- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials Sponsored by Office of Rare Diseases (ORD)
Total 456 results
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic SyndromeUnited States
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University of MinnesotaUnknown
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University of UtahCompleted
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University of UtahCompletedCystic FibrosisUnited States
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University of MinnesotaCompleted
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Johns Hopkins UniversityCompletedPemphigusUnited States
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Northwestern Memorial HospitalCompleted
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House Ear InstituteUnknownMeningioma | Neurofibromatosis 2 | Schwannoma, VestibularUnited States
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Johns Hopkins UniversityCompletedSystemic Lupus Erythematosus | Antiphospholipid Antibody SyndromeUnited States
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Northwestern Memorial HospitalUnknownSystemic Lupus ErythematosusUnited States
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Northwestern Memorial HospitalUnknownAplastic Anemia | Graft Versus Host DiseaseUnited States
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Johns Hopkins UniversityCompletedAutoimmune Diseases | Purpura, Thrombocytopenic | Anemia, Hemolytic, Autoimmune | Felty SyndromeUnited States
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Fred Hutchinson Cancer CenterCompletedSickle Cell AnemiaUnited States
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Fred Hutchinson Cancer CenterCompleted
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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Roswell Park Cancer InstituteCompleted
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Fred Hutchinson Cancer CenterCompletedMetabolism, Inborn Errors | Granulomatous Disease, ChronicUnited States
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Fairview University Medical CenterCompletedNeutropenia | Sickle Cell Anemia | Red-Cell Aplasia, Pure | Thalassemia MajorUnited States
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Fairview University Medical CenterUnknownRheumatoid Arthritis | Systemic Lupus Erythematosus | Giant Cell Arteritis | Wegener's Granulomatosis | Churg-Strauss Syndrome | Polyarteritis Nodosa | Purpura, Schoenlein-Henoch | Juvenile Rheumatoid Arthritis | Takayasu Arteritis | Pure Red Cell Aplasia | Graft Versus Host Disease | Anemia, Hemolytic, Autoimmune and other conditionsUnited States
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Fairview University Medical CenterUnknownHemophagocytic Lymphohistiocytosis | Graft Versus Host Disease | Chediak-Higashi Syndrome | Virus-Associated Hemophagocytic Syndrome | X-Linked Lymphoproliferative Syndrome | Familial Erythrophagocytic LymphohistiocytosisUnited States
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Fred Hutchinson Cancer CenterCompleted
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University of Alabama at BirminghamCompletedPurpura, Thrombocytopenic, IdiopathicUnited States
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Herbert Irving Comprehensive Cancer CenterCompleted
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University of California, Los AngelesRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedCerebellar Diseases | Episodic Ataxia SyndromeUnited States, Canada, United Kingdom
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Icahn School of Medicine at Mount SinaiCompletedShy-Drager Syndrome | Orthostatic HypotensionUnited States
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Icahn School of Medicine at Mount SinaiCompleted
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Icahn School of Medicine at Mount SinaiCompleted
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Office of Rare Diseases (ORD)The University of Texas Medical Branch, GalvestonCompletedHereditary AtaxiaUnited States
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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National Institute of Allergy and Infectious Diseases...University of ChicagoRecruitingToxoplasmosisUnited States
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National Center for Research Resources (NCRR)Mayo ClinicCompletedPolyradiculoneuropathy, Chronic Inflammatory Demyelinating
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National Center for Research Resources (NCRR)Northwestern UniversityCompletedEpidermolysis Bullosa Acquisita
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National Center for Research Resources (NCRR)Yale UniversityCompletedHereditary Hemorrhagic Telangiectasia
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National Center for Research Resources (NCRR)Northwestern UniversityCompletedHIV Infections | Acquired Immunodeficiency Syndrome | HIV Wasting Syndrome
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National Center for Research Resources (NCRR)Northwestern UniversityCompletedHepatic Encephalopathy | Cirrhosis | Portal Hypertension
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National Center for Research Resources (NCRR)Emory UniversityCompletedParkinson Disease
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National Institute of Allergy and Infectious Diseases...National Bacteriological LaboratoryCompleted
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University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedAndersen-Tawil Syndrome | Andersen SyndromeUnited States, Canada, Italy, United Kingdom
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National Center for Research Resources (NCRR)Yale UniversityCompleted
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National Center for Research Resources (NCRR)Northwestern UniversityCompletedSystemic Lupus Erythematosus