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Clinical Trials on Phenylketonuria (PKU)
Total 177 results
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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University of Southern CaliforniaBioMarin PharmaceuticalCompleted
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Stanford UniversityBioMarin PharmaceuticalWithdrawnClassical Phenylketonuria(PKU)
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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University of GlasgowUnknownPhenylketonuria (PKU)United Kingdom
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Dr. Linda RandolphBioMarin PharmaceuticalTerminated
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University of GlasgowCompletedPhenylketonuria (PKU)United Kingdom
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Nutricia ResearchCompleted
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BioMarin PharmaceuticalActive, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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University of ZurichCompletedPhenylketonuria (PKU) and HyperphenylalaninemiaSwitzerland
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BioMarin PharmaceuticalCompletedHyperphenylalaninemia (HPA) Due to Phenylketonuria (PKU) or Tetrahydrobiopterin (BH4) DeficiencySweden, France, Italy, Spain, Germany, Netherlands, Austria, Slovakia, Portugal
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Taipei Veterans General Hospital, TaiwanBioMarin PharmaceuticalUnknownPAH Deficiency | Pku Phenylketonuria
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
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Homology Medicines, IncTerminated
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Children's National Research InstituteGeorgetown UniversityWithdrawn
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Oregon Health and Science UniversityTerminated
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Nutricia ResearchCompleted
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Vitaflo International, LtdRecruitingPhenylketonurias | PKU | Maple Syrup Urine Disease | Homocystinuria | Glutaric Acidemia I | Hereditary TyrosinemiaUnited Kingdom
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University Hospital, ToursCompletedAdult Phenylketonuria Non Treated PatientsFrance
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Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science... and other collaboratorsTerminated
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University of GuelphMcMaster University; Laval UniversityNot yet recruitingAutosomal Recessive Disorder (Genetic Carriers of PKU)Canada
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Vitaflo International, LtdUniversity College London HospitalsRecruiting
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University of GuelphMcMaster UniversityRecruitingAutosomal Recessive Disorder (Genetic Carriers of PKU)Canada
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BioMarin PharmaceuticalSyneos HealthRecruitingPhenylketonuria, MaternalGermany, United States, Italy
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Lumos DiagnosticsAptatek BiosciencesRecruiting
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SanofiRecruiting
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTDRecruiting
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University Hospital, GrenobleRecruitingMetabolic Diseases | PhenylketonuriaFrance
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APR Applied Pharma Research s.a.Recruiting
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University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University...RecruitingPhenylketonuriasSwitzerland
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University Hospital, LilleNot yet recruiting
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
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Klaus ParhoferTerminated
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
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Rubius TherapeuticsTerminated
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Ludwig-Maximilians - University of MunichEuropean UnionCompletedPhenylketonuriaGermany, Italy, Spain, United Kingdom
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States