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Clinical Trials on Paroxysmal Nocturnal Hemoglobinuria PNH
Total 142 results
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AKARI TherapeuticsRadboud University Medical CenterCompletedParoxysmal Nocturnal Haemoglobinuria (PNH)Netherlands
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Apellis Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Paroxysmal HemoglobinuriaMalaysia, United States, Czechia, France, Netherlands, Serbia, Spain, Thailand, United Kingdom
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria PNHLithuania, Japan, Czechia
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Alexion PharmaceuticalsAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, New Zealand, Korea, Republic of, Italy
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AKARI TherapeuticsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Kazakhstan, Lithuania, Sri Lanka
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Alexion PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Czech Republic, Italy, Poland, United Kingdom
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AlexionActive, not recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Italy, Canada, Korea, Republic of, New Zealand, Spain, Turkey
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Belgium, France, Italy, Japan, Spain, Taiwan, United Kingdom, United States, Canada, Czechia, Germany, Sweden, Singapore, Korea, Republic of, Russian Federation, Austria, Poland, Argentina, Australia, Brazil, Estonia, Malaysia, Mexico, Thaila... and more
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Korea, Republic of, Canada, France, Germany, Spain, United Kingdom, Japan, Australia, Italy, Netherlands
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Australia, Canada, Denmark, Finland, Germany, Hungary, New Zealand
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Alnylam PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Spain, United Kingdom
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King's College Hospital NHS TrustCompletedParoxysmal Nocturnal HaemoglobinuriaUnited Kingdom
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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BioCryst PharmaceuticalsTerminatedBCX9930 for Treatment of PNH in Subjects With Inadequate Response to C5 Inhibitor Therapy (REDEEM-1)Paroxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Hungary, France, Italy, Spain
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ADARx Pharmaceuticals, Inc.ADARx Australia Pty LtdRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)Australia
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NovelMed TherapeuticsNot yet recruitingPNH - Paroxysmal Nocturnal Hemoglobinuria
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Alexion Pharmaceuticals, Inc.Achillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, United States, Italy
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Hong Kong, Hungary, Korea, Republic of, Malaysia, United Kingdom
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Wuhan Createrna Science and Technology Co., LtdNot yet recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)
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BioCryst PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)Malaysia, South Africa, Korea, Republic of
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AKARI TherapeuticsEnrolling by invitationParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Ra Pharmaceuticals, Inc.TerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Australia, Canada, Finland, Germany, Hungary, New Zealand, United Kingdom
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal Hemoglobinuria | PNHUnited Kingdom, Austria, South Africa
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Alexion PharmaceuticalsCompletedPNHKorea, Republic of, Australia
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Novartis PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | C3 Glomerulopathy (C3G)
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHKorea, Republic of, Canada, France, Germany, Spain, Taiwan, United Kingdom
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Apellis Pharmaceuticals, Inc.Completed
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHAustralia, France, United Kingdom, Belgium, Germany, Netherlands, Ireland, United States, Switzerland, Italy
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH) With Signs of Active HemolysisItaly, Germany, France
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Regeneron PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | CD55-deficient Protein-losing Enteropathy (PLE) | CD59 Deficiency
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedLeukemia | Lymphoblastic Lymphoma | Myelodysplastic Syndrome | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Allogeneic Stem Cell Transplant | Non-HodgkinsUnited States
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Alexion PharmaceuticalsCompletedParoxysmal Hemoglobinuria, NocturnalUnited States, Australia, Belgium, Canada, Germany, Italy, Spain, Sweden, United Kingdom, France, Ireland, Netherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal Hemoglobinuria, NocturnalUnited States
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Alexion Pharmaceuticals, Inc.AvailableParoxysmal Nocturnal Hemoglobinuria | PNH | Extravascular Hemolysis
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CARE Pharma Shanghai Ltd.CompletedParoxysmal Nocturnal Hemoglobinuria, Natural History StudyChina
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Paroxysmal Hemoglobinuria, NocturnalUnited States
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal HemoglobinuriaUnited States
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Hemoglobinuria, NocturnalFrance, Korea, Republic of, Italy, Japan, Germany, Hungary, Netherlands
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AO GENERIUMCompletedParoxysmal Nocturnal Hemoglobinuria | Marchiafava-Micheli Syndrome | Paroxysmal HemoglobinuriaRussian Federation
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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Kira Pharmacenticals (US), LLC.Not yet recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdCompletedParoxysmal Nocturnal HemoglobinuriaChina
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BioCryst PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Austria, South Africa
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Alexion PharmaceuticalsCMIC Co, Ltd. JapanCompletedParoxysmal Nocturnal Hemoglobinuria