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Clinical Trials on Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant
Total 315 results
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Medical University of ViennaUnknownPolycystic Kidney, Type 1 Autosomal Dominant Disease | Polycystic Kidney, Type 2 Autosomal Dominant DiseaseAustria
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Changlin MeiThe First Affiliated Hospital with Nanjing Medical University; The First Affiliated... and other collaboratorsCompletedPolycystic Kidney, Type 1 Autosomal Dominant DiseaseChina
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Emory UniversityPKD FoundationCompleted
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Regulus Therapeutics Inc.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States, Belgium, United Kingdom, Russian Federation, France, Australia, Netherlands, Italy, Japan, Denmark, Romania, Poland, Canada, Argentina, Germany
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University of ZurichCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Switzerland
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Istanbul UniversityCompletedAutosomal Dominant Polycystic Kidney DiseaseTurkey
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University College, LondonWashington University School of Medicine; University of Washington; Alzheimer... and other collaboratorsNot yet recruitingAlzheimer Disease | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 1 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 2 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Amyloid Precursor Protein (Disorder)
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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Ministry of Health, Labour and Welfare, JapanUnknownKidney, Polycystic, Autosomal DominantJapan
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Medtronic VascularCompletedCoronary Artery Disease, Autosomal Dominant, 1United States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Recruiting
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Mario Negri Institute for Pharmacological ResearchOtsuka Pharmaceutical Italy S.r.l.CompletedAutosomal Dominant Polycystic Kidney DiseaseItaly
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Mayo ClinicUniversity of Kansas Medical CenterCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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CHU de ReimsCompletedAutosomal Dominant Polycystic Kidney DiseaseFrance
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Regional Hospital HolstebroAarhus University HospitalCompletedAutosomal Dominant Polycystic Kidney DiseaseDenmark
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University Hospital, BrestUnknownAutosomal Dominant Polycystic Kidney DiseaseFrance
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Federico II UniversityCompletedAutosomal Dominant Polycystic Kidney Disease
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University of ChicagoWithdrawn
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Mayo ClinicCompletedKidney Disease | Autosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Argentina, Australia, Belgium, Brazil, Canada, Czech Republic, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Mario Negri Institute for Pharmacological ResearchTerminatedSirolimus In Autosomal Dominant Polycystic Kidney Disease And Severe Renal Insufficiency (SIRENA-II)Autosomal Dominant Polycystic Kidney Disease (ADPKD)Italy
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University of Southern CaliforniaEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Korea Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Korea, Republic of
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseNetherlands
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Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney DiseaseJapan
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Kyorin UniversityOtsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney DiseaseJapan
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University of KansasCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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University of KansasCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Kadmon Corporation, LLCTerminatedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States
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Kyorin UniversityUnknown
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University of North Carolina, Chapel HillNational Institute of General Medical Sciences (NIGMS)CompletedRenal Disease | Autosomal Dominant Polycystic Kidney Disease | ADPKDUnited States
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Assistance Publique - Hôpitaux de ParisIPSEN pharmaceutical company, Boulogne-Billancourt, FranceCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKDFrance
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Cambridge University Hospitals NHS Foundation TrustAddenbrookes Charitable Trust; PKD Charity; British Renal Society & British Kidney...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited Kingdom
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University of PittsburghNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Andreas L. SerraUnknownAutosomal Dominant Polycystic Kidney DiseaseFrance, Switzerland, Germany, Netherlands, Belgium, Czech Republic, Italy, Spain, Turkey, United Kingdom
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Galapagos NVTerminatedAutosomal Dominant Polycystic Kidney DiseaseBelgium, Netherlands, Italy, Spain, Czechia, Germany, Poland
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Palladio BiosciencesCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Japan
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney DiseaseJapan
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Shanghai Changzheng HospitalUnknownAutosomal Dominant Polycystic Kidney Disease (ADPKD)China
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Yale UniversityTerminatedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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AceLink Therapeutics, Inc.Novotech (Australia) Pty LimitedCompletedAutosomal Dominant Polycystic KidneyAustralia
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Mei changlinUnknownHypertension | Autosomal Dominant Polycystic Kidney DiseaseChina
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University Medical Center GroningenRadboud University Medical Center; Erasmus Medical Center; Leiden University...UnknownAutosomal Dominant Polycystic Kidney Disease (ADPKD)Netherlands