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Clinical Trials on X-linked Severe Combined Immunodeficiency
Total 1601 results
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendedSevere Combined Immunodeficiency Disease, X-linkedUnited States
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Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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University of MiamiJackson Health SystemNo longer available
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National Institute of Allergy and Infectious Diseases...TerminatedGrowth Failure | X-linked Severe Combined Immunodeficiency (XSCID) | Growth Hormone ResistenceUnited States
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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National Institute of Allergy and Infectious Diseases...UnknownX-Linked Combined Immunodeficiency DiseasesUnited States
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National Institute of Allergy and Infectious Diseases...CompletedSevere Combined ImmunodeficiencyUnited States
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Children's Hospital of Chongqing Medical UniversityRecruiting
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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IRCCS San RaffaeleFondazione TelethonCompletedSevere Combined Immunodeficiency Syndrome
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Children's Hospital of Fudan UniversityThe First Affiliated Hospital of Zhengzhou University; Shanghai Children's... and other collaboratorsActive, not recruitingSevere Combined Immunodeficiency DiseaseChina
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National Human Genome Research Institute (NHGRI)CompletedSevere Combined Immunodeficiency SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...Enrolling by invitationSevere Combined Immune Deficiency (SCID)United States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of MedicineTerminatedSevere Combined Immunodeficiency Disease | Severe Primary Immunodeficiency Disorder | Undefined T Cell Deficiency Disorder | Wiskott-Aldrick SyndromeUnited States
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University of California, Los AngelesGreat Ormond Street Hospital for Children NHS Foundation TrustEnrolling by invitationAdenosine Deaminase Deficiency | Severe Combined Immunodeficiency (SCID)United States, United Kingdom
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencyNetherlands
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University of California, Los AngelesOrchard Therapeutics; California Institute for Regenerative Medicine (CIRM)CompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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Nantes University HospitalCompletedSevere Combined Immunodeficiency, AtypicalFrance
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingArtemis (DCLRE1C ) Deficient Severe Combined ImmunodeficiencyFrance
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited Kingdom
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University of California, Los AngelesWithdrawnSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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Fondazione TelethonEnrolling by invitationImmunologic Deficiency SyndromesItaly
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Fondazione TelethonCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyItaly
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Office of Rare... and other collaboratorsEnrolling by invitationOmenn Syndrome | Reticular Dysgenesis | Severe Combined Immunodeficiency (SCID) | XSCID | Leaky SCID | ADA SCIDUnited States, Canada
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Fondazione TelethonActive, not recruitingSevere Combined Immunodeficiency Due to ADA DeficiencyItaly
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedAdenosine Deaminase Deficiency | Severe Combined Immunodeficiencies (SCID)United Kingdom
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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Assistance Publique - Hôpitaux de ParisRecruitingPediatric Patients | Any Type of Severe Combined Immunodeficiency (SCID) | Partial HLA Incompatible Allogeneic Hematopoietic Stem Cell Transplantation (HSCT)France
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Grifols Therapeutics LLCCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Wiskott-Aldrich Syndrome | Agammaglobulinemia | Immunologic Deficiency SyndromeCanada, United States
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | X-linked Agammaglobulinaemia | Hyperimmunoglobulin M SyndromeUnited States
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Paul SzabolcsEnrolling by invitationChronic Granulomatous Disease (CGD) | Wiskott-Aldrich Syndrome | Severe Chronic Neutropenia | Severe Combined Immunodeficiency (SCID) | Immunodeficiency With Predominant T-cell Defect, Unspecified | Hyper IgE Syndromes | Hyper IgM Deficiencies | Mendelian Susceptibility to Mycobacterial Disease | Common...United States
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National Institute of Allergy and Infectious Diseases...CompletedImmunoproliferative DisorderUnited States
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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Taiga Biotechnologies, Inc.Not yet recruitingSevere Combined ImmunodeficiencyIsrael
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Donald B. Kohn, M.D.National Institutes of Health (NIH); FDA Office of Orphan Products DevelopmentCompletedSevere Combined ImmunodeficiencyUnited States
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King's College LondonUniversity of Sheffield; University of Manchester; National Health Service, United... and other collaboratorsRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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David WilliamsUniversity of California, Los Angeles; Boston Children's Hospital; Children's...CompletedSevere Combined ImmunodeficiencyUnited States
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St. Jude Children's Research HospitalCompletedSevere Combined ImmunodeficiencyUnited States
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University of California, San FranciscoRecruiting
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St. Jude Children's Research HospitalActive, not recruitingSevere Combined ImmunodeficiencyUnited States
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Association Pour l'Aide a la Recherche en Immunologie...CompletedSevere Combined ImmunodeficiencyFrance