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Clinical Trials on Peroxisomal Biogenesis Disorders
Total 60 results
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NCT01626092CompletedConditions: Lysosomal Storage Disease; Peroxisomal Disorder
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NCT03163771RecruitingConditions: Peroxisomal Disorders; Diagnoses Disease
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NCT00004348Unknown statusConditions: Beta-Oxidation Disorder; Peroxisomal Disorders
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NCT00004442TerminatedConditions: Infantile Refsum's Disease; Zellweger Syndrome; Bifunctional Enzyme Deficiency; Adrenoleukodystrophy
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NCT00383448CompletedConditions: Adrenoleukodystrophy; Metachromatic Leukodystrophy; Globoid Cell Leukodystrophy; Tay Sachs Disease; Sandhoffs Disease; Wolman Disease; I-Cell Disease; Sanfilippo Syndrome; GM1 Gangliosidosis
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NCT01838941CompletedConditions: Peroxisome Biogenesis Disorders
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NCT00007020CompletedConditions: Infantile Refsum's Disease; Zellweger Syndrome; Adrenoleukodystrophy; Peroxisomal Disorders; Cholestasis
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NCT02171104RecruitingConditions: Mucopolysaccharidosis Disorders; Hurler Syndrome; Hunter Syndrome; Maroteaux Lamy Syndrome; Sly Syndrome; Alpha-Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Glycoprotein Metabolic Disorders; Sphingolipidoses; Recessive Leukodystrophies; Globoid Cell Leukodystrophy; Metachromatic Leukodystrophy; Niemann-Pick B; Niemann-Pick C Subtype 2; Sphingomyelin Deficiency; Peroxisomal Disorders; Adrenoleukodystrophy With Cerebral Involvement; Zellweger Syndrome; Neonatal Adrenoleukodystrophy; Infantile Refsum Disease; Acyl-CoA Oxidase Deficiency; D-Bifunctional Enzyme Deficiency; Multifunctional Enzyme Deficiency; Alpha-methylacyl-CoA Racmase Deficiency; Mitochondrial Neurogastrointestingal Encephalopathy; Severe Osteopetrosis; Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation); Inherited Metabolic Disorders
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NCT01043640CompletedConditions: Mucopolysaccharidosis; Hurler Syndrome; Hunter Syndrome; Maroteaux-Lamy Syndrome; Sly Syndrome; Alpha Mannosidosis; Fucosidosis; Aspartylglucosaminuria; Adrenoleukodystrophy (ALD); Krabbe Disease; Metachromatic Leukodystrophy (MLD); Sphingolipidoses; Peroxisomal Disorders
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NCT01668186RecruitingConditions: Peroxisome Biogenesis Disorder; Zellweger Spectrum Disorder; RCDP - Rhizomelic Chondrodysplasia Punctata; D-Bifunctional Protein Deficiency; Alpha-Methylacyl-CoA Racemase Deficiency; Peroxisomal Acyl-CoA Oxidase Deficiency; Peroxisomal Acyl-CoA Oxidase 2 Deficiency; ATP Binding Cassette Subfamily D Member 3 Gene Mutation; ACBD5 (AcylCoA Binding Domain 5) Deficiency; Adult Refsum Disease; Sterol Carrier Protein 2 Deficiency
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NCT04687007Not yet recruitingConditions: X-linked Adrenoleukodystrophy
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NCT04675749RecruitingConditions: X-linked Adrenoleukodystrophy
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NCT03856866CompletedConditions: Zellweger Syndrome; Peroxisome Biogenesis Disorders
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NCT04569162RecruitingConditions: RCDP - Rhizomelic Chondrodysplasia Punctata; RCDP1; RCDP2; RCDP3; RCDP4; RCDP5
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NCT04031287RecruitingConditions: Rhizomelic Chondrodysplasia Punctata
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NCT04528706RecruitingConditions: Cerebral Adrenoleukodystrophy
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NCT04303416Not yet recruitingConditions: Adrenomyeloneuropathy; Adrenoleukodystrophy
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NCT04090268RecruitingConditions: Leukemia, Myeloid, Acute; Leukemia, B-cell; Leukemia, T Cell; Lymphoma, Hodgkin; Lymphoma, Non-Hodgkin; Drepanocytosis; Thalassemia Major; Adrenoleukodystrophy
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NCT03864523CompletedConditions: Adrenomyeloneuropathy; X-linked Adrenoleukodystrophy
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NCT03852498RecruitingConditions: Cerebral Adrenoleukodystrophy (CALD)
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NCT03810508RecruitingConditions: Charcot-Marie-Tooth Disease; Hereditary Motor and Sensory Neuropathy IV
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NCT03789721RecruitingConditions: ALD (Adrenoleukodystrophy); Adrenoleukodystrophy; Cerebral Adrenoleukodystrophy
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NCT03727555RecruitingConditions: X-linked Adrenoleukodystrophy
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NCT03627416CompletedConditions: Hereditary Spastic Paraplegia; Adrenomyeloneuropathy
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NCT03513328RecruitingConditions: Bone Marrow Failure Syndrome; Thalassemia; Sickle Cell Disease; Diamond Blackfan Anemia; Acquired Neutropenia in Newborn; Acquired Anemia Hemolytic; Acquired Thrombocytopenia; Hemophagocytic Lymphohistiocytoses; Wiskott-Aldrich Syndrome; Chronic Granulomatous Disease; Common Variable Immunodeficiency; X-linked Lymphoproliferative Disease; Severe Combined Immunodeficiency; Hurler Syndrome; Mannosidosis; Adrenoleukodystrophy