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- US Clinical Trials Registry
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Search clinical trials for: rAAV2-ND4
Total 442 results
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Beijing Tongren HospitalRecruitingBietti's Crystalline DystrophyChina
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, Germany, Italy, France
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, France, Germany, Italy
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STZ eyetrialUniversity Hospital TuebingenCompleted
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Hadassah Medical OrganizationCompletedLeber Congenital AmaurosisIsrael
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis Type 3 BUnited States, Germany, France, Spain
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King Khaled Eye Specialist HospitalKing Faisal Specialist Hospital & Research CenterCompletedRetinitis Pigmentosa | Retinal DiseaseSaudi Arabia
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MeiraGTx, LLCRecruitingGrade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Parotid GlandsUnited States, Canada
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Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics CorporationCompletedRetinal DegenerationUnited Kingdom
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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University of FloridaUniversity of Miami; University of Massachusetts, WorcesterNo longer available
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
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Neurologix, Inc.Terminated
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International AIDS Vaccine InitiativeNational Institute of Allergy and Infectious Diseases (NIAID); Children's Hospital...Unknown
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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Voyager TherapeuticsWithdrawn
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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Spark TherapeuticsCompleted
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UniQure Biopharma B.V.RecruitingHuntington DiseaseGermany, Poland, United Kingdom
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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ViGeneron GmbHRecruiting
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Sangamo TherapeuticsCeregeneCompletedParkinson's DiseaseUnited States
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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National Institute of Neurological Disorders and...Completed
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Zhongmou TherapeuticsRecruitingX-linked RetinoschisisChina