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Clinical Trials on Sickle Beta Thalassemia
Total 1931 results
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M.D. Anderson Cancer CenterWithdrawnSickle Cell Disease | Sickle Beta Thalassemia | Beta Thalassemia Major | Sickle Cell-SS Disease | Sickle Beta 0 Thalassemia | Sickle Beta Plus ThalassemiaUnited States
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University of British ColumbiaCompletedSickle Cell Disease | Beta-Thalassemia | Sickle Cell Trait | Sickle Cell-Beta Thalassemia | Sickle Cell-SS DiseaseCanada, Nepal
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National Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell Anemia | Sickle Beta Thalassemia | Sickle Cell Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Pain | Hbss | Hbsc | Sickle Cell Syndrome VariantUnited States
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Kenneth Ataga, MDAugusta UniversityCompletedSickle Cell Anemia | Sickle - Beta Thalassemia
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Nova Laboratories LimitedCompletedSickle Cell Disease | Sickle Cell Hemoglobin C | Sickle Cell-beta-thalassemia | Sickle-Cell; Hemoglobin Disease, ThalassemiaUnited Kingdom, Jamaica
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany
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National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
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Phoenicia BioScienceNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Beta Thalassemia IntermediaUnited States, Canada
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Northwell HealthCompletedSickle Cell Disease | Beta Thalassemia-MajorUnited States
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Editas Medicine, Inc.Not yet recruitingSickle Cell Disease | Hemoglobinopathies | Transfusion-dependent Beta-Thalassemia
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Emory UniversityPatient-Centered Outcomes Research InstituteCompletedSickle Cell Disease | Sickle Cell Anemia | Hemoglobin SC | Hemoglobin SS | Hemoglobin Beta ThalassemiaUnited States
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Assiut UniversityNot yet recruitingSickle Cell Disease, Beta Thalassemia Intermedia
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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bluebird bioCompletedSickle Cell Disease | Beta-Thalassemia MajorFrance
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Hillel Yaffe Medical CenterUnknownSickle Cell Anemia | Beta-Thalassemia | Microalbuminuria
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)Active, not recruiting
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
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Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
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EdiGene (GuangZhou) Inc.Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle Cell | Beta-Thalassemia | Hematopoietic Stem Cell TransplantationUnited States, Canada
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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Institute of Hematology & Blood Diseases Hospital...EdiGene Inc.; The Affiliated Hospital Of Guizhou Medical University; Zunyi Medical...Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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EdiGene (GuangZhou) Inc.PLA 923 HospitalActive, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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National Institute of Allergy and Infectious Diseases...RecruitingMalaria | Sickle Cell Disease | Alpha and Beta Thalassemia | Human PhysiologyUnited States
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Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Tanta UniversityUnknownStudy of The Therapeutic Benefits of Al-hijamah in Children With Beta Thalassemia Major (Al-hijamah)AL-Hijama in Thalassmia MajorEgypt
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Ain Shams UniversityUnknownSickle Cell Disease | Beta-thalassemia Major | Iron HemosiderosisEgypt
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
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CelgeneTerminatedBeta Thalassemia Intermedia | Beta Thalassemia MajorFrance, United Kingdom, Italy, Greece
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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Editas Medicine, Inc.RecruitingHemoglobinopathies | Thalassemia Major | Thalassemia Intermedia | Transfusion Dependent Beta ThalassemiaUnited States, Canada
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
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Jeffrey Zwicker, MDQuercegen PharmaceuticalsWithdrawnSickle Cell Disease | Sickle Cell-Beta0-Thalassemia
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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Children's Hospital of PhiladelphiaNot yet recruiting
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityNot yet recruiting
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Bristol-Myers SquibbRecruiting
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Assiut UniversityRecruiting
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...RecruitingBeta-ThalassemiaUnited States, Turkey, Italy, Thailand, Germany, Greece
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Rare Partners srl Impresa SocialeUniversità degli Studi di FerraraCompletedBeta-ThalassemiaItaly