- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: AAV8-RPGR
Total 138 results
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Opus Genetics, IncRecruiting
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Baxalta now part of ShireTerminatedHemophilia BTurkey, Spain
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Assiut UniversityCompleted
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
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MeiraGTx, LLCRecruitingGrade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Parotid GlandsUnited States, Canada
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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W. Michael HootenNational Institute on Drug Abuse (NIDA)Recruiting
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CSL BehringActive, not recruiting
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Benjamin GreenbergActive, not recruiting
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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Spaulding Rehabilitation HospitalNortheastern UniversityTerminatedGait Re-training in Healthy Subjects | Gait Re-training in Stroke SurvivorsUnited States
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Repertoire Immune MedicinesMerck Sharp & Dohme LLCTerminated
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHIV-1 Infected Adults With Controlled ViremiaUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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Repertoire Immune MedicinesTerminatedRPTR-168 in Patients With Human Papillomavirus Strain 16 (HPV-16) E6/E7 Positive Tumors and MelanomaMelanoma | Cervical Cancer | Head and Neck Squamous Cell CarcinomaUnited States
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaActive, not recruitingAchromatopsiaUnited Kingdom, United States
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The University of Texas Health Science Center at...CompletedProstate Biopsy | Antibiotic TherapyUnited States
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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uniQure France SASRecruitingMesial Temporal Lobe EpilepsyUnited States
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CSL BehringEnrolling by invitation
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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ViGeneron GmbHRecruiting
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Sangamo TherapeuticsCeregeneCompletedParkinson's DiseaseUnited States
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Celladon CorporationCompletedHeart Failure | Cardiomyopathies | Ischemic Cardiomyopathy | Non-ischemic CardiomyopathyUnited States, United Kingdom, Belgium, Germany, Poland, Israel, Netherlands, Hungary, Denmark, Sweden
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompleted
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National Institute of Neurological Disorders and...Completed
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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Spark TherapeuticsCompleted
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom