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Search clinical trials for: Migalastat
Total 56 results
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Amicus TherapeuticsRecruitingFabry DiseaseSpain, United States, Japan, Australia, France, Portugal
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Amicus TherapeuticsRecruiting
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Amicus TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
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Amicus TherapeuticsCompletedFabry DiseaseUnited States
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation TrustActive, not recruiting
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Amicus TherapeuticsTerminatedFabry DiseaseAustralia, United States, Italy, Spain, Belgium, Turkey, Brazil, Argentina, United Kingdom, Denmark, France, Canada, Egypt
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
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Amicus TherapeuticsCompletedFabry DiseaseUnited Kingdom, United States
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Amicus TherapeuticsCompletedFabry DiseaseCanada, Belgium, United States, Australia, Netherlands
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Amicus TherapeuticsCompleted
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Amicus TherapeuticsCompleted
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Amicus TherapeuticsCompletedOpen-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry DiseaseFabry DiseaseUnited States, Austria, United Kingdom, Argentina, Australia, Belgium, Brazil, Canada, Denmark, Egypt, France, Italy, Japan, Spain, Turkey
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Assistance Publique - Hôpitaux de ParisActelion; CRCM (Centres de Ressources et de Compétences de la Mucoviscidose)Completed
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Cliniques universitaires Saint-Luc- Université...Unknown
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ActelionCompleted
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University of WashingtonEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedContraceptionUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
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SanofiRecruitingFabry DiseaseItaly, United States, Austria, China, Czechia, Denmark, France, Germany, Greece, Japan, Korea, Republic of, Netherlands, Norway, Spain, Taiwan, Turkey, United Kingdom, Canada, Poland
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The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
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Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
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IRCCS Fondazione Stella MarisCompletedHereditary Spastic ParaparesisItaly
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
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University of SurreyThe Whiteley ClinicCompletedVaricose VeinsUnited Kingdom
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ActelionCompleted
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G D SearleNational Institute of Allergy and Infectious Diseases (NIAID)Completed
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States, United Kingdom
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Laboratorio Pablo Cassará S.R.L.National Council of Scientific and Technical Research, Argentina; Fundacion... and other collaboratorsUnknownCutaneous MelanomaArgentina
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National Eye Institute (NEI)CompletedNiemann Pick DiseasesUnited States, United Kingdom
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical SciencesRecruitingEffects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) (EMTISTD)Supportive Care | GM2 GangliosidosisIran, Islamic Republic of
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National Taiwan University HospitalCompleted
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Cliniques universitaires Saint-Luc- Université...Completed
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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National Taiwan University HospitalActelionUnknown
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetTaiwan, United States, France, Germany, Italy, United Kingdom
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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G D SearleCompleted