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Clinical Trials on PDGFR-Alpha D842V
Total 219 results
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Arog Pharmaceuticals, Inc.AvailableFLT3-ITD Mutation | FLT3/TKD Mutation | PDGFR-Alpha D842V | PDGFRA Gene AmplificationItaly
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Centre Leon BerardBlueprint Medicines CorporationActive, not recruitingGIST, Malignant | GIST | PDGFR-Alpha D842VFrance
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Arog Pharmaceuticals, Inc.Centre Leon Berard; Fox Chase Cancer CenterUnknownGIST With D842V Mutated PDGFRA GeneUnited States, France, Spain, Italy, Germany, Norway, Poland
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Grifols Therapeutics LLCRecruiting
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Vertex Pharmaceuticals IncorporatedCompletedAlpha1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland, Sweden, United Kingdom
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Grifols Therapeutics LLCGrifols Japan K.K.Completed
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Baxalta now part of ShireCompletedAlpha1-antitrypsin DeficiencyUnited States, Canada
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Baxalta now part of ShireTerminated
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Grifols Therapeutics LLCGrifols Japan K.K.CompletedAlpha1-Antitrypsin DeficiencyJapan
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Z Factor LimitedHammersmith Medicines Research; Centessa Pharmaceuticals plcTerminatedAlpha1 Anti-Trypsin DeficiencyUnited Kingdom
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Baxalta now part of ShireCompleted
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RWTH Aachen UniversityUnknown
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyUnited States
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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University of California, San FranciscoRecruitingAlpha-Thalassemia | Alpha Thalassemia Major | Alpha Thalassemia MinorUnited States
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CSL BehringCompletedEmphysema | Alpha 1-proteinase Inhibitor DeficiencyAustralia, Canada, Czech Republic, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden
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Johns Hopkins UniversityNational Institute on Drug Abuse (NIDA)Recruiting
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireTerminatedChronic Obstructive Pulmonary Disease | Alpha1-antitrypsin DeficiencyUnited States, Canada, Australia
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ShireWithdrawnChronic Obstructive Pulmonary Disease | Alpha1-antitrypsin Deficiency
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Accademia Italiana Medicina OsteopaticaCompleted
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CENTOGENE GmbH RostockWithdrawnAlpha-Mannosidase B Deficiency | Lysosomal Alpha B Mannosidosis | Alpha-Mannosidase DeficiencyIndia, Sri Lanka, Germany
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Arkansas Tech UniversityCompletedNo Condition Salivary Alpha AmylaseUnited States
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TakedaWithdrawnChronic Obstructive Pulmonary Disease (COPD) | Alpha1-Antitrypsin Deficiency
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National Taiwan University HospitalUnknown
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University of JenaCompletedEndogenous Conversion of Alpha Linolenic AcidGermany
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HaEmek Medical Center, IsraelCompletedHemolytic Anemia | Thalassemia AlphaIsrael
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Zymenex A/SEuropean CommissionUnknown
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Zymenex A/SEuropean CommissionCompleted
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Tanta UniversityRecruitingStress | Dexmedetomidine | Mechanical Ventilation | Propofol | Salivary Alpha AmylaseEgypt
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Assiut UniversityNot yet recruitingPre-Eclampsia | Intrauterine Growth Restriction | alpha1 Anti-trypsin
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Guangxi Medical UniversityCompletedFull Gene Sequences of c-KIT、PDGFRA and DOG1 Are Analyzed With the Screening-sequencing Approach | Investigate the Characteristics and Variations Associated With the Different Gene Mutations of c-KIT、PDGFRA and DOG1 in GIST Patients
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The 923rd Hospital of Joint Logistics Support Force...Guangzhou Reforgene Medicine Co., Ltd.RecruitingHemoglobinopathies | Hereditary Diseases | Alpha Thalassemia Hemoglobin H Constant SpringChina
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University of California, San FranciscoCalifornia Institute for Regenerative Medicine (CIRM)Enrolling by invitationHemoglobinopathies | Alpha Thalassemia Major | Thalassemia Major | Fetal Hydrops | Hemoglobinopathy; With Thalassemia | Fetal Anemia | Alpha; Thalassemia | Thalassemia Alpha | A-ThalassemiaUnited States
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Zymenex A/SEuropean CommissionCompletedAlpha MannosidosisCzechia, Germany, Norway, United Kingdom
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Hospices Civils de LyonCompleted
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Agios Pharmaceuticals, Inc.Active, not recruitingNon-Transfusion-dependent Alpha-Thalassemia | Non-Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United Kingdom, Malaysia, United States, Netherlands, Bulgaria, Turkey, Italy, Canada, Brazil, France, United Arab Emirates, Denmark, Greece, Lebanon, Saudi Arabia
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Grifols Therapeutics LLCCompletedAlpha₁-Antitrypsin DeficiencyUnited States
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Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
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Thomayer University HospitalMasaryk UniversityRecruiting
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University of FloridaAlpha-1 FoundationEnrolling by invitation
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Permian Health Lung InstituteThe Gambia Committee on Traditional Practices Affecting the Health of Women...Not yet recruitingCOPD | Lung Function Decreased | Alpha 1-AntitrypsinGambia
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CSL BehringCompletedCystic FibrosisBulgaria, Hungary, Poland, United Kingdom
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Michael Campos, MDCSL BehringCompletedAlpha 1 Antitrypsin DeficiencyUnited States
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Hospices Civils de LyonCompletedChildren With a Deficiency of Alpha-1 AntitrypsinFrance
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); N... and other collaboratorsTerminatedLiver Cirrhosis | Alpha-1-antitrypsin DeficiencyUnited States
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Alnylam PharmaceuticalsTerminatedZZ Type Alpha-1 Antitrypsin Deficiency Liver DiseaseUnited Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingPortal Hypertension | Cholestasis | Liver Fibrosis | Biliary Atresia | Alagille Syndrome | Alpha1 Anti-Trypsin DeficiencyUnited States, Canada