- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Sickle Beta Thalassemia
Total 1932 results
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Acceleron Pharma Inc. (a wholly owned subsidiary...Completed
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University Hospital of PatrasCompleted
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IRCCS San RaffaeleOrchard Therapeutics; Fondazione TelethonUnknown
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Hoffmann-La RocheCompletedBeta-ThalassemiaItaly, Lebanon, Thailand
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Prolong PharmaceuticalsCompleted
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Shenzhen Geno-Immune Medical InstituteUnknown
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); George Papanicolaou HospitalCompletedBeta-ThalassemiaGreece
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Children's Hospital of Fudan UniversityCorrectSequence Therapeutics Co., LtdNot yet recruiting
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityRecruiting
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Assiut UniversityNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); Genzyme, a Sanofi Company; George Papanicolaou HospitalCompleted
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Royal Brompton & Harefield NHS Foundation TrustCORDA, The Heart Charity; Apotex Inc.; The Cooley's Anemia Foundation,; The UK...UnknownBeta-ThalassemiaItaly
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Aga Khan UniversityCompletedBeta Thalassemia Major
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China Medical University HospitalCompleted
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Boston UniversityMahidol UniversityCompletedBeta Thalassemia IntermediaThailand
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion Dependent Beta-ThalassemiaChina
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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Sangamo TherapeuticsSanofiCompletedTransfusion Dependent Beta-thalassemiaUnited States
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Novartis PharmaceuticalsCompletedBeta Thalassemia Transfusion DependentItaly
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Tehran University of Medical SciencesNovartisUnknownBone Marrow Transplantation | Beta-ThalassemiaIran, Islamic Republic of
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Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
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Wolfson Medical CenterUnknownPatients With Thalassemia Intermedia, | Congenital Dyserythropoietic Anemia Type I
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National Institute of Allergy and Infectious Diseases...TerminatedAnemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Hemoglobin SC Disease | Thalassemia MajorUnited States
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncCompletedBeta-Thalassemia | Non-transfusion-dependent ThalassemiaGreece, Israel, Italy, Lebanon, Thailand
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Tanta UniversityUnknownNigella Sativa With Beta Thalassemia MajorEgypt
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Università degli Studi di FerraraAzienda Ospedaliero, Universitaria Pisana; Rare Partners srl Impresa Sociale; Azienda Ospedaliero, Universitaria MeyerRecruitingBeta-ThalassemiaItaly
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National Institute of Blood and Marrow Transplant...Completed
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Vifor (International) Inc.Labcorp Drug Development IncWithdrawnBeta-ThalassemiaUnited States, Bulgaria, Israel
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Dr.Saqib Hussain AnsariUnknownThalassemia, BetaPakistan
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Xiaofang SunNanfang Hospital of Southern Medical University; Third Affiliated Hospital,... and other collaboratorsUnknownBeta-Thalassemia
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Vanderbilt University Medical CenterWashington University School of Medicine; University of Alabama at BirminghamRecruitingStroke | Sickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Thalassemia | Sickle Cell-Beta0-ThalassemiaUnited States
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EmeraMedCompletedBeta Thalassemia MajorAlbania
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Nanfang Hospital of Southern Medical UniversityGuangdong Yike Gene Science and Technology CO.,LtdUnknownBeta Thalassemia MajorChina
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Ain Shams UniversityUnknownBeta Thalassemia MajorEgypt
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Boston UniversityHemaQuest Pharmaceuticals Inc.CompletedBeta Thalassemia IntermediaLebanon
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Tanta UniversityRecruitingBeta Thalassemia With Increased Tricuspid Regurgitant Jet VelocityEgypt
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Indonesia UniversityCompletedHemolysis | Oxidative Stress | Beta Thalassemia Major AnemiaIndonesia