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- US Clinical Trials Registry
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Clinical Trials on Thalassemia
Total 422 results
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Xiaofang SunNanfang Hospital of Southern Medical University; Third Affiliated Hospital,... and other collaboratorsUnknownBeta-Thalassemia
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Children's Hospital of Fudan UniversityCorrectSequence Therapeutics Co., LtdNot yet recruiting
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityRecruiting
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Shenzhen HemogenRecruiting
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Shanghai BDgene Co., Ltd.Shanghai Children's Medical CenterNot yet recruiting
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Assiut UniversityNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany
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Imara, Inc.Terminatedβ ThalassemiaIsrael, France, Malaysia, Turkey, Denmark, Georgia, Greece, Italy, Lebanon, Morocco, Netherlands, Tunisia, United Kingdom
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedB-ThalassemiaItaly, Greece
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); Genzyme, a Sanofi Company; George Papanicolaou HospitalCompleted
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Royal Brompton & Harefield NHS Foundation TrustCORDA, The Heart Charity; Apotex Inc.; The Cooley's Anemia Foundation,; The UK...UnknownBeta-ThalassemiaItaly
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Cairo UniversityRecruitingPulmonary Function | Physical Fitness | β-ThalassemiaEgypt
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Prothya BiosolutionsTerminated
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EmeraMedCompletedBeta Thalassemia MajorAlbania
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Nanfang Hospital of Southern Medical UniversityGuangdong Yike Gene Science and Technology CO.,LtdUnknownBeta Thalassemia MajorChina
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Novartis PharmaceuticalsWithdrawn
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Ain Shams UniversityUnknownBeta Thalassemia MajorEgypt
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Boston UniversityHemaQuest Pharmaceuticals Inc.CompletedBeta Thalassemia IntermediaLebanon
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Vanderbilt University Medical CenterMedical College of Wisconsin; VersitiCompletedSickle Cell Anemia (HbSS, or HbSβ-thalassemia0)United States
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CorrectSequence Therapeutics Co., LtdNot yet recruitingBeta-Thalassemia MajorChina
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Completedβ Thalassemia MajorChina
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Bioray LaboratoriesPLA 923 HospitalTerminated
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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First Affiliated Hospital of Guangxi Medical UniversityUnknown
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Boston UniversityMahidol UniversityCompletedBeta Thalassemia IntermediaThailand
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Pharmacosmos A/SICON plcRecruitingBeta Thalassemia Major AnemiaDenmark
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Central Hospital, Nancy, FranceNot yet recruitingBeta Thalassemia Major Anemia
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia
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Memorial Sloan Kettering Cancer CenterCompletedBeta Thalassemia Major | Congenital AnemiasUnited States
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Aghia Sophia Children's Hospital of AthensUnknownAsplenia | β-thalassemia MajorGreece
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion-dependent α-ThalassemiaChina
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Sun Yat-sen UniversityRecruitingThalassemia Major | Transfusion-dependent AnemiaChina
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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Sangamo TherapeuticsSanofiCompletedTransfusion Dependent Beta-thalassemiaUnited States
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Novartis PharmaceuticalsCompletedBeta Thalassemia Transfusion DependentItaly
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HaEmek Medical Center, IsraelCompletedHemolytic Anemia | Thalassemia AlphaIsrael
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Tehran University of Medical SciencesNovartisUnknownBone Marrow Transplantation | Beta-ThalassemiaIran, Islamic Republic of
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bluebird bioCompletedSickle Cell Disease | Beta-Thalassemia MajorFrance