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Clinical Trials on Tyrosinemias
Total 13 results
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency ...Kazakhstan
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Centre Hospitalier Régional de la CitadelleRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease ...Belgium
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Vitaflo International, LtdRecruitingPhenylketonurias | PKU | Maple Syrup Urine Disease | Homocystinuria | Glutaric Acidemia I | Hereditary TyrosinemiaUnited Kingdom
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Yassin Abdelghaffar Charity Center for Liver Disea...RecruitingHereditary Tyrosinemia, Type IEgypt
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Nutricia UK LtdCompletedPKU | TyrosinemiasUnited Kingdom
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain and more
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Sutphin DrugsUnknownHereditary Tyrosinemia, Type IIndia
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Cycle Pharmaceuticals Ltd.CompletedHereditary Tyrosinemia, Type ISouth Africa
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Cycle Pharmaceuticals Ltd.CompletedHereditary Tyrosinemia, Type ISouth Africa
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Cycle Pharmaceuticals Ltd.CompletedHereditary Tyrosinemia, Type ISouth Africa
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Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France