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Clinical Trials on Toni-Debre-Fanconi Syndrome
Total 101 results
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPancytopenia | Fanconi's AnemiaUnited States
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University of MinnesotaUnknown
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University of MinnesotaCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Center for Research Resources (NCRR)James Whitcomb Riley Hospital for ChildrenCompletedThrombocytopenia | Dyskeratosis Congenita | Fanconi's Anemia | Shwachman Syndrome
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain
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Rocket Pharmaceuticals Inc.UnknownFanconi Anemia Complementation Group AUnited States
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Rocket Pharmaceuticals Inc.Enrolling by invitationFanconi Anemia | Fanconi Anemia Complementation Group ASpain
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedPreviously Treated Myelodysplastic Syndrome | Fanconi Anemia | de Novo Myelodysplastic Syndrome | Acute Myeloid Leukemia in RemissionUnited States, Brazil
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CENTOGENE GmbH RostockWithdrawnHypophosphatemia | Photophobia | Renal Fanconi SyndromeGermany, India, Sri Lanka
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaTerminated
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedFanconi AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Completed
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Severe Aplastic AnemiaUnited States
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Assistance Publique - Hôpitaux de ParisEuroFancolenCompleted
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Masonic Cancer Center, University of MinnesotaCompleted
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)CompletedFanconi AnemiaUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterCompleted
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Neena Kapoor, M.D.Withdrawn
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical...Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedFanconi AnemiaUnited States, Brazil
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompleted
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Boston Children's HospitalCompleted
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Masonic Cancer Center, University of MinnesotaCompletedFanconi AnemiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiCompletedFanconi AnemiaUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedFanconi Anemia | Severe Aplastic AnemiaUnited States
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Children's Hospital Medical Center, CincinnatiAmgenCompleted
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Eisai Inc.AvailableLennox Gastaut Syndrome | Primary Generalized Tonic-Clonic or Partial Onset SeizuresBelgium, Chile, Estonia, Hungary, Latvia, Lithuania, Poland, Spain
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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TESS Research FoundationBrown University; Stanford University; University of Texas Southwestern Medical...RecruitingEpilepsy | Movement Disorders | Rare Diseases | Genetic Disorder | Citrate Transporter Deficiency | SLC13A5 Deficiency | EIEE25 | Kohlschutter-Tonz Syndrome (Non-ROGDI) | Citrate Transporter Disorder | DEE25United States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Porteus, Matthew, MDRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting