- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: rhASM
Total 9 results
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Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
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BioMarin PharmaceuticalCompleted
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ShireCompletedMetachromatic Leukodystrophy (MLD)Denmark
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ShireTerminatedLate Infantile Metachromatic LeukodystrophyDenmark
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VIUnited States
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ShireCompletedLate Infantile Metachromatic LeukodystrophyDenmark
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)United States, Canada, Belgium, Israel, Netherlands, United Kingdom, Germany, Spain, Japan, Brazil, Argentina, France, Greece, Italy
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VI | Maroteaux-Lamy SyndromeUnited States, Portugal, France