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Clinical Trials on Sanfilippo Disease Type A
Total 57548 results
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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ShireCompletedSanfilippo Syndrome Type AUnited States
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Turkey
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Germany, Turkey
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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Samsung Medical CenterNot yet recruitingSanfilippo Syndrome A
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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ShireCompletedSanfilippo Syndrome Type BUnited States, United Kingdom, Germany
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo Syndrome)Spain, Netherlands, United Kingdom, United States, Brazil
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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Shanghai Jiao Tong University School of MedicineCompletedBotulinum Toxin, Type A
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Peking UniversityCompletedBotulinum Toxins, Type A | SmilingChina
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Peking UniversityCompletedBotulinum Toxins, Type A | SmilingChina
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Peking UniversityCompletedBotulinum Toxins, Type A | SmilingChina
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Loma Linda UniversityAllerganCompletedMuscle Strength | Botulinum Toxins, Type AUnited States
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Assistance Publique Hopitaux De MarseilleUnknownAcute Type A DissectionFrance
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Hospices Civils de LyonCompletedHighlights a New Clinical Sign Which Point Out a Meniscus Posterior Luxation Because of a MCA-type DLMFrance
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Alexion PharmaceuticalsTerminatedMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BUnited Kingdom
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Cairo UniversityRecruiting
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Centre Hospitalier Universitaire DijonTerminatedPatients With Type 1 or Type 2 Diabetes | Patients With a Type A or B Behaviour ProfileFrance
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Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
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Vanderbilt University Medical CenterHuman Vaccines ProjectCompletedVaccine Reaction | Influenza | Influenza, Human | Influenza A | Influenza Type B | Influenza A H3N2 | Influenza A H1N1United States
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Mansoura UniversityActive, not recruitingBulk-fill Which is Special Type of Resin Composite | Bisphenol A-Glycidyl MethacrylateEgypt
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Helsinki University Central HospitalAssistance Publique - Hôpitaux de Paris; Universitaire Ziekenhuizen KU Leuven; Azienda Ospedaliera Universitaria Integrata Verona and other collaboratorsActive, not recruitingType A Aortic DissectionSpain, Belgium, Finland, United Kingdom, Germany, Italy, Czechia, France
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Lundquist Institute for Biomedical Innovation at...Not yet recruitingMucopolysaccharidosis III | Sanfilippo SyndromeUnited States
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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CerbaXpertNot yet recruitingWoman Suffering From a Pathology Frequently Associated With the Presence of These Anti-autoantibodies Type-I Interferons
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Shanghai Zhongshan HospitalCompletedType A Aortic Dissection
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CryoLife, Inc.Active, not recruitingType A Aortic DissectionChina
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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Gruppo Italiano Studio LinfomiUnknownChronic Lymphocytic Leukemia Stage A(0) | Chronic Lymphocytic Leukemia Stage A(I) | Chronic Lymphocytic Leukemia Stage A(II)Italy
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Universidad Autonoma de Nuevo LeonCompletedPlantar Fascitis | Botulinum Toxins, Type AMexico
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University Hospital, Strasbourg, FranceUnknown
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ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
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Shanghai Zhongshan HospitalShanghai Changzheng HospitalRecruitingChronic Lymphocytic Leukemia Stage A(0) | Chronic Lymphocytic Leukemia Stage A(I) | Chronic Lymphocytic Leukemia Stage A(II) | Chronic Lymphocytic Leukaemia Stage B(I)China
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo B Syndrome)United Kingdom
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Yunlong FanCompletedCumulative Sum Learning Curves | Stanford Type A Aorta DissectionChina
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Hospital Universitario La FeCompletedBotulinum Toxin Type A | Rives Repair | Large Midline Hernia | Component SeparationSpain
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Chulalongkorn UniversityHIV-NAT, Thai Red Cross - AIDS Research Centre; Chula Clinical Research Center...RecruitingSafety of a Single Dose of COMVIGEN Vaccine | Reactogenicity of a Single Dose of COMVIGEN Vaccine | Immunogenicity of a Single Dose of COMVIGEN Vaccine | Safety of a Single Dose of BIVALENT Pfizer/BNT Vaccine | Reactogenicity of a Single Dose of BIVALENT Pfizer/BNT Vaccine | Immunogenicity...Thailand
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Wolfson Medical CenterCompletedA Positive or a Negative Brain SPECTIsrael
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Assiut UniversityRecruitingOpen Type III (A&B)Pediatric and Adolescent Tibial Shaft Fractures | Ilizarov FixationEgypt
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Carilion ClinicSanofiTerminatedAdvanced Endometrial Adenocarcinoma, Stage III A, B, CUnited States
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E-DA HospitalUnknownTennis Elbow | Type A Botulinum ToxinTaiwan
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Beijing Anzhen HospitalUnknownStanford Type A Aortic DissectionChina