- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: rAAV-Olig001-ASPA
Total 777 results
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University of FloridaUniversity of Miami; University of Massachusetts, WorcesterNo longer available
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Myrtelle Inc.RecruitingCanavan DiseaseUnited States
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Beijing Tongren HospitalRecruitingBietti's Crystalline DystrophyChina
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics CorporationCompletedRetinal DegenerationUnited Kingdom
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Neurologix, Inc.Terminated
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Zhongmou TherapeuticsRecruitingX-linked RetinoschisisChina
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Liveome Inc.RecruitingA Study of LIV001 in Healthy Subjects and Those With Mild-to-Moderate Active Ulcerative Colitis (UC)Ulcerative ColitisAustralia
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Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
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BioGend Therapeutics Co.LtdRecruiting
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis Type 3 BUnited States, Germany, France, Spain
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STZ eyetrialUniversity Hospital TuebingenCompleted
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Hadassah Medical OrganizationCompletedLeber Congenital AmaurosisIsrael
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Boston Scientific CorporationCompletedHeart Failure | AV Block | Sinus Node DiseaseDenmark, United Kingdom, Spain, Hong Kong, Netherlands, Sweden, Malaysia, Austria, Belgium, France, Germany, Italy
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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University of California, Los AngelesAll India Institute of Medical Sciences, New Delhi; University of California... and other collaboratorsCompleted
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaActive, not recruitingAchromatopsiaUnited Kingdom, United States
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Zhejiang UniversityNot yet recruitingHemophilia B Without Inhibitor
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompleted
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UniQure Biopharma B.V.RecruitingHuntington DiseaseGermany, Poland, United Kingdom
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Appa HealthUniversity of WashingtonRecruitingDepressive Symptoms | Anxiety Disorders and SymptomsUnited States
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BiOMOTUM, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting
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Imperial College LondonWithdrawn
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Affiliated Hospital of Guangdong Medical UniversityNot yet recruitingHemophilia B Without Inhibitor
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McGill University Health Centre/Research Institute...Jewish General Hospital (Montreal, Quebec, Canada); Montreal General Hospital... and other collaboratorsCompleted
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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Le Syndicat Intercommunal pour le Thermalisme et...University Grenoble Alps; FloralisRecruitingChronic Venous InsufficiencyFrance
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Columbia UniversityMedical University of South Carolina; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruiting
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International AIDS Vaccine InitiativeNational Institute of Allergy and Infectious Diseases (NIAID); Children's Hospital...Unknown
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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University of ArizonaCompletedHepatitis C | Hiv | Bloodstream Infection | Skin and Soft Tissue InfectionsUnited States
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Seoul St. Mary's HospitalBoehringer IngelheimActive, not recruiting
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Voyager TherapeuticsWithdrawn
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States