- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: rAAV1-CB-hAAT
Total 812 results
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Beijing Tongren HospitalRecruitingBietti's Crystalline DystrophyChina
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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International AIDS Vaccine InitiativeNational Institute of Allergy and Infectious Diseases (NIAID); Children's Hospital...Unknown
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University of MinnesotaRecruitingCannabis Use DisorderUnited States
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Voyager TherapeuticsWithdrawn
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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CymaBay Therapeutics, Inc.Completed
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National Cancer Institute (NCI)WithdrawnLocally Advanced Malignant Solid Neoplasm | Metastatic Malignant Solid Neoplasm | Aggressive Non-Hodgkin Lymphoma | Indolent Non-Hodgkin LymphomaUnited States
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDry Age-related Macular DegenerationItaly
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Fate TherapeuticsTerminatedHematologic MalignanciesUnited States
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University of FloridaUniversity of Miami; University of Massachusetts, WorcesterNo longer available
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis Type 3 BUnited States, Germany, France, Spain
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STZ eyetrialUniversity Hospital TuebingenCompleted
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Hadassah Medical OrganizationCompletedLeber Congenital AmaurosisIsrael
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Cleave Therapeutics, Inc.CompletedMyelodysplastic Syndromes | Acute Myeloid Leukemia, in RelapseUnited States, Australia
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics CorporationCompletedRetinal DegenerationUnited Kingdom
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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University of ZurichRecruitingLung Transplant Rejection | Lung Transplant Failure and RejectionSwitzerland
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Cleave Biosciences, Inc.TerminatedAdvanced Solid TumorsUnited States
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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Calithera Biosciences, IncCompletedRenal Cell Carcinoma | Non Small Cell Lung Cancer | Mesothelioma | Solid Tumors | Triple-Negative Breast Cancer | Fumarate Hydratase (FH)-Deficient Tumors | Succinate Dehydrogenase (SDH)-Deficient Gastrointestinal Stromal Tumors (GIST) | Succinate Dehydrogenase (SDH)-Deficient Non-gastrointestinal... and other conditionsUnited States
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Neurologix, Inc.Terminated
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Calithera Biosciences, IncCompletedHealthy VolunteersUnited States
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Calithera Biosciences, IncTerminatedNon-GCB/ABC Diffuse Large B-Cell Lymphoma | With and Without MyD88 and/or CD79B MutationsUnited States
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National Center for Research Resources (NCRR)University of North CarolinaCompleted
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University of MinnesotaRecruitingPeripheral Artery DiseaseUnited States
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Cosmo Technologies LtdRecruitingAdvanced Refractory Solid Tumors | Subjects Considered Likely to Respond to CB-03-10United States
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Calithera Biosciences, IncTerminatedNon-Small Cell Lung Cancer | Squamous Non-small-cell Lung Cancer | NFE2L2 Gene Mutation | Squamous Non-Small Cell Neoplasm of LungUnited States
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Second Affiliated Hospital, School of Medicine,...RecruitingB-cell Non Hodgkin LymphomaChina
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UniQure Biopharma B.V.RecruitingHuntington DiseaseGermany, Poland, United Kingdom
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Cellestia Biotech AGTerminatedBreast Cancer | Adenoid Cystic Carcinoma | Hepatocellular Carcinoma | Colorectal Cancer | Osteosarcoma | Non-hodgkin Lymphoma | Glomus Tumor, Malignant | T-ALLUnited States, Spain, Korea, Republic of, Germany, France, Switzerland
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VA Office of Research and DevelopmentCompleted
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Cukurova UniversityRecruitingThree-Dimensional Printing, Computer-Aided Design, DentalTurkey
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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Celladon CorporationCompletedHeart Failure | Cardiomyopathies | Ischemic Cardiomyopathy | Non-ischemic CardiomyopathyUnited States, United Kingdom, Belgium, Germany, Poland, Israel, Netherlands, Hungary, Denmark, Sweden