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Clinical Trials on Sanfilippo Syndrome Type A
Total 3544 results
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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ShireCompletedSanfilippo Syndrome Type AUnited States
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Turkey
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Germany, Turkey
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Samsung Medical CenterNot yet recruitingSanfilippo Syndrome A
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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ShireCompletedSanfilippo Syndrome Type BUnited States, United Kingdom, Germany
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo Syndrome)Spain, Netherlands, United Kingdom, United States, Brazil
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Alexandria UniversityUnknownDiagnoses, Syndromes, and Conditions | Sepsis Following A Procedure
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Lundquist Institute for Biomedical Innovation at...Not yet recruitingMucopolysaccharidosis III | Sanfilippo SyndromeUnited States
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Assistance Publique Hopitaux De MarseilleCompletedA Potential Infectious Respiratory Clinical Syndrome | Potential Clinical Urinary Infectious Syndrome | A Potential Clinical Abdominal Infection SyndromeFrance
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Shanghai Jiao Tong University School of MedicineCompletedBotulinum Toxin, Type A
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ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
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Peking UniversityCompletedBotulinum Toxins, Type A | SmilingChina
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Peking UniversityCompletedBotulinum Toxins, Type A | SmilingChina
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Peking UniversityCompletedBotulinum Toxins, Type A | SmilingChina
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Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
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Nanjing Medical UniversityBeijing Anzhen HospitalCompletedAcute Aortic Syndrome | Type A Aortic DissectionChina
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Loma Linda UniversityAllerganCompletedMuscle Strength | Botulinum Toxins, Type AUnited States
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationActive, not recruitingMucopolysaccharidoses | Mucopolysaccharidosis VI | Morquio A Syndrome | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio Syndrome A | Morquio SyndromeBrazil
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Assistance Publique Hopitaux De MarseilleUnknownAcute Type A DissectionFrance
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China Medical University HospitalUnknownA Study of Clinical and Genetic Mutations in a Family of Neuromyotonia, so Called Isaac's SyndromeTaiwan
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First Affiliated Hospital Xi'an Jiaotong UniversityCompleted
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo B Syndrome)United Kingdom
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Hospices Civils de LyonCompletedHighlights a New Clinical Sign Which Point Out a Meniscus Posterior Luxation Because of a MCA-type DLMFrance
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AGIR à DomWithdrawnObstructive Sleep Apnea Syndrome | Melanoma With a Breslow's Thickness ≥ 1mmFrance
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaCompletedHepatocellular Carcinoma | Acquired Immunodeficiency Syndrome Virus | Hepatitis, Viral, Non-A, Non-B, Parenterally-TransmittedSpain
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First Affiliated Hospital Xi'an Jiaotong UniversityZhejiang Provincial People's Hospital; Qinghai People's Hospital; Second Affiliated...Not yet recruitingComplication of Surgical Procedure | Aortic Diseases | Type A Aortic DissectionChina
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Alexion PharmaceuticalsTerminatedMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BUnited Kingdom
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Cairo UniversityRecruiting
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Cyclacel Pharmaceuticals, Inc.SuspendedLeukemia | Myelodysplastic Syndrome(MDS)United States
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Second Affiliated Hospital, School of Medicine,...CompletedDevelopment and Validation of a Prediction Model for Refeeding Syndrome in ICU Patients Undergoing Enteral NutritionChina
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Mansoura UniversityActive, not recruitingBulk-fill Which is Special Type of Resin Composite | Bisphenol A-Glycidyl MethacrylateEgypt
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Centre Hospitalier Universitaire DijonTerminatedPatients With Type 1 or Type 2 Diabetes | Patients With a Type A or B Behaviour ProfileFrance
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University of GroningenWithdrawnComplex Regional Pain Syndrome Type I of the Upper LimbNetherlands
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Ruhr University of BochumUnknownComplex Regional Pain Syndrome Type I of the Upper LimbGermany
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Vanderbilt University Medical CenterHuman Vaccines ProjectCompletedVaccine Reaction | Influenza | Influenza, Human | Influenza A | Influenza Type B | Influenza A H3N2 | Influenza A H1N1United States
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UPECLIN HC FM Botucatu UnespUnknownHIV Infections | Acquired Immune Deficiency Syndrome | Hepatitis, Viral, Non-A, Non-B, Parenterally-TransmittedBrazil