- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: PTC124
Total 49 results
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PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden, United Kingdom
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCystic Fibrosis Foundation; FDA Office of Orphan Products DevelopmentCompleted
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompleted
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PTC TherapeuticsTerminatedCystic FibrosisUnited States, France, Spain, Belgium, Israel, Italy, Sweden
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PTC TherapeuticsCompleted
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PTC TherapeuticsWithdrawn
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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PTC TherapeuticsCompletedAniridiaUnited States, Canada
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NYU Langone HealthPTC TherapeuticsCompleted
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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PTC TherapeuticsTerminatedCystic FibrosisUnited States, Spain, France, Belgium, United Kingdom, Australia, Brazil, Bulgaria, Canada, Germany, Israel, Italy, Netherlands, Poland, Argentina, Greece
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PTC TherapeuticsCystic Fibrosis Foundation; ECFS-Clinical Trial Network (ECFS-CTN)CompletedCystic FibrosisUnited States, Spain, United Kingdom, Netherlands, Germany, France, Belgium, Italy, Australia, Argentina, Brazil, Bulgaria, Canada, Greece, Israel, Poland
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedHemophilia A | Hemophilia BUnited States, Canada, France, Italy
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PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, United Kingdom, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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PTC TherapeuticsCompletedBH4 Deficiency | HyperphenylalaninemiaUnited States
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NovartisCompletedPostmenopausal OsteoporosisSwitzerland
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PTC TherapeuticsNot yet recruitingPhenylketonuriaUnited States
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Centre d'Investigation Clinique et Technologique...CompletedNeuromuscular Disease | Chronic Respiratory Insufficiency | Intermittent Positive-pressure VentilationFrance
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Centre Hospitalier St AnneNot yet recruiting
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National Institute of Allergy and Infectious Diseases...Completed
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EuroVacc FoundationMedical Research Council; Centre Hospitalier Universitaire Vaudois; MRC/UVRI... and other collaboratorsCompleted
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NovartisCompletedPost-menopausal OsteoporosisGermany, Denmark
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EuroVacc FoundationCentre Hospitalier Universitaire Vaudois; MRC/UVRI and LSHTM Uganda Research... and other collaboratorsCompleted
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsUnited States, Switzerland
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National Institute of Allergy and Infectious Diseases...IPPOX Foundation; EuroVacc Foundation; Global Solutions for Infectious DiseasesWithdrawn
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Centre Hospitalier Metropole SavoieRecruitingHealthy | Pulmonary Disease, Chronic Obstructive | Pulmonary Arterial Hypertension | Lung Diseases, Interstitial | Chronic Heart Failure | Hyperventilation SyndromeFrance
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National Institute of Allergy and Infectious Diseases...Novartis Vaccines; HIV Vaccine Trials Network; IPPOX FoundationCompletedHIV InfectionsSouth Africa, Zambia, Tanzania
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MRC/UVRI and LSHTM Uganda Research UnitKing's College London; Karolinska Institutet; Gilead Sciences; Imperial College... and other collaboratorsEnrolling by invitation
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National Institute of Allergy and Infectious Diseases...Completed
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National Institute of Allergy and Infectious Diseases...HIV Vaccine Trials Network; IPPOX Foundation; EuroVacc Foundation; Global Solutions...Withdrawn
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ANRS, Emerging Infectious DiseasesUniversity College London Hospitals; Imperial College London; Medical Research... and other collaboratorsActive, not recruitingHealthy AdultsUnited Kingdom, Switzerland, France
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HIV Vaccine Trials NetworkCompletedHIV InfectionsSwitzerland