesterol Ester Storage Disease | Lysosomal Acid Lipase DeficiencyUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Alexion PharmaceuticalsTerminated
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Alexion PharmaceuticalsNo longer availableLysosomal Acid Lipase Deficiency
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Massachusetts General HospitalGlaxoSmithKlineCompletedSchizophrenia | Schizoaffective Disorder | Bipolar Disorder | Hypercholesterolemia | High TriglyceridesUnited States
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University of AarhusThe Danish Dairy Research Foundation, DenmarkRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Fondazione SISA (Societa Italiana per lo Studio...Recruiting
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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Assy NimerUnknownNon-alcoholic Fatty Liver Disease | Cholesterol Ester Storage DiseaseIsrael
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CENTOGENE GmbH RostockWithdrawnCholesterol Ester Storage Disease | Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Wolman TypeGermany, India, Sri Lanka
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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Medical University of South CarolinaEli Lilly and CompanyWithdrawnSchizophrenia | Bipolar DisorderUnited States
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New York State Psychiatric InstituteTemple University; The Zucker Hillside Hospital; Feinstein Institutes for Medical...Not yet recruitingSchizophrenia | Schizoaffective Disorder | Delusional Disorder | Schizophreniform Disorders | Other Specified Schizophrenia Spectrum and Other Psychotic Disorder
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingLipid Metabolism DisorderUnited States
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Université de SherbrookeHospices Civils de LyonCompleted
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Merck Sharp & Dohme LLCCompletedLipid Metabolism Disorder
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Hospices Civils de LyonUnknownLiver Post-transplant PatientsFrance
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Zydus Lifesciences LimitedTerminatedObesity | Lipid DisordersIndia
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TakedaActive, not recruiting
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CENTOGENE GmbH RostockActive, not recruiting
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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Hospices Civils de LyonUnknownPatients Waiting for a Liver Transplant.France
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Hospital St. Joseph, Marseille, FranceCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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Amicus TherapeuticsCompleted
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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TakedaNot yet recruiting
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Duke UniversityRecruiting
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TakedaCompletedGaucher DiseaseUnited States