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Clinical Trials Sponsored by Recordati Rare Diseases
Total 376 results
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Recordati Rare DiseasesRecruitingPropionic Acidemia | Methylmalonic AcidemiaFrance, Spain, Italy, United Kingdom, Norway, Germany, Sweden
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Recordati Rare DiseasesCompletedCystinosisBelgium, France, United Kingdom, Germany, Italy
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Recordati Rare DiseasesSyneos HealthRecruitingNeurotrophic KeratitisUnited Kingdom, Spain, Italy, United States, Germany, France, Hungary
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The Cleveland ClinicRecordati Rare DiseasesNot yet recruitingMild Autonomous Cortisol Secretion (MACS)United States
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.RecruitingPropionic Acidemia | Methylmalonic Acidemia | HyperammonemiaUnited States
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Target PharmaSolutions, Inc.Recordati Rare DiseasesEnrolling by invitationPropionic Acidemia | Methylmalonic Acidemia | HyperammonemiaUnited States
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Centre for Human Drug Research, NetherlandsRecordati Rare DiseasesCompleted
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Centre hospitalier de l'Université de Montréal...Recordati Rare DiseasesActive, not recruitingEndogenous Cushing SyndromeCanada
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Massachusetts General HospitalUnited States Department of Defense; Recordati Rare DiseasesRecruitingPain, Chronic | Schwannomatosis | SchwannomasUnited States
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Fundación Grupo de Investigación en Cuidados Intensivos...Recordati Rare DiseasesActive, not recruiting
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Recordati...CompletedDiabetes Mellitus | GastroparesisUnited States
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Imagine InstituteReference center for rare diseases (Rare Gynecologic Diseases)RecruitingMayer Rokitansky Kuster Hauser SyndromeFrance
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic SyndromeUnited States
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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Myasthenia Gravis Rare Disease NetworkRecruitingMyasthenia Gravis | MuSK Myasthenia Gravis | MuSK MGUnited States
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University of California, Los AngelesRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedCerebellar Diseases | Episodic Ataxia SyndromeUnited States, Canada, United Kingdom
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Assistance Publique - Hôpitaux de ParisFrench rare diseases Healthcare Network; The French Foundation for Rare DiseasesActive, not recruitingAmelogenesis Imperfecta | Dentinogenesis Imperfecta | Dentin AnomaliesFrance
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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University of UtahCompleted
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House Ear InstituteUnknownMeningioma | Neurofibromatosis 2 | Schwannoma, VestibularUnited States
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Johns Hopkins UniversityCompletedSystemic Lupus Erythematosus | Antiphospholipid Antibody SyndromeUnited States
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Northwestern Memorial HospitalUnknownSystemic Lupus ErythematosusUnited States
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Northwestern Memorial HospitalUnknownAplastic Anemia | Graft Versus Host DiseaseUnited States
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Johns Hopkins UniversityCompletedPemphigusUnited States
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University of MinnesotaUnknown
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Northwestern Memorial HospitalCompleted
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University of UtahCompletedCystic FibrosisUnited States
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Johns Hopkins UniversityCompletedAutoimmune Diseases | Purpura, Thrombocytopenic | Anemia, Hemolytic, Autoimmune | Felty SyndromeUnited States
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University of MinnesotaCompleted
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTemporal ArteritisUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedPolyarteritis NodosaUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsRecruitingGiant Cell Arteritis | Microscopic Polyangiitis | Polyarteritis Nodosa | Takayasu's Arteritis | Eosinophilic Granulomatosis With Polyangiitis (Churg-Strauss) | Granulomatosis With Polyangiitis (Wegener's)United States, Canada, Turkey
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare...CompletedGiant Cell Arteritis | Takayasu's ArteritisUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedWegener's GranulomatosisUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMicroscopic Polyangiitis | Granulomatosis With Polyangiitis | Wegener'sUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTakayasu's ArteritisUnited States, Canada
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University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedAndersen-Tawil Syndrome | Andersen SyndromeUnited States, Canada, Italy, United Kingdom
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Fred Hutchinson Cancer CenterCompletedSickle Cell AnemiaUnited States
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Fred Hutchinson Cancer CenterCompleted
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States